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Study on genotype and phenotype relation by genome analysis of responsible gene region in SMA

Not Applicable
Conditions
Spinal Muscular Atrophy
Registration Number
JPRN-UMIN000040095
Lead Sponsor
Institute of Medical Genetics, Tokyo Women's Medical University
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Complete: follow-up continuing
Sex
All
Target Recruitment
50
Inclusion Criteria

Not provided

Exclusion Criteria

DNA samples from patients who were confirmed without SMA DNA samples without demographic data including age, SMA type, age at onset and maximum and current motor function

Study & Design

Study Type
Observational
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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