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GEN-001 Plus Pembrolizumab for Patients With Advanced Refractory Biliary Tract Cancer

Phase 2
Recruiting
Conditions
Biliary Tract Cancer
Interventions
Registration Number
NCT05998447
Lead Sponsor
Genome & Company
Brief Summary

This is a phase II, multicenter, open-label study with a safety run-in to evaluate the safety and efficacy of GEN-001 in combination with pembrolizumab or in combination with pembrolizumab and mFOLFOX for patients with advanced refractory BTC who have progressed after 1 or 2 prior standard therapy and are not candidates for any other standard therapy. The safety run-in phase will be conducted before the main study phase

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
148
Inclusion Criteria
  • The patient (or legally acceptable representative if applicable) provides written informed consent for the trial.
  • Be ≥19 years of age on day of signing informed consent.
  • Patient with histologically or cytologically confirmed diagnosis of unresectable, recurrent, or metastatic advanced biliary tract adenocarcinoma of the gallbladder or biliary tree (either intrahepatic or extrahepatic cholangiocarcinoma)
Exclusion Criteria
  • A WOCBP who has a positive urine pregnancy test (within 72 hours) prior to treatment. If the urine test is positive or cannot be confirmed as negative, a serum pregnancy test will be required.
  • Has received prior therapy with an anti-PD-1, anti-PD-L1, or anti-PD-L2 agent or with an agent directed to another stimulatory or co-inhibitory T-cell receptor (Cohort 1 only), and was discontinued from the previous IO therapy due to a Grade 3 or higher immune-related AE (irAE) (Cohort 2 and Cohort 3).
  • Is currently participating and receiving study treatments or has participated in a study of an investigational agent and received the study therapy or has used an investigational device within 4 weeks prior to the first dose of study treatment.
  • Has had an allogeneic tissue/solid organ transplan

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
GEN-001 with pembrolizumab or GEN-001 with pembrolizumab and mFOLFOXmFOLFOXDrug: GEN-001 Drug: pembrolizumab Drug: mFOLFOX
GEN-001 with pembrolizumab or GEN-001 with pembrolizumab and mFOLFOXPembrolizumabDrug: GEN-001 Drug: pembrolizumab Drug: mFOLFOX
GEN-001 with pembrolizumab or GEN-001 with pembrolizumab and mFOLFOXGEN-001Drug: GEN-001 Drug: pembrolizumab Drug: mFOLFOX
Primary Outcome Measures
NameTimeMethod
The recommended Phase 2 dose (RP2D) of GEN-001 in patients with advanced refractory biliary tract cancer (BTC), when administered as combined with pembrolizumab or as combined with pembrolizumab and mFOLFOX.1 years

Incidence of dose-limiting toxicity (DLT)

Objective Response Rate (ORR) per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 by the Investigator.1 years

The assessment of the anti-tumor activity per cohort

Secondary Outcome Measures
NameTimeMethod
Incidence of Adverse Event (AE)s and laboratory abnormalities per National Cancer Institute Common Terminology Criteria for AEs (NCI CTCAE) v.5.0. cohort.1 years

The assessment the overall safety and tolerability per cohort.

Duration of Response (DoR)1 years

the time from the first documentation of objective tumor response to the first documentation of objective tumor progression or to death due to any cause, whichever occurs first

Progression-free Survival (PFS)1 years

the time from the start date of treatment to the date of PD by RECIST v1.1 or death due to any cause, whichever occurs first

Overall Survival (OS)1 years

the time from the start date of treatment to the date of death

Trial Locations

Locations (6)

Severance Hospital

🇰🇷

Seoul, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Samsung Medical Center.

🇰🇷

Seoul, Korea, Republic of

Korea University Guro Hospital

🇰🇷

Seoul, Korea, Republic of

Ajou University Medical Center

🇰🇷

Suwon, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

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