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Observational Study of Surgical Treatment of Necrotizing Enterocolotis

Completed
Conditions
Infant, Newborn
Infant, Low Birth Weight
Infant, Small for Gestational Age
Infant, Premature
Enterocolitis, Necrotizing
Intestinal Perforation
Registration Number
NCT01223261
Lead Sponsor
NICHD Neonatal Research Network
Brief Summary

The purposes of this study were: 1) to compare mortality and postoperative morbidities in extremely low birth weight (ELBW) infants who underwent initial laparotomy or drainage for necrotizing enterocolitis (NEC) or isolated intestinal perforation (IP); 2) to determine the ability to distinguish NEC from IP preoperatively and the importance of this distinction on outcome measures; and 3) to evaluate the association between extent of intestinal disease determined at operation and outcome measures. All ELBW infants born at participating NRN centers were screened for the presence of NEC or IP that was thought by the pediatric surgeon and neonatologist to require surgical intervention. Data were collected enrolled infants, including: intraoperative findings recorded by the surgeon and specific post-operative complications. Neurodevelopmental examinations were conducted on surviving infants at 18-22 months corrected age.

Detailed Description

Necrotizing enterocolitis (NEC) is a condition, generally affecting premature infants, in which the intestines become ischemic (lack oxygen and/or blood flow). NEC occurs in up to 5-15% of extremely low birth weight (ELBW) infants. Isolated or focal intestinal perforation (IP) is a less common condition, affecting an estimated 4% of ELBWs, in which a hole develops in the intestines leaking fluid into the abdomin. The outcomes for infants with NEC or IP are poor: 49% die and half of the surviving infants are neurodevelopmentally impaired.

Surgical options for NEC and IP include two possible procedures: peritoneal drainage, in which a tube is placed in the abdominal cavity through a small incision for fluid to drain out; or laparotomy, in which an incision is made in the abdomen and diseased intestine is removed. Infants treated with an initial drainage sometimes go on to need a laparotomy. Most surgeons now believe that a diagnosis of the intestinal perforation (IP) may actually be either true NEC or a different and distinct pathology, termed isolated intestinal perforation. The ability to distinguish these 2 conditions preoperatively, based on perinatal characteristics, physical examination findings, and findings on abdominal plain film imaging, remains unknown. If these 2 entities can be distinguished preoperatively, the intervention chosen and outcomes may be different. From the two available surgical options, tt is not known whether initial laparotomy or peritoneal drain placement is more effective for either NEC or IP.

This study was a prospective, multicenter observational study to describe the surgical outcomes (mortality, post-operative intestinal stricture, intra-abdominal abscess formation, etc.) in ELBW infants with either NEC or IP who underwent initial laparotomy or peritoneal drainage. We also evaluated the ability of surgeons to distinguish NEC and IP pre-operatively and the relevance of this distinction on outcome. Finally, an analysis of the impact of extent of intestinal involvement with NEC on outcome measures is reported.

All ELBW infants born at participating NRN centers were screened for the presence of NEC or IP that was thought by the pediatric surgeon and neonatologist to require surgical intervention. Data were collected enrolled infants, including: intraoperative findings recorded by the surgeon and specific post-operative complications.

Neurodevelopmental examinations were conducted on surviving infants at 18-22 months corrected age.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
156
Inclusion Criteria
  • Infants born 401-1,000 grams at birth enrolled in the NRN Generic Database
  • Sage III NEC or isolated intestinal perforation
  • Pediatric surgeon decision to perform surgery for suspected NEC or IP
Exclusion Criteria
  • Decision not to treat

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Feasibility of conducting a randomized trial1 year

Ability to enroll infants in a 1-year period

Secondary Outcome Measures
NameTimeMethod
Frequency of postoperative complicationsUntil hospital discharge or 120 days of life
Neurodevelopmental impairment18-22 months corrected age
Document variation in current surgical practicesUntil hospital discharge or 120 days of life
Prevalence of infants who would qualify for the studyUntil hospital discharge or 120 days of life

Trial Locations

Locations (17)

Case Western Reserve University, Rainbow Babies and Children's Hospital

🇺🇸

Cleveland, Ohio, United States

University of Texas Southwestern Medical Center at Dallas

🇺🇸

Dallas, Texas, United States

University of Miami

🇺🇸

Miami, Florida, United States

Cincinnati Children's Medical Center

🇺🇸

Cincinnati, Ohio, United States

Yale University

🇺🇸

New Haven, Connecticut, United States

Stanford University

🇺🇸

Palo Alto, California, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

University of California at San Diego

🇺🇸

San Diego, California, United States

Emory University

🇺🇸

Atlanta, Georgia, United States

Indiana University

🇺🇸

Indianapolis, Indiana, United States

University of Rochester

🇺🇸

Rochester, New York, United States

Wake Forest University

🇺🇸

Charlotte, North Carolina, United States

Wayne State University

🇺🇸

Detroit, Michigan, United States

Duke University

🇺🇸

Durham, North Carolina, United States

RTI International

🇺🇸

Durham, North Carolina, United States

Brown University, Women & Infants Hospital of Rhode Island

🇺🇸

Providence, Rhode Island, United States

University of Texas Health Science Center at Houston

🇺🇸

Houston, Texas, United States

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