MedPath

Phase 2a, Dose-ranging Study With PF-05221304 in Nonalcoholic Fatty Liver Disease (NAFLD)

Phase 2
Completed
Conditions
Nonalcoholic Fatty Liver Disease
Nonalcoholic Steatohepatitis
Interventions
Drug: Placebo
Registration Number
NCT03248882
Lead Sponsor
Pfizer
Brief Summary

Phase 2a, dose-ranging Study with PF-05221304 in Nonalcoholic Fatty Liver Disease (NAFLD)

Detailed Description

A Phase 2a, Randomized, Double-blind, Placebo-controlled, Dose-ranging, Parallel Group Study To Evaluate Safety, Tolerability, And Pharmacodynamics Of PF-05221304 Administered Daily For 16-weeks To Adult Subjects With Nonalcoholic Fatty Liver Disease

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
305
Inclusion Criteria
  • Body Mass Index >= 25 kg/m2
  • Body Weight > 50 kg
  • Liver fat (assessed via MRI-PDFF) >= 8%
  • Biopsy-proven NASH - diagnosed in previous 24-months
  • Presumed NASH - per Sponsor's definition
  • NAFLD with minimal inflammation/fibrosis
  • Features of Metabolic Syndrome
Exclusion Criteria
  • Alcohol-induced steatohepatitis or other forms of chronic liver disease
  • Positive for Hepatitis B, Hepatitis C, or Human Deficiency Virus
  • Severe Renal Impairment
  • Contraindications for MRI

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlaceboDouble-Blind, PF-05221304-matching Placebo
PF-05221304 - 2 mgPF-05221304PF-05221304 - 2 mg, once-daily
PF-05221304 - 10 mgPF-05221304PF-05221304 - 10 mg, once-daily
PF-05221304 - 25 mgPF-05221304PF-05221304 - 25 mg, once-daily
PF-05221304 - 50 mgPF-05221304PF-05221304 - 50 mg, once-daily
Primary Outcome Measures
NameTimeMethod
Percent Change From Baseline in Liver Fat by Magnetic Resonance Imaging-Proton Density Fat Fraction (MRI- PDFF) at Week 16Baseline (between Day -14 and Day 1), Week 16

MRI-PDFF utilized a gradient echo sequence with low flip angle (FA) to minimize T1 bias, corrected T2\* decay (due to iron overload) via modeling of the fat signal as a superposition of multiple frequency components from 5 different lipid types, and was applied in each of the 9 Couinaud segments. This technique improved fat quantification accuracy for the entire liver permitting quantification of small differences/changes following pharmacological intervention.

Secondary Outcome Measures
NameTimeMethod
Number of Participants With Treatment-Emergent Adverse EventsFrom first dose of study treatment (Day 1) up to Week 20

An AE was any untoward medical occurrence in a study subject administered a product or medical device. A serious AE (SAE) is an AE resulting in any of the following outcomes or deemed significant for any other reason: death; life-threatening; initial or prolonged inpatient hospitalization; persistent or significant disability/incapacity; congenital anomaly/birth defect. Any such events with initial onset or increasing in severity after the first dose of study treatment were counted as treatment-emergent.

Percent Change From Baseline in Alanine Aminotransferase at Week 16Baseline (Day 1 pre-dose), Week 16

Potential improvement in liver function was denoted by reduction in alanine transaminase (ALT)

Number of Participants With Laboratory AbnormalitiesFrom first dose of study treatment (Day 1) up to Week 20

Following laboratory parameters were assessed against pre-defined abnormality criteria: hematology (hemoglobin, hematocrit, erythrocytes, reticulocytes, platelets, leukocytes, lymphocytes, neutrophils, basophils, eosinophils, monocytes, activated partial thromboplastin time, prothrombin time \[PT\], PT/international normalized ratio, reticulocytes); chemistry (indirect bilirubin, direct bilirubin, protein, albumin, blood urea nitrogen, creatinine, creatine kinase, urate, calcium, sodium, potassium, chloride, bicarbonate, urine urobilinogen); urinalysis (pH, urine glucose, urine ketones, urine protein, urine hemoglobin, nitrites, leukocyte esterase, urine erythrocytes, urine leukocytes, urine hyaline casts, urine bilirubin, granular casts).

Number of Participants With Vital Signs Data Meeting Predefined CriteriaFrom first dose of study treatment (Day 1) up to Week 18

Vital signs categorical summarization criteria: 1) sitting systolic blood pressure (SBP) \<90 or \>180 millimeters of mercury (mmHg); 2) sitting diastolic blood pressure (DBP) \<50 mmHg or \>110 mmHg; 3) sitting pulse rate \<40 or \>120 beats per minute (bpm); 4) change from baseline (increase or decrease) in sitting DBP greater than or equal to (\>=) 20 mmHg; 5) change from baseline (increase or decrease) in sitting SBP \>=30 mmHg.

Number of Participants With 12-Lead Electrocardiogram (ECG) Data Meeting Predefined CriteriaFrom first dose of study treatment (Day 1) up to Week 18

ECG categorical summarization criteria: 1) QRS interval (time from ECG Q wave to the end of the S wave corresponding to ventricle depolarization) \>=140 milliseconds (msec); 2) QRS interval \>=50% change from baseline; 3) PR interval (the interval between the start of the P wave and the start of the QRS complex, corresponding to the time between the onset of the atrial depolarization and onset of ventricular depolarization) \>=300 msec; 4) PR interval \>=25% change when baseline is \>200 msec or \>=50% change when baseline is \<=200 msec; 5) QT interval (time from ECG Q wave to the end of the T wave corresponding to electrical systole): absolute value of \>=500 msec; 6) QTcF interval (QT corrected for heart rate using Fridericia's formula) absolute value of 450 to \<480 msec; 7) QTcF interval: absolute value of 480 to \<500 msec; 8) QTcF interval: absolute value \>=500 msec; 9) QTcF interval: a change from baseline of 30 to \<60 msec; 10) QTcF interval: a change from baseline \>=60 msec.

Trial Locations

Locations (137)

Discovery Clinical Services Ltd.

🇨🇦

Victoria, British Columbia, Canada

South Denver Gastroenterology, P.C.

🇺🇸

Englewood, Colorado, United States

ClinSearch

🇺🇸

Chattanooga, Tennessee, United States

Oxford Medical Imaging

🇨🇦

Mississauga, Ontario, Canada

Digestive Disease Associates, PA

🇺🇸

Catonsville, Maryland, United States

Krakowskie Centrum Medyczne sp. z o.o.

🇵🇱

Krakow, Poland

Schiff Center for Liver Diseases/University of Miami

🇺🇸

Miami, Florida, United States

Stand Up MRI of Miami

🇺🇸

Miami, Florida, United States

Harborview Medical Center

🇺🇸

Seattle, Washington, United States

Midwest Institute for Clinical Research

🇺🇸

Indianapolis, Indiana, United States

Precision Research Institute

🇺🇸

San Diego, California, United States

Sterling Research Group, Ltd.

🇺🇸

Cincinnati, Ohio, United States

Holy Family Hospital

🇮🇱

Nazareth, Israel

Independent Imaging

🇺🇸

Wellington, Florida, United States

Franco Felizarta MD

🇺🇸

Bakersfield, California, United States

University of California, San Diego

🇺🇸

La Jolla, California, United States

Dr. Jones & Partners Medical Imaging

🇦🇺

Adelaide, South Australia, Australia

IRM Quebec

🇨🇦

Quebec, Canada

Storr Liver Centre, Westmead Hospital

🇦🇺

Westmead, New South Wales, Australia

Rabin Medical Center

🇮🇱

Petah Tikva, Israel

Gabinet Lekarski Malgorzata Saryusz-Wolska

🇵🇱

Lodz, Poland

Quest Clinical Research

🇺🇸

San Francisco, California, United States

Henry Ford Health System

🇺🇸

Detroit, Michigan, United States

Clinical Trials of Texas, Inc.

🇺🇸

San Antonio, Texas, United States

Pinnacle Clinical Research, PLLC

🇺🇸

San Antonio, Texas, United States

St. Joseph's Health Care London

🇨🇦

London, Ontario, Canada

St. Michael's Hospital - MRI Research Centre

🇨🇦

Toronto, Ontario, Canada

Toronto Liver Centre - Liver Care Centre Corporation

🇨🇦

Toronto, Ontario, Canada

Resonance Magnetique du Saguenay-Lac-Saint-Jean

🇨🇦

Chicoutimi, Quebec, Canada

Medpharmgene Inc

🇨🇦

Montreal, Quebec, Canada

Radiologie Varad

🇨🇦

Montreal, Quebec, Canada

Shaare Zedek Medical Center

🇮🇱

Jerusalem, Israel

Flinders Medical Centre/Department of Gastroenterology & Hepatology

🇦🇺

Adelaide, South Australia, Australia

eStudySite

🇺🇸

La Mesa, California, United States

Clinical Trials Research

🇺🇸

Lincoln, California, United States

San Diego Imaging Chula Vista

🇺🇸

Chula Vista, California, United States

Inland Empire Liver Foundation

🇺🇸

Rialto, California, United States

Jacksonville Center for Clinical Research

🇺🇸

Jacksonville, Florida, United States

Avail Clinical Research, LLC

🇺🇸

Orange City, Florida, United States

Heartland Research Associates, LLC

🇺🇸

Wichita, Kansas, United States

Ascension Via Christi Imaging at St. Francis

🇺🇸

Wichita, Kansas, United States

Mercy Medical Center

🇺🇸

Baltimore, Maryland, United States

Wake Research Associates, LLC

🇺🇸

Raleigh, North Carolina, United States

PMG Research of Wilmington, LLC

🇺🇸

Wilmington, North Carolina, United States

Baylor College of Medicine - Advanced Liver Therapies

🇺🇸

Houston, Texas, United States

Pinnacle Clinical Research

🇺🇸

Rollingwood, Texas, United States

Clinical Research Advantage, Inc./Wasatch Peak Family Practice

🇺🇸

Layton, Utah, United States

Australian Clinical Research Network

🇦🇺

Maroubra, New South Wales, Australia

Spectrum Medical Imaging

🇦🇺

Randwick, New South Wales, Australia

Castlereagh Imaging

🇦🇺

Westmead, New South Wales, Australia

Royal Melbourne Hospital

🇦🇺

Parkville, Victoria, Australia

Radiology SA

🇦🇺

Adelaide, South Australia, Australia

False Creek Healthcare

🇨🇦

Vancouver, British Columbia, Canada

Nova Scotia Health Authority, QEII Health Sciences Centre

🇨🇦

Halifax, Nova Scotia, Canada

LMC Clinical Research Inc. (Bayview)

🇨🇦

Toronto, Ontario, Canada

Aggarwal and Associates Limited

🇨🇦

Brampton, Ontario, Canada

London Health Sciences Centre - University Hospital

🇨🇦

London, Ontario, Canada

Nova Scotia Health Authority - QEII Health Sciences Centre

🇨🇦

Halifax, Nova Scotia, Canada

St. Michael's Hospital

🇨🇦

Toronto, Ontario, Canada

University Health Network (UHN)

🇨🇦

Toronto, Ontario, Canada

Ecogene-21

🇨🇦

Chicoutimi, Quebec, Canada

Clinique de Medecine Urbaine du Quartier Latin

🇨🇦

Montreal, Quebec, Canada

Centre de recherche du CHUM

🇨🇦

Montreal, Quebec, Canada

Chronic Viral Illness Service - Royal Victoria Hospital - McGill University Health Centre (MUHC)

🇨🇦

Montreal, Quebec, Canada

Cedar Cancer Center - McGill University Health Centre

🇨🇦

Montreal, Quebec, Canada

McGill University Health Centre

🇨🇦

Montreal, Quebec, Canada

Research Institute of the MUHC

🇨🇦

Montreal, Quebec, Canada

Recherche Medicale St-Jerome Inc

🇨🇦

St-Jerome, Quebec, Canada

Centre Intégré Universitaire de Santé et de Services Sociaux (CIUSSS) de l'Estrie

🇨🇦

Sherbrooke, Quebec, Canada

Centre de recherche de l'Institut Universitaire de Cardiologie et de pneumologie de Quebec

🇨🇦

Quebec, Canada

Centre de recherche Saint-Louis

🇨🇦

Quebec, Canada

IRM Québec - Clinique St-Louis

🇨🇦

Quebec, Canada

CHU de Quebec - Universite Laval - site Centre Hospitalier de l'Universite Laval (CHUL)

🇨🇦

Quebec, Canada

Hillel Yaffe Medical Center

🇮🇱

Hadera, Israel

Rambam Health Care Campus

🇮🇱

Haifa, Israel

Alpha Recherche Clinique

🇨🇦

Quebec, Canada

Clinix

🇨🇦

Quebec, Canada

Hadassah Hebrew University Medical Center - Ein Kerem

🇮🇱

Jerusalem, Israel

The Chaim Sheba Medical Center

🇮🇱

Ramat-Gan, Israel

Galilee Medical Center

🇮🇱

Nahariya, Israel

Tel-Aviv Sourasky Medical Center

🇮🇱

Tel-Aviv, Israel

Synexus Polska Sp. z o.o. Oddzial w Gdyni

🇵🇱

Gdynia, Poland

Osrodek Badan Klinicznych

🇵🇱

Jaworze, Poland

Synexus Polska Sp. z o.o. Oddzial w Katowicach

🇵🇱

Katowice, Poland

Centrum Medyczne A-Z Clinic

🇵🇱

Krakow, Poland

Centrum Medyczne Medyk

🇵🇱

Rzeszow, Poland

Synexus Polska Sp. z o.o. Oddzial we Wroclawiu

🇵🇱

Wroclaw, Poland

Niepubliczny Zaklad Opieki Zdrowotnej Centrum Badan Klinicznych

🇵🇱

Wroclaw, Poland

DOBROSTAN - Gabinety Lekarskie

🇵🇱

Wroclaw, Poland

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

Changhua Christian Hospital

🇨🇳

Changhua city, Changhua County, Taiwan

Qps-Mra, Llc

🇺🇸

South Miami, Florida, United States

University of California, San Diego (Altman Clinical and Translational Research Institute)

🇺🇸

La Jolla, California, United States

National Research Institute

🇺🇸

Los Angeles, California, United States

Ocean Blue Medical Research Center, Inc

🇺🇸

Miami Springs, Florida, United States

BioTelemetry Research

🇺🇸

Rochester, New York, United States

Stanford University Medical Center, Blake wilbur Building

🇺🇸

Palo Alto, California, United States

Huntington Medical Research Institute

🇺🇸

Pasadena, California, United States

Stanford University Medical Center

🇺🇸

Palo Alto, California, United States

Gastrointestinal Associates, PA

🇺🇸

Flowood, Mississippi, United States

Borland-Groover Clinic

🇺🇸

Jacksonville, Florida, United States

Advanced Gastroenterology Associates, LLC

🇺🇸

Palm Harbor, Florida, United States

South Florida Center Of Gastroenterology, PA

🇺🇸

Wellington, Florida, United States

Colonnades at Baptist

🇺🇸

Jackson, Mississippi, United States

Prime Imaging (Chattanooga Outpatient Center)

🇺🇸

Chattanooga, Tennessee, United States

Royal Adelaide Hospital, Department of Gastroenterology and Hepatology

🇦🇺

Adelaide, South Australia, Australia

University Health Network (UHN) - Toronto General Hospital - Toronto Centre for Liver Disease (TCLD)

🇨🇦

Toronto, Ontario, Canada

University of Toronto - Toronto General Hospital

🇨🇦

Toronto, Ontario, Canada

Lady Davis Carmel Medical Center

🇮🇱

Haifa, Israel

Tampa General Medical Group

🇺🇸

Tampa, Florida, United States

Invision Imaging

🇺🇸

Honolulu, Hawaii, United States

Ochsner Medical Center

🇺🇸

New Orleans, Louisiana, United States

Centrum Badan Klinicznych PI-House Sp. z o.o.

🇵🇱

Gdansk, Poland

Synexus Polska Sp. z o. o. Oddzial w Warszawie

🇵🇱

Warszawa, Poland

National Cheng-Kung University Hospital

🇨🇳

Tainan, Taiwan

Synexus Polska Sp. z o.o. Oddzial w Gdansku

🇵🇱

Gdansk, Poland

Silmedic Sp. z o.o. Oddzial w Katowicach

🇵🇱

Katowice, Poland

Synexus Polska Sp. z o.o Oddzial w Poznaniu

🇵🇱

Poznan, Poland

False Creek Healthcare Centre

🇨🇦

Vancouver, British Columbia, Canada

Taipei Veterans General Hospital

🇨🇳

Taipei, Taiwan

ClinicMed Badurski i wspolnicy Spolka Jawna

🇵🇱

Bialystok, Poland

Chung-Ho Memorial Hospital, Kaohsiung Medical University

🇨🇳

Kaohsiung, Taiwan

LAIR Centre

🇨🇦

Vancouver, British Columbia, Canada

West Coast Medical Imaging

🇨🇦

Victoria, British Columbia, Canada

Dr TG Elliott Inc - BC Diabetes

🇨🇦

Vancouver, British Columbia, Canada

Bioclinica Research

🇺🇸

Orlando, Florida, United States

East-West Medical Research Institute

🇺🇸

Honolulu, Hawaii, United States

Tulane University Health Sciences Center

🇺🇸

New Orleans, Louisiana, United States

University of South Florida

🇺🇸

Tampa, Florida, United States

University of Michigan

🇺🇸

Ann Arbor, Michigan, United States

The University of North Carolina at Chapel Hill, Biomedical Research Imaging Center (MRI Facility)

🇺🇸

Chapel Hill, North Carolina, United States

PMG Research, Inc.

🇺🇸

Winston-Salem, North Carolina, United States

Touchstone

🇺🇸

Austin, Texas, United States

Mayo Clinic- Main Campus

🇺🇸

Rochester, Minnesota, United States

Investigational Drug Service, University of North Carolina Hospitals

🇺🇸

Chapel Hill, North Carolina, United States

The University of NC at Chapel Hill, Clinical and Translational Research Center (CTRC)

🇺🇸

Chapel Hill, North Carolina, United States

National Clinical Research - Richmond, Inc.

🇺🇸

Richmond, Virginia, United States

© Copyright 2025. All Rights Reserved by MedPath