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Interventional, randomised, partial double-blind, placebo- and positive controlled, multiple-dose, 4-way-cross-over trial Investigating the effect of arimoclomol on cardiac repolarization in healthy men.

Completed
Conditions
protein aggregation and protein misfolding diseases (lysosomal storage diseases and neuromuscular disorders such as ALS
Registration Number
NL-OMON49378
Lead Sponsor
Orphazyme A/S
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Not specified
Target Recruitment
32
Inclusion Criteria

1. The subject is able to read and understand the Subject Information Sheet and
Informed Consent Form.
2. The subject has signed the trial-specific Informed Consent Form.
3. The subject is a man
4. The subject must:
a. remain sexually abstinent, when this is in line with his preferred and usual
lifestyle OR
b. engage exclusively in same-sex relationships OR
c. agree to avoid impregnating his partner from the Screening Visit until 2
weeks after the last dose of IMP, AND
d. agree to use highly effective contraception methods as described in Appendix
4 from the Screening Visit until 2 weeks after dosing if his female partner is
of childbearing potential
e. not donate sperm until *3 months after the last dose of IMP

Exclusion Criteria

1. The subject has taken any prescription or non-prescription medication <1
week prior to the first IMP dosing or *5 half-lives prior to the Screening
Visit for any medication taken.
2. The subject has significant alcohol consumption, defined as an alcohol
intake >21 units per week, or substance use (excluding nicotine or caffeine)
deemed significant by the investigator, or a history of substance abuse (DSM-5®
criteria) <12 months prior to the Screening Visit. A unit of alcohol is defined
as 250 mL of lager/beer, 100 mL of wine, or 25 mL of spirits
3. The subject has taken any investigational medicinal product within 3 months
prior to the first IMP dosing.
4. The subject has taken any nutritional or dietary supplements, herbal
preparations, or vitamins within 7 days prior to the first IMP dosing.
5. The subject has previously been dosed with arimoclomol.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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