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A Double-Blinded Study to Evaluate the Safety, Tolerability, and Efficacy of BMS-986020 Versus Placebo in Diffuse Cutaneous Systemic Sclerosis (dcSSc)

Phase 2
Withdrawn
Conditions
Scleroderma
Interventions
Other: Placebo
Registration Number
NCT02588625
Lead Sponsor
Bristol-Myers Squibb
Brief Summary

This is a two part study.

The purpose of Part A is to determine if BMS-986020 is effective in treatment of diffuse cutaneous systemic sclerosis using one dose of BMS-986020.

The purpose of Part B is to determine if BMS-986020 is effective in treatment of diffuse cutaneous systemic sclerosis using two different doses of BMS-986020.

Detailed Description

Not available

Recruitment & Eligibility

Status
WITHDRAWN
Sex
All
Target Recruitment
Not specified
Inclusion Criteria
  • Diagnosis of diffuse cutaneous systemic sclerosis for 60 months or less
  • Men and women ≥ 18 years of age
  • Ability to comply with birth control requirements
  • Certain immunosuppressive agents are permitted
Exclusion Criteria
  • Limited cutaneous systemic sclerosis or sine scleroderma
  • Active ulcers on fingers
  • Pulmonary arterial hypertension
  • Any gastrointestinal surgery that may impact absorption of study drug

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Part A - BMS-986020BMS-986020BMS-986020 or Placebo tablets specified dose on specified days
Part A - BMS-986020PlaceboBMS-986020 or Placebo tablets specified dose on specified days
Part B - BMS-986020BMS-986020BMS-986020 or Placebo tablets specified dose on specified days
Part B - BMS-986020PlaceboBMS-986020 or Placebo tablets specified dose on specified days
Primary Outcome Measures
NameTimeMethod
Part B - Change in modified Rodnan skin score (mRSS)Week 48
Part A - Change in modified Rodnan skin score (mRSS)Week 24
Secondary Outcome Measures
NameTimeMethod
Part A: Change in physical function based on health assessment questionnaire-disability index from baseline at specified timepoints (HAQ-DI)Week 4, 12 and 24
Part A: Tolerability as measured by the frequency of deaths, SAEs, drug related AEs, AEs leading to discontinuation as well as marked abnormalities in clinical laboratory tests, vital sign measurements, ECGs, physical examinationsup to Month 3 of the Follow-Up
Part B: Change in percent predicted forced vital capacityWeek 48
Part B:Proportion of subjects with ≥ 20%, 40%, or 60% change in mRSS from baseline at specified time pointsWeek 4, 12, 24, 36, and 48
Part B: Proportion of subjects with > 10% absolute decline in % FVCWeek 48
Part B:Proportion of subjects with % FVC change > 0Week 48
Part B: Change in quantitative lung fibrosis (QLF) score on High resolution CT (HRCT) from baseline at specified time pointsWeek 48
Part B: Change in health-related quality of life (HRQOL) using Patient Reported Outcomes Measurement Information System (PROMIS)-29 score from baseline at specified time pointsWeek 4, 12, 24, 36, and 48
Part A: Proportion of subjects with ≥ 20%, 40%, or 60% change in mRSS from baseline at specified time pointsWeek 4, 12 and 24
Part A: Change in physician's global assessment on a visual analog scale (VAS) from baseline at specified time pointsWeek 4, 12 and 24
Part A: Change in percent predicted forced vital capacity (FVC) from baseline at specified time pointsWeek 4, 12 and 24
Part A: Change in subject's global assessment on a visual analog scale (VAS) from baseline at specified time pointsWeek 4, 12 and 24
Part A: Safety as measured by the frequency of deaths, SAEs, drug related AEs, AEs leading to discontinuation as well as marked abnormalities in clinical laboratory tests, vital sign measurements, ECGs, physical examinationsup to Month 3 of the Follow-Up

Serious adverse event (SAE), Adverse event (AE)

Part B: Change in physical function based on health assessment questionnaire-disability index (HAQ-DI)Week 48
Part B: Change in subject's global assessment on a visual analog scale (VAS) from baseline at specified time pointsWeek 4, 12, 24, 36, and 48
Part B: Change in physician's global assessment on a visual analog scale (VAS) from baseline at specified time pointsWeek 4, 12, 24, 36, and 48
Part B: Safety as measured by the frequency of deaths, SAEs, drug related AEs, AEs leading to discontinuation as well as marked abnormalities in clinical laboratory tests, vital sign measurements, ECGs, physical examinationsup to Month 3 of the Follow-Up
Part B: Tolerability as measured by the frequency of deaths, SAEs, drug related AEs, AEs leading to discontinuation as well as marked abnormalities in clinical laboratory tests, vital sign measurements, ECGs, physical examinationsup to Month 3 of the Follow-Up

Trial Locations

Locations (1)

Local Institution

🇬🇧

London, Greater London, United Kingdom

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