CRD007 for the Treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy and Symptomatic Carriers
Phase 2
Completed
- Conditions
- Becker Muscular DystrophyDuchenne Muscular Dystrophy
- Interventions
- Registration Number
- NCT01540604
- Lead Sponsor
- RSPR Pharma AB
- Brief Summary
This is an investigation of the efficacy and safety of CRD007 in Duchenne Muscular Dystrophy (DMD), Becker Muscular Dystrophy (BMD) and symptomatic carriers.
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- COMPLETED
- Sex
- All
- Target Recruitment
- Not specified
Inclusion Criteria
- Documented diagnosis of dystrophinopathy
Exclusion Criteria
- Severe functional impairment
Study & Design
- Study Type
- INTERVENTIONAL
- Study Design
- Not specified
- Arm && Interventions
Group Intervention Description CRD007 10 mg tablet CRD007 -
- Primary Outcome Measures
Name Time Method
- Secondary Outcome Measures
Name Time Method
Related Research Topics
Explore scientific publications, clinical data analysis, treatment approaches, and expert-compiled information related to the mechanisms and outcomes of this trial. Click any topic for comprehensive research insights.
What molecular mechanisms does CRD007 target in DMD and BMD pathophysiology?
How does CRD007 compare to corticosteroids in DMD/BMD treatment efficacy and safety?
Which biomarkers are used for patient selection in RSPR Pharma's CRD007 DMD/BMD trial?
What adverse events are associated with CRD007 in DMD/BMD phase 2 trials?
Are there combination therapies involving CRD007 for DMD/BMD being investigated by RSPR Pharma AB?