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Study of MEDI 507 in the Treatment of Pediatric Patients

Phase 1
Completed
Conditions
Graft Versus Host Disease
Interventions
Registration Number
NCT00813618
Lead Sponsor
MedImmune LLC
Brief Summary

To assess the safety of escalating dose levels of MEDI-507 in pediatric stem cell and bone marrow allograft recipients who have at least Grade II GvHD.

Detailed Description

This is a Phase I, open-label dose escalation trial of MEDI-507 in pediatric SCT and BMT recipients with at least Grade II acute GvHD. All patients will receive steroid therapy and MEDI-507 for treatment of GvHD

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
10
Inclusion Criteria
  • Allogeneic BMT or SCT recipients
  • Acute GvHD of at least Grade II severity
  • Age 2 to 17 years
  • Evidence of engraftment (ANC over 500 cells/mm3 on two consecutive days within seven days before study entry)
  • Receipt of GvHD prophylaxis regimen including methotrexate, tacrolimus or cyclosporine
  • Receipt of at least 2 mg/kg of methylprednisolone (or equivalent corticosteroid) between eight and 24 hours prior to the first MEDI-507 dose for GvHD treatment
  • Both males and females are eligible, but sexually active females at risk of pregnancy of childbearing potential must agree to use an effective method of avoiding pregnancy (which includes oral or implanted contraceptives, IUD, female condom, diaphragm with spermicide, cervical cap, abstinence, use of a condom by the sexual partner or sterile sexual partner) beginning 30 days before the first study infusion and continuing through 60 days after the final study infusion.
Exclusion Criteria
  • Treatment of acute GvHD with methylprednisolone (or equivalent corticosteroid) at a total dose exceeding 14 mg/kg (or equivalent) over a seven day period (for example, 2 mg/kg/day for seven days)
  • Previous receipt of MEDI 507
  • Previous treatment with any anti-T cell monoclonal antibodies, such as OKT3, daclizumab (Zenapax), or basiliximab (Simulect)
  • Treatment with anti-thymocyte globulin (ATG, ATGAM or others) within 14 days
  • More than one allogeneic bone marrow or hematopoietic stem cell allograft
  • Use of other investigational agents within 30 days (this does not include the use of licensed agents for indications not listed in the package insert) or current participation in a research protocol in which an investigational agent was administered
  • Any of the following clinical settings or diagnoses:
  • documented or presumed significant active infection
  • pregnancy or nursing mother
  • evidence of infection with HIV-1, hepatitis B or C virus
  • hemodialysis or chronic peritoneal dialysis
  • use of a ventilator
  • chronic GvHD
  • active veno-occlusive disease of the liver
  • moribund patient

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
1MEDI-507MEDI-507
2MEDI-507MEDI-507
3MEDI-507MEDI-507
Primary Outcome Measures
NameTimeMethod
Safety assessment of escalating dose levels of MEDI-507 in pediatric stell scell (SCT) and bone marrow (BMT) allograft recipients who have at least Grade II Graft-versus-Host Disease (GvHD).Through Study Day 44
Secondary Outcome Measures
NameTimeMethod
Evaluate the serum concentrations and pharmacokinetics (PK) of MEDI 507 and pharmacodynamic effects of MEDI-507 on the absolute lymphocyte count and dynamics of lymphocyte phenotypes.Through Study Day 364

Trial Locations

Locations (6)

Children's Hospital of Orange County

🇺🇸

Orange, California, United States

Children's Hospital

🇺🇸

Birmingham, Alabama, United States

Hackensack U. Medical Center

🇺🇸

Hackensack, New Jersey, United States

Univ. of Michigan Medical Center

🇺🇸

Ann Arbor, Michigan, United States

Children's Memorial Hospital

🇺🇸

Chicago, Illinois, United States

The Children's Hosp. of Phila., Abramson Ped. Research Center

🇺🇸

Philadelphia, Pennsylvania, United States

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