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Observational Study for the Evaluation of Incidence of Familial AML/MDSs in Patients With Myeloid Neoplasms

Recruiting
Conditions
Acute Myeloid Leukemia
Familial Acute Myeloid Leukemia
Myelodysplastic Syndromes
Registration Number
NCT04460950
Lead Sponsor
Gruppo Italiano Malattie EMatologiche dell'Adulto
Brief Summary

Observational study aimed at evaluating the incidence of familial AML/MDSs in patients with de novo MDSs or AML with almost one relative affected by hematologic neoplasms and/or other cancers at young age (\< 40 years)

Detailed Description

This is a multicenter, retrospective and prospective, observational study aims to collect clinical information on patients with familial AML/MDSs from January 2014 to December 2022. No intervention is expected.

The purpose of this study is to identify and characterize the patients with familial MDSs or AML (i.e. with relatives affected by hematologic neoplasms and/or other cancers at young age (\< 40 years)) or presence of signs, symptoms or laboratory tests compatible with one of the known syndromes with germinal susceptibility to AML/MDSs.

In order to estimate the incidence of familial AML/MDSs, a survey will be sent every year to all participating sites to collect only the number of the all diagnosis of AML/MDS. All patients will be followed until December 2023 in order to have at least 1 year of observation.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
237
Inclusion Criteria
  • Patient age > 18 years old
  • Diagnosis of AML or MDSs from January 2014 to December 2022
  • Suspected familiarity for myeloid neoplasm: at least one family member of first or second degree affected by myeloid neoplasm or other hematological malignancy, or by solid tumors with onset at age < 40 years or presence of signs, symptoms or laboratory tests compatible with one of the known syndromes with germinal susceptibility to AML/MDSs
  • Signed written informed consent according to ICH/EU/GCP and national local laws.
Exclusion Criteria
  • none

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Incidence of familial AML/MDSsat 1 year

Evaluation of incidence of familial AML/MDSs in patients with de novo MDSs or AML with almost one relative affected by hematologic neoplasms and/or other cancers at young age (\< 40 years). The incidence of familial AML/MDSs will be evaluated by means of number of diagnosis of familial AML/MDSs on the number of all diagnosis of AML/MDS between January 2014 and December 2022.

Secondary Outcome Measures
NameTimeMethod
Hematological characteristics of familial AML/MDSsat 1 year

Evaluation of hematological characteristics of patients with familial AML/MDS.

Standardized Mortality Ratio (SMR)at 1 year

SMR to compare the survival risk in patients with familial AML/MDS with the risk in the Italian general population

Distribution of familial hematologic neoplasms and/or other cancersat 1 year

Type and rate of familial hematologic neoplasms and/or other cancers

Incidence of transplantationat 1 year

Outcome of transplant in patients with familial AML/MDS

Survival Distributionat 1 year

Overall Survival (OS) and Progression Free Survival (PFS)

Trial Locations

Locations (27)

Fondazione Policlinico Universitario Agostino Gemelli Irccs - Roma - Area Ematologica

🇮🇹

Roma, Italy

Asst Grande Ospedale Metropolitano Niguarda - Milano - Sc Ematologia

🇮🇹

Milano, Italy

Aou Di Bologna - Policlinico S. Orsola-Malpighi - Uoc Ematologia

🇮🇹

Bologna, Italy

Aou Ospedali Riuniti - Foggia - Uoc Ematologia

🇮🇹

Foggia, Italy

Ao Di Rilievo Nazionale E Di Alta Specialità "San Giuseppe Moscati" - Avellino - Uoc Ematologia Con Unità Di Trapianto

🇮🇹

Avellino, Italy

Ao Brotzu, Presidio Ospedaliero A. Businco - Cagliari - Sc Ematologia E Ctmo

🇮🇹

Cagliari, Italy

Ao Ospedali Riuniti "Papardo Piemonte" - Po Papardo - Messina - Sc Ematologia

🇮🇹

Messina, Italy

Aon Ss. Antonio E Biagio E C. Arrigo - Alessandria - Soc Ematologia

🇮🇹

Alessandria, Italy

Asl Lecce, Ospedale 'V. Fazzi' - Uo Ematologia

🇮🇹

Lecce, Italy

Aou Città Della Salute E Della Scienza, Ospedale S. Giovanni Battista Molinette - Torino - Sc Ematologia - Università Degli Studi Di Torino

🇮🇹

Torino, Italy

Ao Di Perugia, Ospedale S. Maria Della Misericordia - Ematologia E Trapianto Midollo Osseo

🇮🇹

Perugia, Italy

Aou Pisana - Uo Ematologia Universitaria

🇮🇹

Pisa, Italy

Aou Di Parma - Sc Ematologia E Centro Trapianti Midollo Osseo

🇮🇹

Parma, Italy

Ausl Della Romagna, Ospedale "Infermi" - Rimini - Uo Ematologia

🇮🇹

Rimini, Italy

Asui Di Udine - Presidio Ospedaliero "Santa Maria Della Misericordia" - Clinica Ematologica

🇮🇹

Udine, Italy

Aou Ospedali Riuniti "Umberto I - G.M. Lancisi - G. Salesi"- Ancona - Sod Clinica Ematologica

🇮🇹

Ancona, Italy

Asl Caserta, Presidio Ospedaliero S.G.Moscati - Aversa - Uo Oncoematologia

🇮🇹

Aversa, Italy

Asst Degli Spedali Civili Di Brescia - Uo Ematologia

🇮🇹

Brescia, Italy

Fondazione Irccs Ca' Granda, Ospedale Maggiore Policlinico - Milano - Ematologia - Padiglione Marcora

🇮🇹

Milano, Italy

Asst Degli Spedali Civili Di Brescia - Ssvd Centro Trapianti Midollo Per Adulti - Cattedra Di Ematologia

🇮🇹

Brescia, Italy

Aou San Luigi Gonzaga - Orbassano - Scdu Ematologia Generale E Oncoematologia

🇮🇹

Orbassano, Italy

Asl Salerno, Presidio Ospedaliero Tortora Pagani - Ematologia

🇮🇹

Pagani, Italy

Aou Policlinico P. Giaccone - Palermo - Uo Ematologia

🇮🇹

Palermo, Italy

Ausl Di Reggio Emilia - Arcispedale Santa Maria Nuova, Irccs - Sc Ematologia

🇮🇹

Reggio Emilia, Italy

Asl Roma 2, Ospedale S. Eugenio- Ospedale S.Eugenio - Uoc Ematologia

🇮🇹

Roma, Italy

Ente Ecclesiastico Casa Sollievo Della Sofferenza - San Giovanni Rotondo - Ematologia

🇮🇹

San Giovanni Rotondo, Italy

Aou Di Sassari - Cliniche Universitarie - Stabilimento Cliniche Di San Pietro - Uoc Ematologia

🇮🇹

Sassari, Italy

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