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Efficacy and Safety of Adipose Stem Cells to Treat Complex Perianal Fistulas Not Associated to Crohn´s Disease

Phase 3
Completed
Conditions
Anal Fistula
Interventions
Drug: ASCs (Cx401, company code)
Registration Number
NCT00475410
Lead Sponsor
Tigenix S.A.U.
Brief Summary

Anal fistula is defined as an abnormal communication between the anal canal and the perianal skin. Adipose-derived stem cells are a new therapy for the closure of these fistulas. This study will test the safety and efficacy of ASCs (adipose stem cells) in the treatment of patients without Crohn´s disease.

Detailed Description

Perianal fistula accounts for 10% to 30% of coloproctological surgical procedures. Currently accepted conventional treatment is surgery intended to treat the tracts using different technical options. This surgery usually has a highly bothersome postoperative period and may involve two major complications: anal incontinence and recurrence. The biological properties of stem cells derived from adult tissues make them adequate candidates for the treatment of diseases in which tissues are damaged or the healing process is altered. This study will compare the efficacy of ASCs versus ASCs plus Fibrin adhesive versus Fibrin adhesive alone for closure of complex perianal fistulas not associated to Inflammatory Bowel Disease. Fistula closure is defined as absence of suppuration and re-epithelization of the external opening in the clinical evaluation and absence of collections \>2 cm directly related to the fistula tract treated, as measured by MRI

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
214
Inclusion Criteria
  1. Patient with a complex perianal fistula. A complex perianal fistula must meet one of the following:

    • No fistula tract is palpated under the perianal skin or tract parallel to the rectum on examination with a stylet.
    • Associated anal incontinence in transsphincteric fistulas.
    • Risk factors for anal incontinence.
    • At least one prior surgery for a fistulous disease.
    • Suprasphincteric tracts shown by an image test.
  2. Women of childbearing age should have a negative serum or urine pregnancy test (sensitive to 25IU of hCG) and not be lactating before study entry. Both men and women should use adequate birth control methods as defined by the investigator.

  3. Seton presence is allowed at the time of study entry and until cells (in groups receiving ASCs) or Fibrin adhesive are implanted.

  4. No condition that may prevent the patient from following the study procedures until 26 weeks of follow-up are completed is foreseen.

  5. Patient should give his/her signed, written informed consent. -

Exclusion Criteria
  1. Patient has been diagnosed with IBD

  2. Patient has a rectovaginal fistula

  3. Patient is pregnant or lactating woman

  4. Patient has acute sepsis at the time of study entry

  5. A liposuction to draw at least 100 cc of fat from the abdominal wall is not technically feasible.

  6. Patient needs surgery in the perianal region for reasons other than fistulas

  7. Presence of two or more complex perianal fistulas

  8. Patient has collections > 2 cm in MRI. If such collections exist, the surgeon may perform a complete toilette of the area.

  9. Patient is allergic to local anesthetics or Gadolinium (MRI contrast agent).

  10. MRI is not technically feasible.

  11. Patient has abused alcohol or other addictive substances within 6 months of study entry.

  12. Patient has active or latent infection by HIV, HBV or HCV.

  13. Patient has undergone major surgery or sustained a severe trauma, in the investigator's judgment, within 28 days of recruitment.

  14. Patient is receiving or has received immunomodulatory treatment for reasons other than the fistula within 6 months of study entry.

  15. Patient has a malignant tumour, except for basal or squamous cell carcinoma of the skin, or has a prior history of a malignant tumour, except if the tumour has been in remission for at least the past 5 years.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
ASCsASCs (Cx401, company code)-
ASCs+fibrin glueASCs (Cx401, company code)-
ASCs+fibrin glueFibrin adhesive-
Fibrin glueFibrin adhesive-
Primary Outcome Measures
NameTimeMethod
Closure of fistulas defined as absence of suppuration and re-epithelization of the external opening and absence of collections>2 cm directly related to the fistula tract treated, as measured by MRI (healing)weeks 1, 4, 12 and 24. Week 26 in patients with a second dose
Secondary Outcome Measures
NameTimeMethod
• Clinical complexity of fistula (complexity of fistula score) • Safety: Cumulative incidence of adverse effects. • Quality of life (SF-36 score) • Degree of anal incontinence (Wexner incontinence score)weeks 1, 4, 12 and 24. Week 26 in patients with a second dose

Trial Locations

Locations (10)

Lozano Blesa Clinical Hospital

🇪🇸

Zaragoza, Aragon, Spain

12 De Octubre University Hospital

🇪🇸

Madrid, Spain

Universitary Clinical Surgery

🇩🇪

Mannheim, Germany

Virgen Del Camino Hospital

🇪🇸

Pamplona, Navarra, Spain

Gregorio Marañon University Hospital

🇪🇸

Madrid, Spain

La Paz University Hospital

🇪🇸

Madrid, Spain

San Carlos Clinical Hospital

🇪🇸

Madrid, Spain

Universitary General Hospital

🇪🇸

Valencia, Spain

Mutua de Terrasa Hospital

🇪🇸

Tarrasa, Tarragona, Spain

John Radcliff Hospital

🇬🇧

Oxford, Oxfordshire, United Kingdom

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