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Development of the Virtual Unified Huntington's Disease Rating Scale

Completed
Conditions
Huntington Disease
Registration Number
NCT05748288
Lead Sponsor
Huntington Study Group
Brief Summary

The Huntington Study Group currently holds the registered trademark for the Unified Huntington's Disease Rating Scale. The UHDRS® is a research tool which has been developed by the HSG to provide a uniform assessment of the clinical features and course of HD. The UHDRS® has undergone extensive reliability and validity testing and has been used as a major outcome measure by the HSG in controlled clinical trials.

The purpose of this research study is to determine if a standard HD assessment (the UHDRS®) is as reliable when conducted virtually as it is when conducted at an in-person visit (vUHDRS)

Detailed Description

The UHDRS® is comprised of five components:

Motor Assessment Cognitive Assessment Behavioral Assessment Independence Scale Functional Assessment Total Functional Capacity (TFC)

This observational study seeks to characterize and compare in-person versus TeleVisits. Fifty percent of participants will be provided computer equipment for their remote assessment and the other 50% will use their existing home-based equipment for this purpose.

TeleVisit is a method for participants to connect to the research study team remotely, via video and audio connection either on their computer or iPad.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
60
Inclusion Criteria
  1. Are male or female and 18 years or older at the time of signing the informed consent
  2. Are able and willing to provide written informed consent
  3. Are English speaking
  4. Currently exhibit motor signs and symptoms of Huntington Disease
  5. Have a genetic diagnosis of HD with an expanded CAG repeat (greater than or equal to 36) in the huntingtin (HTT) gene at or before Screening/Baseline visit from a validated laboratory
  6. Have oral and written communication skills that are sufficient/adequate to complete all cognitive assessments
  7. Are ambulatory, but may use any assistive device or require help
  8. Are able to maintain stable medications for 30 days prior to Screening/Baseline through the second in-person visit
  9. Have a study partner available to help with technology and set-up and to attend all study visits
  10. Have the ability to get email on the device used for the study
Exclusion Criteria
  1. Are unable to complete cognitive or functional assessments due to inability to communicate
  2. Are unable to obtain satisfactory internet connection (i.e., internet connection must be stable and support the audio and video needs without freezing or interruption) at home or designated location, even with provided equipment
  3. Have inadequate space at home to assess 10 steps for gait assessments
  4. Have active suicidal ideation endorsed with a score of 4 (Active Suicidal Ideation with Some Intent to Act, without Specific Plan) if the ideation occurred within 1 year of Screening or 5 (Active Suicidal Ideation with Specific Plan and Intent) on the C-SSRS if the attempt or acts were performed within 1 year of Screening/Baseline, or participants who, in the opinion of the Site Investigator (SI), present a serious risk of suicide.
  5. Have received gene therapy or an investigational drug within 30 days or 5 half-lives, whichever is longer, of the Screening/Baseline visit or plan to use an investigational drug during this study.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Unified Huntington's Disease Rating Scalefrom the TeleVisit to the second In-Person Visit, up to 6 weeks

Total Functional Capacity:

Minimum Score = 0 Maximum Score = 13 Greater scores indicate higher functioning

United Huntington's Disease Rating Scalefrom TeleVisit to the second In-Person Visit, up to 6 weeks

Functional Assessment Minimum Score = 0 Maximum Score = 25 Higher scores indicate greater functionality

Secondary Outcome Measures
NameTimeMethod
virtual Unified Huntington's Disease Rating Scalefrom first In-Person visit through Follow-Up, up to 6 weeks

Feasibility of completing the vUHDRS™ using participant personal equipment vs. Huntington Study Group provided equipment.

Unified Huntington's Disease Rating Scalefrom the TeleVisit to the second In-Person Visit, up to 6 weeks

Behavior minimum = 0, maximum = 88 Higher scores indicate more behavioral symptoms

Safety of conducting the UHDRS remotelyfrom initial informed consent and continue until 30 days following the Participant's completion of the study

Reported adverse events

Trial Locations

Locations (17)

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Indiana University School of Medicine

🇺🇸

Indianapolis, Indiana, United States

Ohio State University Medical Center

🇺🇸

Columbus, Ohio, United States

University of Vermont Medical Center

🇺🇸

Burlington, Vermont, United States

University of Texas, Health Science Center

🇺🇸

Houston, Texas, United States

University of Alabama at Birmingham, Department of Neurology

🇺🇸

Birmingham, Alabama, United States

University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

University of South Florida, Huntington Disease Center of Excellence

🇺🇸

Tampa, Florida, United States

University of California, San Diego

🇺🇸

La Jolla, California, United States

Hereditary Neurological Disease Center

🇺🇸

Wichita, Kansas, United States

Northwestern University Medical Center, Department of Neurology

🇺🇸

Chicago, Illinois, United States

Washington University

🇺🇸

Saint Louis, Missouri, United States

Massachusetts General Hospital

🇺🇸

Charlestown, Massachusetts, United States

Sanford Brain and Spine Clinic

🇺🇸

Fargo, North Dakota, United States

Georgetown University

🇺🇸

Washington, District of Columbia, United States

Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

University of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

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