MedPath

Bone Marrow Aspirate Concentrate (BMAC) for Treatment of Critical Limb Ischemia (CLI)

Phase 3
Completed
Conditions
Critical Limb Ischemia
Interventions
Device: Placebo injection
Device: BMAC injection
Registration Number
NCT01245335
Lead Sponsor
Harvest Technologies
Brief Summary

Critical Limb Ischemia prevents the legs and feet from receiving oxygen and nutrients needed for proper function. This severe lack of blood flow can lead to painful legs while walking or at rest and can result in foot sores, ulcers, gangrene, and even amputation. The purpose of this study is to determine if injections of concentrated bone marrow into damaged tissues will result in improved blood flow. If successful, this treatment could improve blood flow to the lower limb, reduce pain, and reduce the frequency of limb amputations.

Detailed Description

Bone marrow aspirate is collected and processed by centrifugation to remove red blood cells. The resulting concentrate of cells is injected into ischemic tissues of the lower limb. The purpose of this study is to determine if injections of concentrated bone marrow nucleated cells into ischemic tissues will result in vasculogenesis.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
97
Inclusion Criteria
  • Patient has Peripheral Arterial Occlusive Disease (PAOD) with clinical Rutherford Category 5 disease, as defined in the reporting standards adopted by the Society of Vascular Surgeons(table 1); Minor Tissue loss-focal gangrene with diffuse pedal ischemia

  • Patient meets at least one of the following diagnostic criteria in the study limb:

    • Ankle artery occlusion pressure absolute ≤60 mmHg or ABI ≤0.6
    • Toe artery occlusive pressure < 50mm Hg or TBI ≤0.6
  • There is no reasonable open surgical or endovascular revascularization option as determined by the treating vascular specialist. Factors that may contribute to the determination of inoperability may include:

    • Anatomical considerations
  • No outflow targets

  • No appropriate conduit (i.e. vein for bypass)

  • Long segment occlusions or calcified lesions that predict poor outcome with endovascular approaches.

    • High risk medical conditions i.e. Unstable cardiac disease.
    • History of prior failed revascularization attempts
  • The Patient's case was reviewed at the treating institution's Multidisciplinary Vascular Conference where the patient's status as a poor candidate for conventional therapies was confirmed.

  • Age ≥18 years and ability to understand the planned treatment

  • Subject has read and signed the IRB approved Informed Consent form

  • Patients for whom the following medication(s) is prescribed must have a one month stable baseline therapy prior to enrollment: Plavix/asprin therapy, anticoagulation therapy, cholesterol lowering agent, and or blood pressure medication. If any of these medications are not prescribed notation of the reason for omission is to be provided.

  • Hematocrit ≥ 28.0%, White Blood Cell count ≤ 14,000, Platelet count ≥ 50,000, Creatinine ≤ 2.5 mg / dL, INR ≤ 1.6 unless on Coumadin, or PTT <1.5 x control (to avoid bleeding complications) Patients on Coumadin will be corrected prior to the procedure and must have an INR<1.6 at the time of randomization/surgery.

Exclusion Criteria
  • Life expectancy <6 months due to concomitant illnesses

  • History of bone marrow diseases (especially NHL, MDS) that prohibit transplantation

  • Terminal renal failure with existing dependence on dialysis or serum creatinine >2.5 mg/dL

  • Known active malignancy or results outside of normal limits from the following tests: PAP, Chest X-ray, PSA, Mammogram, Hemocult unless follow-up studies reveal patient to be cancer free.

  • Poorly controlled diabetes mellitus (HgbA1C>10%)

  • Medical risk that precludes anesthesia (conscious sedation), or ASA Class 5

  • Life-threatening complications of the ischemia necessitating immediate amputation

  • Uncorrected occlusion of the common or external iliac artery on index side

  • Absence of any pulsatile Doppler flow below the ankle.

  • Extensive necrosis of the index limb or other conditions that make amputation inevitable (Rutherford Category 6).

  • Ulceration with exposed bone proximal to the distal metatarsal heads (ie. heel or mid foot)

  • Active clinical infection or infection being treated by antibiotics within one week of enrollment

  • Treatment with immunosuppressant drugs (including Prednisone > 5 mg per day).

  • Female who is pregnant or nursing, or of child bearing potential and is not using a reliable birth control method.

  • Underwent a major open cardiovascular surgical procedure (carotid endarterectomy, arterial aneurysm or bypass surgery, or coronary artery bypass surgery) or a myocardial infarction within the 3 months prior to randomization

  • Underwent a successful or partially successful endovascular intervention for peripheral arterial occlusive disease. (ie. Aorta, iliac, femoral, popliteal, or tibial artery angioplasty, stenting, or atherectomy) within the prior 3 months.

  • Endovascular coronary intervention (ie. Angioplasty, atherectomy, stenting) within 1 month prior to randomization.

  • Underwent a failed attempt for endovascular revascularization during the prior 1 month. For the purpose of this exclusion criteria an endovascular procedure is considered a failure if:

    1. The procedure is diagnostic only with no intervention performed, (for example in the case where wire crossing can not be obtained).
    2. The treated artery recoils, thromboses, or dissects resulting in occlusion of the treated arterial segment, documented by intraoperative imaging. Note that endovascular procedures with suboptimal results but not meeting criteria 1 or 2 above may qualify for inclusion after 3 months as in #16 above.
  • Cerebrovascular accident within 6 months prior to randomization.

  • Treatment with topical growth factors or hyperbaric oxygen (HBO) within 30 days, or systemic growth factor treatment within 6 months of enrollment.

  • Known hypersensitivity to heparin; or history of heparin-induced thrombocytopenia (HIT).

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo InjectionPlacebo injectionInjection of placebo (diluted peripheral blood) into ischemic tissue of the lower extremity
BMAC TreatmentBMAC injectionIntervention- Injection of 40 ml of autologous bone marrow concentrate (BMAC injection) prepared with the SmartPReP2 BMAC System
Primary Outcome Measures
NameTimeMethod
Amputation Free SurvivalSix Months

Survival without a major (above the ankle) amputation

Secondary Outcome Measures
NameTimeMethod
Change In Rutherford ClassificationSix Months

Change in the subjects clinical status as measured by Rutherford Classification

Change in PainSix Months

Change in Subjects perception of pain as measured on a 100 mm visual analog scale

Trial Locations

Locations (34)

Johns Hopkins Hospital

🇺🇸

Baltimore, Maryland, United States

USF / Tampa General

🇺🇸

Tampa, Florida, United States

University of Alabama

🇺🇸

Birmingham, Alabama, United States

Ochsner Clinic

🇺🇸

New Orleans, Louisiana, United States

North Shore-Long Island Jewish

🇺🇸

Lake Success, New York, United States

Regional Infectious Disease and Infusion Ctr

🇺🇸

Lima, Ohio, United States

Florida Hospital - Vascular Institute of Central Florida

🇺🇸

Orlando, Florida, United States

Coastal Vascular & Interventional

🇺🇸

Pensacola, Florida, United States

Kansas City Vascular

🇺🇸

Kansas City, Missouri, United States

Wake Forest Baptist Health

🇺🇸

Winston-Salem, North Carolina, United States

St. Luke's Roosevelt

🇺🇸

New York, New York, United States

Peace Health Southwest Medical Center

🇺🇸

Vancouver, Washington, United States

University of Illinois-Chicago

🇺🇸

Chicago, Illinois, United States

Holy Name Medical Center

🇺🇸

Teaneck, New Jersey, United States

University of North Carolina at Chapel Hill

🇺🇸

Chapel Hill, North Carolina, United States

Baylor Medical Ctr

🇺🇸

Dallas, Texas, United States

University of Oklahoma

🇺🇸

Tulsa, Oklahoma, United States

University of Cincinnati

🇺🇸

Cincinnati, Ohio, United States

Cadence Health, Central DuPage Hospital

🇺🇸

Winfield, Illinois, United States

Tufts Medical Center

🇺🇸

Boston, Massachusetts, United States

Mercy Hospital

🇺🇸

St. Louis, Missouri, United States

Oregon Health Science University

🇺🇸

Portland, Oregon, United States

Charleston Area Medical Center Institute

🇺🇸

Charleston, West Virginia, United States

University of Texas - Houston Medical School

🇺🇸

Houston, Texas, United States

Cooper University Hospital

🇺🇸

Camden, New Jersey, United States

University of Tennessee

🇺🇸

Knoxville, Tennessee, United States

Roper St Francis Medical Center

🇺🇸

Charleston, South Carolina, United States

Greenville Health System

🇺🇸

Greenville, South Carolina, United States

Beth Israel Deaconess

🇺🇸

Boston, Massachusetts, United States

USC Keck School of Medicine

🇺🇸

Los Angeles, California, United States

Medical Center of South Arkansas

🇺🇸

El Dorado, Arkansas, United States

Maine Medical Ctr

🇺🇸

Portland, Maine, United States

Dartmouth Hitchcock Medical Ctr

🇺🇸

Lebanon, New Hampshire, United States

Rhode Island Hospital

🇺🇸

Providence, Rhode Island, United States

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