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A study to monitor safety of Velaglucerase alfa in India

Phase 4
Conditions
Health Condition 1: E752- Other sphingolipidosis
Registration Number
CTRI/2021/07/034906
Lead Sponsor
Shire Human Genetic Therapies Inc
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Open to Recruitment
Sex
Not specified
Target Recruitment
0
Inclusion Criteria

Patients with Gaucher disease prescribed VPRIV according to the investigators judgment and current Indian PI are eligible for this study. Patient or legally authorized representative must provide written informed consent to participate

Exclusion Criteria

Patients will be excluded from this study if the patient met any of the contraindications included

in the current Indian PI for VPRIV

Study & Design

Study Type
PMS
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
To characterize the safety profile of VPRIV using both retrospective and prospective data, when used as standard clinical practice for patients with Gaucher disease in India.Timepoint: 12 months (Throughout the study)
Secondary Outcome Measures
NameTimeMethod
To collect and record genetic mutation data, if available, from patients with Gaucher diseaseTimepoint: 12 Months (Throughout the study);To collect retrospective data on treatment history, effectiveness, and safety data of the previous VPRIV treatmentTimepoint: 12 Months (Throughout the study);To describe effectiveness in patients with Gaucher disease receiving VPRIV using both retrospective and prospective data, when used in standard clinical practice in IndiaTimepoint: 12 Months (Throughout the study)
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