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Study to Evaluate ARO-APOC3 in Adults With Severe Hypertriglyceridemia

Phase 2
Completed
Conditions
Severe Hypertriglyceridemia
Interventions
Drug: Placebo
Registration Number
NCT04720534
Lead Sponsor
Arrowhead Pharmaceuticals
Brief Summary

The purpose of AROAPOC3-2001 is to evaluate the efficacy and safety of ARO-APOC3 in participants with severe hypertriglyceridemia. Participants will receive 2 subcutaneous injections of ARO-APOC3.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
229
Inclusion Criteria
  • Based on medical history, evidence of TG ≥ 500 mg/dL and ≤ 4000 mg/dL at Screening
  • Fasting TG ≥ 500 mg/dL at Screening
  • Willing to follow diet counseling per Investigator judgment based on local standard of care
  • Women of childbearing potential must have a negative pregnancy test, cannot be breastfeeding, and must be willing to use contraception
  • Willing to provide written informed consent and to comply with study requirements
Exclusion Criteria
  • Active pancreatitis within 12 weeks prior to first dose
  • Any planned bariatric surgery or similar procedures to induce weight loss from consent to end of study
  • Acute coronary syndrome event within 24 weeks of first dose
  • Major surgery within 12 weeks of first dose
  • Planned coronary intervention (e.g., stent placement or heart bypass) or any non-cardiac major surgical procedure throughout the study
  • Uncontrolled hypertension
  • Human immunodeficiency virus (HIV) infection, seropositive for Hepatitis B (HBV), seropositive for Hepatitis C (HCV)
  • Uncontrolled hypothyroidism or hyperthyroidism
  • Hemorrhagic stroke within 24 weeks of first dose
  • Malignancy within the last 2 years prior to date of consent requiring systemic treatment (some exceptions apply)

Note: additional inclusion/exclusion criteria may apply per protocol

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo, Day 1 and Week 12Placebocalculated volume to match active treatment by sc injection
ARO-APOC3 10 mg, Day 1 and Week 12ARO-APOC32 doses of ARO-APOC3 by subcutaneous (sc) injection
ARO-APOC3 50 mg, Day 1 and Week 12ARO-APOC32 doses of ARO-APOC3 by sc injection
ARO-APOC3 25 mg, Day 1 and Week 12ARO-APOC32 doses of ARO-APOC3 by sc injection
Primary Outcome Measures
NameTimeMethod
Percent Change from Baseline in Fasting Triglycerides (TG) at Week 24Baseline, Week 24
Secondary Outcome Measures
NameTimeMethod
Percent Change from Baseline in Fasting Total Apolipoprotein B (ApoB) at Week 24Baseline, Week 24
Percent Change from Baseline in Apolipoprotein (Apo)C-III at Week 24Baseline, Week 24
Percent Change from Baseline in Fasting High-Density Lipoprotein-Cholesterol (HDL-C) at Week 24Baseline, Week 24
Percent Change from Baseline in Fasting Total ApoB Over Time Through Week 48Baseline, up to Week 48
Percent Change from Baseline in Fasting TG Over Time Through Week 48Baseline, up to Week 48
Percent Change from Baseline in ApoC-III Over Time Through Week 48Baseline, up to Week 48
Percent Change from Baseline in Fasting Non-HDL-C Over Time Through Week 48Baseline, up to Week 48
Percent Change from Baseline in Fasting HDL-C Over Time Through Week 48Baseline, up to Week 48
Change from Baseline in Plasma Concentration of ARO-APOC3 Over Time Through Week 48Baseline, up to Week 48
Percent Change from Baseline in Fasting Non-High-Density Lipoprotein-Cholesterol (Non-HDL-C) at Week 24Baseline, Week 24
Percent Change from Baseline in Fasting Low-density Lipoprotein-Cholesterol (LDL-C) Using UltracentrifugationBaseline, Week 24
Percent Change from Baseline in Fasting LDL-C Using Ultracentrifugation Over Time Through Week 48Baseline, up to Week 48
Number of Participants with Adverse Events (AEs) and/or Serious Adverse Events (SAEs) Possibly or Probably Related to Treatmentup to Week 48

Trial Locations

Locations (74)

Westside Medical Associates of Los Angeles

🇺🇸

Beverly Hills, California, United States

Desert Oasis Healthcare (Desert Medical Group, Inc.)

🇺🇸

Palm Springs, California, United States

Preventive Cardiology Inc.

🇺🇸

Boca Raton, Florida, United States

Invesclinic U.S., LLC

🇺🇸

Fort Lauderdale, Florida, United States

Ocean Blue Medical Research Center Inc.

🇺🇸

Miami Springs, Florida, United States

A Positive Research, Inc.

🇺🇸

Miami, Florida, United States

Y&L Advance Health care, Inc. D/B/A Elite Clinical Research

🇺🇸

Miami, Florida, United States

AppleMed Research Group

🇺🇸

Miami, Florida, United States

HeartWell LLP

🇺🇸

Miami, Florida, United States

Progressive Medical Research

🇺🇸

Port Orange, Florida, United States

Scroll for more (64 remaining)
Westside Medical Associates of Los Angeles
🇺🇸Beverly Hills, California, United States

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