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Phase II Study in the Treatment of Patients With Advanced Mucinous Melanoma

Phase 2
Conditions
Advanced Mucosal Melanoma
Interventions
Other: JS001 and Axitinib
Biological: JS001(Toripalimab Injection)
Registration Number
NCT03941795
Lead Sponsor
Peking University Cancer Hospital & Institute
Brief Summary

This is a randomized, controlled, multicenter Phase II clinical study to evaluate the efficacy and safety of toripalimab injection combined with axitinib in the first-line treatment of patients with advanced mucosal melanoma. The target population is the patients with previously untreated, histopathologically confirmed, unresectable or metastatic mucosal melanoma. At the randomization, patients are randomized 1:1:1 into three groups with approximately 33 subjects in each group to receive toripalimab injection plus axitinib, toripalimab injection monotherapy (subjects who meet the criteria after disease progression may cross over to receive toripalimab plus axitinib), or axitinib monotherapy (subjects who meet the criteria after disease progression may cross over to receive toripalimab plus axitinib); when the patient has disease progression or intolerable toxicity, the treatment is terminated, and the survival follow-up will be initiated.

Detailed Description

Not available

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
99
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
CROSSOVER
Arm && Interventions
GroupInterventionDescription
JS001(Toripalimab Injection) Combined With AxitinibJS001 and Axitinib-
Axitinib aloneAxitinib 1 MG [Inlyta]-
JS001 aloneJS001(Toripalimab Injection)-
Primary Outcome Measures
NameTimeMethod
the progression-free survival (PFS)36 months

Progression-free survival (PFS) per RECIST 1.1 criteria: Time from the date of randomization to the first documented disease progression (per RECIST 1.1 criteria), or death from any cause, whichever occurs first.

Secondary Outcome Measures
NameTimeMethod
INV-ORR36 months

INV-ORR in crossover subjects is the number of subjects with DOR of CR or PR based on INV assessment divided by the number of crossover subjects. DOR is defined as the best response recorded as measured by INV from the date of the first crossover dose to the date of objective documentation of progression per RECIST 1.1 or the date of subsequent therapy, including tumor-directed radiotherapy and tumor-directed surgery, whichever occurs first. For subjects without documented progression or subsequent treatment, all available response designations will be assigned to the DOR evaluation. Baseline tumor assessments for crossover subjects are based on the last tumor assessment for monotherapy prior to the combination crossover. Exploratory endpoints will be analyzed at the time of primary endpoint analysis if data are available.

ORR36 months

Objective response rate (ORR) according to RECIST 1.1;

PFS36 months

Progression-free survival (PFS) according to RECIST 1.1;

DOR36 months

Duration of response (DOR) according to RECIST 1.1;

TTR36 months

Time to response (TTR) according to RECIST 1.1;

DCR36 months

Disease control rate (DCR) according to RECIST 1.1;

OS36 months

Overall survival (OS): Time from the date of randomization to death from any cause. Surviving patients as of the date of analysis will be censored at the date of their last contact.

safety: Number of Participants With Abnormal Laboratory Values and/or Adverse Events That Are Related to Treatment36 months

Number of Participants With Abnormal Laboratory Values and/or Adverse Events That Are Related to Treatment.

Trial Locations

Locations (2)

Beijing Cancer Hospital

🇨🇳

Beijing, Beijing, China

Baishen First Hospital of Jilin University

🇨🇳

Shengyang, Liaoning, China

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