Expanded Access to Triheptanoin
- Conditions
- Long Chain Fatty Acid Oxidation Disorders
- Registration Number
- NCT03773770
- Lead Sponsor
- Ultragenyx Pharmaceutical Inc
- Brief Summary
Expanded access may be provided for qualified patients who have limited treatment options and are not eligible for a clinical trial.
- Detailed Description
Long Chain Fatty Acid Oxidation Disorders (LC-FAOD) and other Non-FAOD conditions, where applicable: Expanded access may be available outside of the US in countries prior to approval by the local regulatory agencies.
For full details, please visit the links provided below.
Recruitment & Eligibility
- Status
- AVAILABLE
- Sex
- All
- Target Recruitment
- Not specified
Inclusion Criteria
Not provided
Exclusion Criteria
Not provided
Study & Design
- Study Type
- EXPANDED_ACCESS
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method
- Secondary Outcome Measures
Name Time Method