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The Effect of Treatment With Teriparatide and Zoledronic Acid in Patients With Osteogenesis Imperfecta

Phase 2
Terminated
Conditions
Osteogenesis Imperfecta
Interventions
Other: No active treatment
Registration Number
NCT01679080
Lead Sponsor
University of Aarhus
Brief Summary

Osteogenesis imperfecta (OI) is an inherited disease of the connective tissue. Symptoms are fractures, growth retardation, blue sclera, bad teeth, impaired hearing a.o. The aim of the present study is to investigate the effect of treatment of adult OI patients with bisphosphonate (zoledronic acid), parathyroid hormone (PTH) or placebo on bone mass, fracture risk and quality of life.

The investigators will therefore conduct a double blind, placebo controlled trial, taking genotype and previous antiresorptive therapy into account.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
9
Inclusion Criteria
  • clinical diagnosis of osteogenesis imperfecta
  • BMD<-1.0 or
Exclusion Criteria
  • creatinine clearance <30mL/min
  • treatment with glucocorticoids > 5mg daily during the last 3 months
  • metabolic bone disease or vitamin d deficiency
  • liver or kidney disease
  • contradictions to zoledronic acid or teriparatide
  • increased baseline risk of osteosarcoma

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
No active treatmentNo active treatmentObservation in three years, no treatment
Zolendronic acid, 3 yr + placebo teriparatide, 2 yrZoledronic acidyearly intravenous infusion of 5mg active zoledronic acid in 3 yr
teriparatide 2 yr; active zol in 3rd yrZoledronic aciddaily injection of one dose active teriparatide for two years, active zoledronic acid in year 3.
teriparatide 2 yr; active zol in 3rd yrTeriparatidedaily injection of one dose active teriparatide for two years, active zoledronic acid in year 3.
Primary Outcome Measures
NameTimeMethod
Bone Mineral Density (BMD)Three years

Dual-energy X-ray absorptiometry scans are performed at the lumbar spine, hip and whole body twice yearly. The value of the lumbar BMD is the primary outcome.

Secondary Outcome Measures
NameTimeMethod
Fracture riskThree years

Participants are asked to report fractures throughout the study. Medical examination yearly with a focus on possible new fractures. Columnar x-ray before and after the study investigate new fractures.

Trial Locations

Locations (3)

Department of Endocrinology M

🇩🇰

Odense, Denmark

Department of endocrinology

🇩🇰

Hvidovre, Denmark

Osteoporosis clinic; department of endocrinology and metabolism

🇩🇰

Aarhus, Aarhus C, Denmark

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