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Trial to Assess the Efficacy of EMPAgliflozin and Personalized Dietary Counseling for Kidney STONE Prevention

Phase 3
Not yet recruiting
Conditions
Kidney Stone
Nephrolithiasis
Dietary Exposure
Interventions
Drug: Placebo
Behavioral: Personalized dietary counseling
Behavioral: Generic dietary counseling
Registration Number
NCT06653738
Lead Sponsor
Insel Gruppe AG, University Hospital Bern
Brief Summary

The aim of this randomized trial with a 2-by-2 factorial design is to test the efficacy of the SGLT2 inhibitor empagliflozin and personalized dietary counseling based on 24-hr urine collection results and dietary assessments for kidney stone recurrence prevention in patients with calcium kidney stones.

Study interventions:

* Empagliflozin 25 mg once daily per os for 36 months

* Personalized dietary counseling for 36 months.

Control interventions:

* Placebo once daily per os for 36 months

* Generic dietary counseling for 36 months.

Detailed Description

Background:

Nephrolithiasis is a highly prevalent kidney disorder that causes substantial morbidity, reduced quality of life and enormous healthcare expenditures worldwide. Kidney stones recur frequently, with 10-year recurrence rates of up to 80 %. Existing pharmacological strategies for the prevention of kidney stone recurrence are limited, and dietary counselling practices for patients with kidney stones vary widely. In observational studies and post-hoc analyses of cardiovascular outcome trials, sodium-glucose cotransporter 2 inhibitor (SGLT2i) use was associated with a reduction in kidney stone events in patients with type 2 diabetes. In the recent randomized phase 2 trial SWEETSTONE (NCT04911660), the SGLT2i empagliflozin significantly improved the urinary lithogenic risk profile compared to placebo in non-diabetic patients with calcium kidney stones, by far the most common kidney stone type.

Rationale:

The efficacy of SGLT2is in the prevention of kidney stone recurrence in patients with kidney stones is unknown. Furthermore, the optimal dietary counseling approach for individuals with kidney stones remains unclear.

Objective:

The investigators plan to conduct a 3-year multicentric, double-blind, placebo-controlled factorial trial to assess the efficacy of empagliflozin with either a personalized or generic dietary counselling strategy for recurrence prevention in patients with calcium kidney stones.

Methodology:

The investigators will include 380 adult (≥ 18 years) patients with recurrent (≥ 2 kidney stone episodes in the last 10 years) calcium kidney stones (containing 50% or more of calcium oxalate, calcium phosphate or a mixture of both). Patients with known secondary causes of kidney stones will be excluded. In this randomized trial with a 2-by-2 factorial design, patients will be allocated to either empagliflozin 25 mg or placebo once daily, and to either personalized or generic dietary counselling according to 24-hr urine results. Randomization will be stratified according to the number of kidney stone episodes during the 10 years before enrolment.

The primary endpoint will be radiologic kidney stone recurrence (a composite of stone growth or new stones formed assessed by computed tomography) at 3 years. Secondary endpoints will be symptomatic kidney stone recurrence up to 3 years, and the number of symptomatic recurrences over 3 years. Exploratory endpoints will be changes in blood and urine parameters, vital signs and weight; asymptomatic kidney stone passage; patient-reported pain and quality of life; and kidney stone event-related health care utilization and cost. Safety endpoints assessed will be the frequency of serious adverse events and of pre-defined adverse events of special interest.

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
380
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
FACTORIAL
Arm && Interventions
GroupInterventionDescription
Placebo and personalized dietary counselingPlaceboPlacebo once daily per os and personalized dietary counseling for 3 years
Placebo and personalized dietary counselingPersonalized dietary counselingPlacebo once daily per os and personalized dietary counseling for 3 years
Empagliflozin and generic dietary counselingEmpagliflozin 25 MGEmpagliflozin 25 mg once daily per os and generic dietary counseling for 3 years
Empagliflozin and generic dietary counselingGeneric dietary counselingEmpagliflozin 25 mg once daily per os and generic dietary counseling for 3 years
Placebo and generic dietary counselingPlaceboPlacebo once daily per os and generic dietary counseling for 3 years
Placebo and generic dietary counselingGeneric dietary counselingPlacebo once daily per os and generic dietary counseling for 3 years
Empagliflozin and personalized dietary counselingEmpagliflozin 25 MGEmpagliflozin 25 mg once daily per os and personalized dietary counseling for 3 years
Empagliflozin and personalized dietary counselingPersonalized dietary counselingEmpagliflozin 25 mg once daily per os and personalized dietary counseling for 3 years
Primary Outcome Measures
NameTimeMethod
Number of patients with radiologic stone recurrenceAfter 3 years

Radiological stone recurrence is defined as a new stone formed or enlargement of a preexisting stone (assessed by low-dose CT of the kidney at the end of the study compared to the low-dose CT of the kidney at the baseline visit).

Secondary Outcome Measures
NameTimeMethod
Time to symptomatic kidney stone recurrence up to 3 years (time-to-event)From enrollment to the end of treatment at 3 years

Symptomatic recurrence is defined as the visible passage of a stone with or without accompanying typical symptoms (such as flank or loin pain and hematuria) or as the presence of a symptomatic or asymptomatic stone that was determined to require surgical removal.

Number of symptomatic stone recurrences per patient (cumulative)From enrollment to the end of treatment at 3 years

Symptomatic recurrence is defined as the visible passage of a stone with or without accompanying typical symptoms (such as flank or loin pain and hematuria) or as the presence of a symptomatic or asymptomatic stone that was determined to require surgical removal.

Trial Locations

Locations (21)

Hôpital Tenon

🇫🇷

Paris, France

Charité University Medicine Berlin

🇩🇪

Berlin, Germany

Verona University Hospital

🇮🇹

Verona, Italy

University Hospital Amiens-Picardie

🇫🇷

Amiens, France

Kantonsspital Aarau

🇨🇭

Aarau, Switzerland

Kantonsspital Baden

🇨🇭

Baden, Switzerland

University Hospital Basel

🇨🇭

Basel, Switzerland

Regionalspital Bellinzona e Valli

🇨🇭

Bellinzona, Switzerland

Inselspital Bern

🇨🇭

Bern, Switzerland

Kantonsspital Chur

🇨🇭

Chur, Switzerland

Kantonsspital Fribourg

🇨🇭

Fribourg, Switzerland

University Hospital Geneva (HUG)

🇨🇭

Geneva, Switzerland

Lausanne University Hospital (CHUV)

🇨🇭

Lausanne, Switzerland

Regionalspital Lugano

🇨🇭

Lugano, Switzerland

Kantonsspital Luzern

🇨🇭

Luzern, Switzerland

Kantonsspital Neuchâtel

🇨🇭

Neuchâtel, Switzerland

Kantonsspital Olten

🇨🇭

Olten, Switzerland

Kantonsspital Sion

🇨🇭

Sion, Switzerland

Kantonsspital Solothurn

🇨🇭

Solothurn, Switzerland

Kantonsspital St. Gallen

🇨🇭

St. Gallen, Switzerland

Universitätsspital Zürich

🇨🇭

Zürich, Switzerland

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