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Initial Non-operative Treatment Strategy Versus Appendectomy Treatment Strategy for Simple Appendicitis in Children

Phase 4
Active, not recruiting
Conditions
Appendicitis
Interventions
Procedure: Appendectomy
Registration Number
NCT02848820
Lead Sponsor
Ramon Gorter
Brief Summary

OBJECTIVE

The aim of this study is to compare the effectiveness of initial non-operative treatment strategy (reserving appendectomy for those not responding or with recurrent disease) with immediate appendectomy in children from 7 to 17 years old, inclusive, with acute simple appendicitis in terms of complications, health-related QOL and costs.

Main research question: What is the difference in proportion of patients experiencing complications within 1 year between both strategies in children from 7 to 17 years old, inclusive, with acute simple appendicitis?

Detailed Description

Initial non-operative treatment of acute simple appendicitis has recently been investigated in both the adult as the paediatric population. In the adult population, six Randomised Controlled Trial (RCTs) showed that an appendectomy could be avoided in 40-76% of the patients at the end of their follow-up period. Despite the fact that some patients need to undergo a delayed appendectomy, it has been demonstrated in systematic reviews that non-operative treatment strategy is associated with a significant reduction in complications, faster recovery and return to work, less pain duration and analgesic medication consumption. In children only pilot data is yet available. Short-term success rates of this strategy (including of the investigators own pilot cohort study) are between the 83-92%. Long-term results (one-year follow-up) are available from two studies; 62-75% did not require an appendectomy. No large RCT have yet been conducted in the paediatric population. It is therefore essential to generate high quality empirical evidence regarding this strategy in this subset of patients.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
302
Inclusion Criteria
  • Age 7-17 years

  • Radiologically confirmed simple appendicitis, defined as:

    1. Clinical findings:

      • Unwell, but not generally ill
      • Localized tenderness in the right iliac fossa region
      • Normal/hyperactive bowel sounds
      • No guarding
      • No mass palpable
    2. Ultrasonography:

      • Incompressible appendix with an outer diameter of ≥6 mm
      • Hyperaemia within the appendiceal wall
      • Without faecolith
      • Infiltration of surrounding fat
      • No signs of perforation
      • No signs of intra-abdominal abscess/phlegmon
Exclusion Criteria
  • Generalized peritonitis, complex appendicitis or sepsis (based upon predefined criteria and scoring system).

  • Scoring system: As scoring system was developed determining the risk of complex appendicitis based upon five pre-operative variable. Points have been awarded to each variable. In case the total score is less than 4 points, the patient is likely to have a simple appendicitis. In case the score is 4 or more points, the chance of having complex appendicitis is significant and those children will be excluded from this study. Variables:

    • Diffuse abdominal guarding (3 points)
    • C-Reactive Protein level more than 38 mg/L (2 points)
    • Signs on ultrasound indicative of complex appendicitis (2 points)
    • More than one day abdominal pain (2 points)
    • Temperature: more than 37.5 degree Celsius (1 point)
  • Faecolith (ultrasound)

  • Serious co-morbidity

  • Recurrent appendicitis

  • Suspicion of an underlying malignancy or inflammatory bowel disease

  • Documented type 1 allergy to the antibiotics used.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Augmentin + GentamicinAugmentin + GentamicinInitial non-operative treatment strategy reserving an appendectomy for those not responding or with recurrent disease. It consist of: Clinical observation for 48 hours with administration of Intravenous administration of amoxicillin/clavulanic acid 25/2.5mg 6-hourly (total 100/10 mg/kg daily; maximum 6000/600mg a day) and gentamicin 7mg/kg once daily for 48 hours. If after 48 hours the patient fulfils the predefined discharge criteria, the antibiotics will be switched to oral amoxicillin/clavulanic acid 50/12.5 mg/kg 8-hourly (max 1500/375mg a day) for in total 7 days and discharge. An appendectomy is reserved for those patients with clinical deterioration, non-improvement after 72 hours or recurrent appendicitis. Pain medication according to national protocol.
Operative treatment strategyAppendectomyClinical observation and semi-urgent appendectomy. Pre-, peri- and postoperative care according to local protocol. No routine postoperative antibiotics. Discharge if the patient fulfils the predefined discharge criteria. Pain medication according to national protocol.
Primary Outcome Measures
NameTimeMethod
Proportion of patients experiencing complicationsOne year follow up
Secondary Outcome Measures
NameTimeMethod
Medical and non-medical costs (Health and Labor questionnaire)1,6,12 months
Quality adjusted life years (QALY's). Calculating using outcome 13 and 141,6,12 months
Pain score measured by the Visual Analogue Scale (VAS)Clinical phase (up to 7 days)
Proportion of patients experiencing recurrent appendicitis7 days, 1,6,12 months
Proportion of patients not having to undergone appendectomy7 days, 1,6,12 months
Proportion of patients experiencing early failure of initial non-operative treatment.7 days, 1,6,12 months
Proportion of patients that undergo interval appendectomy.7 days, 1,6,12 months
Quality of life questionnaire (CHQ-CF87, EQ-5d-Youth, EQ-5d-Proxy)7 days, 1,6,12 months
Total length of hospital stay during the follow-up period for strategy related treatment or complications7 days, 1,6,12 months
Total days of analgesics medication use.one month
Proportion of patients with missed diagnosis of complex appendicitis with risk of peritonitis7 days, 1,6,12 months
Patient satisfaction questionnaire (PSQ-18 & Net promotor score)7 days, 1,6,12 months
Number of days absent from school, social or sport events7 days, 1,6,12 months
Number of days absent from work7 days, 1,6,12 months
Total number of extra visits (not the already scheduled ones) to the outpatient clinic, general practitioners office or emergency department for abdominal pain.7 days, 1,6,12 months
Promoting and obstructing factors of implementability measured by questionnaires12 months

Trial Locations

Locations (15)

Medical Center Alkmaar

🇳🇱

Alkmaar, Netherlands

Zuyderland

🇳🇱

Heerlen, Netherlands

AMC

🇳🇱

Amsterdam, Netherlands

Flevoziekenhuis

🇳🇱

Almere, Netherlands

OLVG

🇳🇱

Amsterdam, Netherlands

Maxima medical center

🇳🇱

Eindhoven, Netherlands

Amstelland

🇳🇱

Amstelveen, Netherlands

VU University medical center

🇳🇱

Amsterdam, Netherlands

Albert Schweitzer

🇳🇱

Dordrecht, Netherlands

Haga ziekenhuis

🇳🇱

Den Haag, Netherlands

Franciscus, Gasthuis en Vlietland

🇳🇱

Rotterdam, Netherlands

Rijnstate

🇳🇱

Arnhem, Netherlands

Antonius Hospital

🇳🇱

Nieuwegein, Netherlands

Gelre Hospital

🇳🇱

Apeldoorn, Netherlands

Red Cross Hospital

🇳🇱

Beverwijk, Netherlands

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