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Efficacy and Safety Study of Pamoate of Triptorelin in Children With Precocious Puberty

Phase 3
Completed
Conditions
Precocious Puberty
Interventions
Registration Number
NCT00564850
Lead Sponsor
Ipsen
Brief Summary

The purpose of the study is to assess the efficacy of triptorelin 11.25 mg pamoate in the delay of premature onset of puberty in girls less than 9 years and boys less than 10 years. This is measured by assessing the proportion of children who have a suppressed Luteinizing Hormone (LH) response to Gonadotropin Releasing Hormone (GnRH) test performed 3 months after injection with triptorelin 11.25 mg.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
37
Inclusion Criteria

Not provided

Exclusion Criteria
  • Patient with a peripheral precocious puberty: extrapituitary secretion of gonadotropins or gonadotropin-independent gonadal or adrenal sex steroids secretion.
  • Patient with a cerebral tumour requiring a neurosurgery or cerebral irradiation.
  • Patient with a Body Weight ≥ 125% of the ideal weight for the height and age (growth curves).
  • The patient has received a previous treatment with a GnRH analogue, or medroxyprogesterone or cyproterone acetate.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Triptorelin pamoate 11.25mg (Decapeptyl® SR)Triptorelin pamoate 11.25mg (Decapeptyl® SR)-
Primary Outcome Measures
NameTimeMethod
Number of Participants With a GnRH-stimulated LH Level ≤3 IU/L3 months after the first injection of triptorelin pamoate 11.25 mg
Secondary Outcome Measures
NameTimeMethod
Basal FSH LevelMonth 0, 1, 2, 3, 4, 5, and 6
Number of Girls With Oestradiol Levels ≤ 20 pg/mlMonth 0, 1, 2, 3, 4, 5 and 6
Number of Participants Whose Intravenous (i.v.) GnRH-stimulated LH Response Was ≤3 IU/LMonth 6
Difference Between Bone Age and Chronological AgeMonth 0 and 6

Bone age was defined according to Greulich and Pyle method. Chronological age was calculated using the date of birth.

Basal LH LevelMonth 0, 1, 2, 3, 4, 5 and 6
Change From Baseline in Growth Velocity (GV) SDS at Month 6Baseline and month 6

Change from baseline of GV was calculated as: GV at month 6 - GV at baseline. GV SDS was calculated using SAS algorithm.

Growth velocity during the study was calculated using the two height measures as: GV = (Height at baseline - Height at screening)\*365/delay between two height measures.

Triptorelin Plasma LevelsMonth 1, 2, 3, 4, 5 and 6
Follicle Stimulating Hormone (FSH) Level Following GnRH TestScreening, month 3 and 6
Testosterone LevelMonth 0, 3 and 6
Body Mass Index (BMI) SDSMonth 0, 3 and 6
Number of Girls With Inhibin B Levels < 6 pg/mlMonth 0, 3 and 6
Change From Screening in Pubertal Stage (Tanner Method) at Month 6Between screening and month 6

Pubertal stage (graded from 1 to 5 for penis and breast development, graded from 1 to 6 for pubic hair development) according to the Tanner method was collected. A low stage (i.e. 1) corresponds to a pre-pubertal stage and a high stage (i.e. 5 or 6) to an adult stage. Any increase of grade was defined as 'increased' and no change in grade or a reduced grade was defined as 'stabilised or reduced'.

Height Standard Deviation Score (SDS)Month 0, 3 and 6

Standard deviation (SD) is a standard term used in growth studies and represents Standard Deviations calculated as the patient value minus the mean divided by the standard deviation. Standard Deviation Scores vary depending on the age and sex of the child.

Uterine LengthMonth 0, 3 and 6

Trial Locations

Locations (18)

Hôpital Hotel-Dieu (CHU)

🇫🇷

Angers, France

Hôpital Saint-Jacques

🇫🇷

Besancon, France

Medical Centre

🇫🇷

Bordeaux, France

Hôpital du Bocage

🇫🇷

Dijon, France

Hôpital Flaubert

🇫🇷

Le Havre, France

Hôpital Jeanne de Flandre

🇫🇷

Lille, France

Hôpital de la Timone Enfants

🇫🇷

Marseille, France

Hôpital Debrousse

🇫🇷

Lyon, France

Hôpital Archet 2

🇫🇷

Nice, France

Hôpital St-Vincent de Paul

🇫🇷

Paris, France

Hôpital Necker - Enfants Malades

🇫🇷

Paris, France

Hôpital Trousseau

🇫🇷

Paris, France

American Memorial Hospital

🇫🇷

Reims, France

Hôpital Robert Debré

🇫🇷

Paris, France

Hôpital Charles Nicolle

🇫🇷

Rouen, France

Hôpital Hautepierre

🇫🇷

Strasbourg, France

Hôpital de la Gespe

🇫🇷

Tarbes, France

Hôpital des Enfants

🇫🇷

Toulouse, France

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