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The effect of intranasal insulin on development and behaviour of children with Phelan-McDermid syndrome.Dutch: Het effect van insuline neusspray op ontwikkeling en gedrag van kinderen met het Phelan-McDermid syndroom.

Conditions
Phelan-McDermid syndrome, 22q13.3 deletion syndrome, insulin, intranasal, development, behaviour.Dutch: Phelan-McDermid syndroom, 22q13.3 deletie syndroom, insuline, intransasaal, ontwikkeling, gedrag.
Registration Number
NL-OMON24236
Lead Sponsor
niversity Medical Centre Groningen
Brief Summary

On the moment of registration, the study has yet to begin. Therefore there currently are no publications concerning this study.

Detailed Description

Not available

Recruitment & Eligibility

Status
Pending
Sex
Not specified
Target Recruitment
20
Inclusion Criteria

1. Age between 12 months and 18 years 0 months old at 1-1-2013;

2. Proven SHANK3 deletion by array-comparative genomic hybridization (array-CGH);

Exclusion Criteria

1. A contra-indication for the use of intranasal application (e.g. anatomical obstruction);

2. Severe perinatal brain damage (e.g. asphyxia, haemorrhage, infection);

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Developmental pace, calculated as the difference in developmental age equivalent between two assessments divided by the difference in calendar age in months at the time of these assessments (typically 6 months).
Secondary Outcome Measures
NameTimeMethod
Behaviour, improvement of behaviour represented by the increase in test scores between assessment (typically 6 months).
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