MedPath

Topotecan in Treating Young Patients With Neoplastic Meningitis Due to Leukemia, Lymphoma, or Solid Tumors

Phase 1
Terminated
Conditions
Brain and Central Nervous System Tumors
Lymphoma
Leukemia
Unspecified Childhood Solid Tumor, Protocol Specific
Carcinoma of Unknown Primary
Registration Number
NCT00112619
Lead Sponsor
Pediatric Brain Tumor Consortium
Brief Summary

RATIONALE: Drugs used in chemotherapy, such as topotecan, work in different ways to stop the growth of cancer cells, either by killing the cells or by stopping them from dividing.

PURPOSE: This phase I trial is studying the side effects, best way to give, and best dose of topotecan when given by intraventricular infusion in treating young patients with neoplastic meningitis due to leukemia, lymphoma, or solid tumors.

Detailed Description

OBJECTIVES:

Primary

* Determine the maximum tolerated dose (MTD) of intraventricular topotecan in young patients with neoplastic meningitis secondary to leukemia, lymphoma, or solid tumors.

* Determine the toxic effects and dose-limiting toxicity of this drug in these patients.

* Determine whether the MTD of this drug is also the pharmacokinetic optimal dose, defined by the topotecan lactone concentration in the cerebral spinal fluid (CSF), in these patients.

Secondary

* Determine, preliminarily, the antitumor activity of this drug in these patients.

* Determine the pharmacokinetics of this drug in the CSF of these patients.

* Correlate observed effects of post-treatment central review imaging (if feasible) with response to this drug in these patients.

OUTLINE: This is a non-randomized, dose-escalation, multicenter study.

* Induction therapy (weeks 1-4): Patients receive topotecan intraventricularly\* over 5 minutes on days 1-5 in weeks 1 and 3. Patients then proceed to consolidation therapy in week 5.

NOTE: \*Patients who are willing, receive 1 intralumbar (instead of intraventricular) dose of topotecan on day 1 of week 3 only.

* Consolidation therapy (weeks 5-10): Patients receive topotecan intraventricularly on days 1-5 in weeks 5 and 8. Patients then proceed to maintenance therapy in week 11.

* Maintenance therapy (weeks 11-54): Patients receive topotecan intraventricularly on days 1-5 in weeks 11, 15, 19, 23, 27, 31, 35, 39, 43, 47, and 51.

Cohorts of 3-6 patients receive escalating doses of intraventricular topotecan until the maximum tolerated dose (MTD) is determined. The MTD is defined as the dose preceding that at which 2 of 3 or 2 of 6 patients experience dose-limiting toxicity.

Once the MTD is determined, the cohort is expanded to 25 patients and the MTD is declared the pharmacokinetic optimal dose provided 23 of 25 patients treated at the MTD achieve the target pharmacokinetic parameter.

PROJECTED ACCRUAL: A total of 28-49 patients will be accrued for this study within 9-24 months.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
19
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Primary Outcome Measures
NameTimeMethod
Number of patients with dose-limiting toxicityFirst 14 days of therapy
Estimate the dose of intraventricular topotecan that will result in cerebrospinal fluid lactone concentrations exceeding 1 ng/mL for at least 8 hours after an intrathecal injectionDay 1 of Week 1
Estimate the maximum tolerated dose of intraventricular topotecan on this scheduleFirst 14 days of therapy
Secondary Outcome Measures
NameTimeMethod
Number of patients with objective documentation of tumor response to intraventricular topotecanWeeks 5, 11 and then every 12 weeks until off study

MRI of the brain and spine is obtained pre-consolidation, pre-maintenance, and then every 12 weeks in maintenance.

PharmacokineticsDay 1 of Week 1

The cerebrospinal fluid (CSF) concentration-time profile for topotecan after intrathecal CSF administration will be modeled from the CSF samples collected on day 1 of week 1. Individual pharmacokinetic parameters estimated will include volume of central compartment, elimination rate constant, half-life, and clearance.

Correlation of imaging parameters with tumor responsePre-treatment, week 5, week 11, and then every 12 weeks until off study

MRI scans of the brain and spine is obtained pre-treament, pre-consolidation, pre-maintenance, and then every 12 weeks on maintenance.

Trial Locations

Locations (11)

Children's Memorial Hospital - Chicago

🇺🇸

Chicago, Illinois, United States

Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

Children's Hospital of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

Dan L. Duncan Cancer Center at Baylor College of Medicine

🇺🇸

Houston, Texas, United States

Children's Hospital and Regional Medical Center - Seattle

🇺🇸

Seattle, Washington, United States

Duke Comprehensive Cancer Center

🇺🇸

Durham, North Carolina, United States

Children's National Medical Center

🇺🇸

Washington, District of Columbia, United States

St. Jude Children's Research Hospital

🇺🇸

Memphis, Tennessee, United States

Dana-Farber/Harvard Cancer Center at Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Warren Grant Magnuson Clinical Center - NCI Clinical Trials Referral Office

🇺🇸

Bethesda, Maryland, United States

UCSF Helen Diller Family Comprehensive Cancer Center

🇺🇸

San Francisco, California, United States

© Copyright 2025. All Rights Reserved by MedPath