MedPath

Chemotherapy-Free pCR-Guided Strategy With Trastuzumab-pertuzumab and T-DM1 in HER2-positive Early Breast Cancer

Phase 2
Active, not recruiting
Conditions
Early Breast Cancer
Interventions
Registration Number
NCT04733118
Lead Sponsor
MedSIR
Brief Summary

This is a multicenter, open-label, single-arm, one-stage, phase II study to assess the efficacy of a chemotherapy-free pathological complete response (pCR)-guided strategy with trastuzumab and pertuzumab (given as a subcutaneous fixed-dose combination) and T-DM1, for patients with previously untreated HER2-positive early breast cancer.

Detailed Description

Patients ≥ 18 years of age with previously untreated HER2 IHC 3+ invasive carcinoma according to ASCO/CAP 2018 guidelines.

Tumor size between \>5 to 30 mm by breast MRI and node-negative status by clinical exam, MRI, and ultrasound. In patients with suspected axillary node involvement, a negative fine needle aspiration biopsy (FNAB) will be mandatory.

Central review for:

Breast MRI. HER2 status. Neoadjuvant treatment will consist In 8 cycles of fixed-dose subcutaneous (SC FDC) HP combination (± ET according to HR status).

urgery will be performed within 4 weeks from the last cycle of HP (sentinel node biopsy will be mandatory; subsequent axillary dissection will be performed according to local guidelines). Surgery will require free margins for any infiltrating or DCIS lesion.

Radiotherapy will be mandatory for patients with breast preservation.

Adjuvant systemic therapy will be started within 4 weeks from surgery depending on pathological report:

Arm A: pCR (breast and axilla): HP SC FDC x 10 cycles. Arm B: Residual invasive breast tumor and/or ypN0(i+), ypN0(mol+), ypN1mi: T-DM1 x 10 cycles Arm C: ypN1 to N3: T-DM1 x 10 cycles, with physician's choice chemotherapy allowed between surgery and T-DM1.

All patients with HR\[+\] tumors will receive adjuvant ET up to at least 5 years (ET will also be administered in association with adjuvant HP or T-DM1, with the exception of the cycles involving the use of chemotherapy in Arm C).

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
393
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Patient HER 2+ IHC 3+Trastuzumab and Pertuzumab (FDC SC) and T-DM1Patients ≥18 years of age with previously untreated HER2-positive (HER2\[+\]) (Immunohistochemistry \[IHC\] 3+) invasive carcinoma according to the 2018 American Society of Clinical Oncology/College of American Pathologists (ASCO/CAP) criteria and tumor size between \>5 to 25 mm by breast magnetic resonance imaging (MRI) and node-negative status by clinical exam, MRI, and ultrasound. Patients must have not been previously treated with chemotherapy, anti-HER2 therapy, radiation therapy, or endocrine therapy (ET) for invasive breast cancer. Patients with metastatic disease are not eligible. In patients with suspected axillary node involvement, a negative fine needle aspiration biopsy (FNAB) will be mandatory
Primary Outcome Measures
NameTimeMethod
3-year recurrence-free interval (3y-RFI)3 years

3-year recurrence-free interval (3y-RFI) defined as time from start of treatment in adjuvant setting until recurrence, new invasive disease, or death from breast cancer. Recurrence will be defined in accordance with the standardized efficacy endpoints (STEEP) criteria.

Global health status decline1 year

Global health status decline rate at 1 year from start of neoadjuvant treatment, defined as the rate of patients with a ≥10% global health status decline at 1 year from start of neoadjuvant treatment as assessed by the Global Health Status/QoL EORTC-QLC-C30 scale and its breast cancer module QLQ-BR23.

Secondary Outcome Measures
NameTimeMethod
Survival rates invasive disease-free survival (iDFS)3 years and 5 years

Analyze iDFS

Survival rates EFS3 years and 5 years

Analyze the event-free survival (EFS)

Health-Related Quality of Life (HRQoL) - QLQ-BR23Baseline up to 5 years

Change from baseline in scores using the European Organisation for Research and Treatment of Cancer QLQ-BR23 \[with 4 functional and 4 symptom scales\], at baseline, Day 1 of cycles 2-4, then on Day 1 of each subsequent cycle starting with cycle 6, and at the end-of-treatment. Responses to all items are converted to a 0-100 scale using a standard scoring algorithm. For functional scales, higher score represents a better level of functioning; for symptom scales, a higher score represents a higher severity of symptoms.

pathological complete response (pCR)after neoadjuvant treatment (8 cycles, an average of 6months)

pCR rates concerning breast and lymph nodes (pCRBREAST+LYMPH NODE) and pCR concerning breast only (pCRBREAST) in the overall population.

Breast-conserving surgery (BCS)after neoadjuvant treatment (8 cycles, an average of 6months)

Evaluate the rate of BCS

Response rate BCSafter neoadjuvant treatment (8 cycles, an average of 6months)

Evaluate the correlation between final MRI-guide response rate results and breast-conserving surgery (BCS)

Response rate pCRafter neoadjuvant treatment (8 cycles, an average of 6months)

Evaluate the correlation between final MRI- guide response rate and pCR

Survival rates relapse-free interval (RFI)5 years

Analyze RFI

To evaluate the ratio of patients who have needed chemotherapy.before T-DM1

Ratio of patients of cohort C who will receive adjuvant chemotherapy before T-DM1.

pathological complete response (pCR) according to hormone receptor (HR) statusafter neoadjuvant treatment (8 cycles, an average of 6months)

pCR rates according to HR status

Residual cancer burden (RCB)after neoadjuvant treatment (8 cycles, an average of 6months)

RCB -0, -I, -II, -III; (0:best outcome, III: worst outcome)

Survival rates relapse-free survival (RFS)3 years and 5 years

Analyze RFS

Survival rates disease-free survival (DFS)3 years and 5 years

Analyze DFS

Health-Related Quality of Life (HRQoL) - QLQ-C30Baseline up to 5 years

Change from baseline in scores using the European Organisation for Research and Treatment of Cancer QoL Questionnaire Core 30 (QLQ-C30) \[with 5 functional and 3 symptom scales, a Global Health Status (GHS)/QoL scale, and 6 single items\], at baseline, Day 1 of cycles 2-4, then on Day 1 of each subsequent cycle starting with cycle 6, and at the end-of-treatment. Responses to all items are converted to a 0-100 scale using a standard scoring algorithm. For functional scales, higher score represents a better level of functioning; for symptom scales, a higher score represents a higher severity of symptoms.

Response rate RCBafter neoadjuvant treatment (8 cycles, an average of 6months)

Evaluate the correlation between final MRI -guide response rate and RCB at surgery

Survival ratesdistant relapse-free survival (DRFS)3 years and 5 years

Analyze DRFS

Safety adverse events (AEs)Baseline up to 5 years

Number of patients with treatment-related AEs (Grade 3 and 4 AEs and serious adverse events \[SAEs\]) by using the National Cancer Institute (NCI)-Common Terminology Criteria for Adverse Events (CTCAE) v.5.0.

Survival rates overall survival (OS)3 years and 5 years

Analyze OS

Survival ratesbreast cancer-specific survival (BCSS).3 years and 5 years

Analyze BCSS

To assess the cardiac toxicity profile after 1 year of adjuvant treatmentafter 1 year of adjuvant treatment

Adverse events of cardiotoxicity after 1 year of adjuvant treatment according to the NCI-CTCAE v.5.0.

To assess the general toxicity profile according to CTCAE v.5.0.at 3 and 5 year

Toxicity and safety profile at 3 and 5 years as per NCI-CTCAE v.5.0.

Trial Locations

Locations (41)

Hospital Universitari San Joan de Reus

🇪🇸

Reus, Tarragona, Spain

Tolna County Balassa János Hospital

🇭🇺

Szekszárd, Hungary

Praxisnetzwerk Hämatologie und intern. Onkologie

🇩🇪

Cologne, Germany

Azienda Ospedaliero Universitaria Di Bologna - Policlinico S.Orsola-Malpighi

🇮🇹

Bologna, Italy

AO Ospedale Civile Legnano

🇮🇹

Milan, Italy

UMHAT Sveti Ivan Rilski EAD Department of Medical Oncology

🇧🇬

Sofia, Bulgaria

Evangelisches Krankenhaus Bethesda

🇩🇪

Duisburg, Germany

Kliniken Essen Mitte

🇩🇪

Essen, Germany

Universitätsklinikum Essen Frauenklinik

🇩🇪

Essen, Germany

Universitätsklinikum Mannheim GmbH

🇩🇪

Manheim, Germany

Klinikum Ernst von Bergmann

🇩🇪

Potsdam, Germany

Békés county hospital

🇭🇺

Békés, Hungary

Istituto Europeo di Oncologia - NC

🇮🇹

Milan, Italy

Ospedale San Gerardo

🇮🇹

Monza, Italy

Azienda Ospedaliero-Universitaria di Parma

🇮🇹

Parma, Italy

Ospedale Guglielmo da Saliceto

🇮🇹

Piacenza, Italy

Fondazione Policlinico Universitario Agostino Gemelli

🇮🇹

Roma, Italy

ICO L'Hospitalet - Instituto Catalán de Oncología

🇪🇸

L'Hospitalet de Llobregat, Barcelona, Spain

Hospital Universitario Reina Sofia

🇪🇸

Córdoba, Cordoba, Spain

Hospital Universitario A Coruña

🇪🇸

A Coruna, Spain

Centro Oncológico de Galicia

🇪🇸

A Coruña, Spain

Hospital General Universitario de Alicante

🇪🇸

Alicante, Spain

Hospital Universitari Dexeus - Grupo Quirónsalud

🇪🇸

Barcelona, Spain

Institut Català d' Oncologia Badalona (ICO)

🇪🇸

Badalona, Spain

VHIO Vall d'Hebron Institute of Oncology

🇪🇸

Barcelona, Spain

Hospital Universitario de Basurto

🇪🇸

Bilbao, Spain

Consorcio Hospitalario Provincial De Castelló

🇪🇸

Castelló De La Plana, Spain

Hospital Universitario Clínico San Cecilio de Granada

🇪🇸

Granada, Spain

Complejo Hospitalario de Jaen

🇪🇸

Jaen, Spain

Complejo Asistencial Universitario de León

🇪🇸

León, Spain

Hospital Universitari Arnau de Vilanova de Lleida

🇪🇸

Lleida, Spain

Hospital Clínico San Carlos

🇪🇸

Madrid, Spain

Hospital Quirón San Camilo- Ruber Juan Bravo

🇪🇸

Madrid, Spain

Hospital Ramón y Cajal

🇪🇸

Madrid, Spain

Hospital Universitario Virgen del Rocio

🇪🇸

Sevilla, Spain

Hospital Universitario de Torrejón

🇪🇸

Torrejón, Spain

Instituto Valenciano de Oncología (IVO)

🇪🇸

Valencia, Spain

Hospital La Fe

🇪🇸

Valencia, Spain

Consorcio Hospital General de Valencia

🇪🇸

Valencia, Spain

Hospital Arnau de Vilanova de Valencia

🇪🇸

Valencia, Spain

Hospital Clinico Universitario de Valencia

🇪🇸

Valencia, Spain

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