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Trial Aimed at Reducing Complications After Half-Matched BMT for Thalassemia

Phase 1
Conditions
Health Condition 1: D561- Beta thalassemiaHealth Condition 2: D570- Hb-SS disease with crisis
Registration Number
CTRI/2019/04/018379
Lead Sponsor
Manashi Chakrabarti Foundation
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Yet Recruiting
Sex
Not specified
Target Recruitment
0
Inclusion Criteria

1)First Transplantation

2)Diagnosis of Hemoglobinopathy

3)No major organ dysfunction

Exclusion Criteria

1)Patients with uncontrolled bacterial, viral or fungal infections (undergoing appropriate treatment and with progression of clinical symptoms) within 1 month prior to conditioning. Patients with febrile illness or suspected minor infection should await clinical resolution prior to starting conditioning.

2)Patients seropositive for the human immunodeficiency virus (HIV)

3)Patient with active Hepatitis B or C determined by serology and/or NAAT not on treatment

4)Active hepatitis, bridging fibrosis or cirrhosis on liver biopsy (biopsy required for patients on chronic transfusion therapy for > 1 year and evidence of iron overload with ferritin >1000 ng/mL)

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
1)Engraftment by Day 30. <br/ ><br> <br/ ><br> <br/ ><br>2)Incidence of grade IIâ??IV acute graft-versus-host disease (GVHD) until Day 100 post-transplantation <br/ ><br> <br/ ><br> <br/ ><br> <br/ ><br> <br/ ><br> <br/ ><br> <br/ ><br>3)Incidence of Post-Transplantation Hemophagocytic Syndrome <br/ ><br>Timepoint: 3 months <br/ ><br>6 months <br/ ><br>one year
Secondary Outcome Measures
NameTimeMethod
­Incidence and severity of chronic GVHD at 1 year and 2 years <br/ ><br>­Incidence of TRM at all visits throughout the study <br/ ><br>­Incidence and severity of acute infusional toxicities <br/ ><br>­Graft failure from Day 0 to Day 28 <br/ ><br>Timepoint: 3 months <br/ ><br>6 months <br/ ><br>one year <br/ ><br>two years
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