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Safety, Pharmacokinetics and Pharmacodynamics of TKI258 in Subjects With Acute Myeloid Leukemia

Phase 1
Terminated
Conditions
Acute Myeloid Leukemia
Interventions
Registration Number
NCT00279773
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

The primary objective is to determine the maximum tolerated dose (MTD), dose limiting toxicity (DLT), and safety profile of TKI258 when administered to subjects with acute myeloid leukemia (AML).

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
34
Inclusion Criteria
  • Confirmed diagnosis of Acute Myeloid Leukemia
  • Eighteen years of age or older
  • Life expectancy of at least 2 months
Exclusion Criteria
  • Intracranial disease or epidural disease
  • Clinically significant cardiac disease
  • Diabetes mellitus uncontrolled with medication
  • Pregnant or breast feeding women
  • Dementia or altered mental status
  • Known pre-existing clinically significant or uncontrolled disorder of the hypothalamic-pituitary axis, adrenal or thyroid glands
  • Previous pericarditis
  • Malabsorption syndrome or uncontrolled gastrointestinal symptoms such as nausea,diarrhea,vomiting

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
TKI258 - dose escalationTKI258Dose-Escalation
TKI258 - dose expansionTKI258Dose-Expansion
Primary Outcome Measures
NameTimeMethod
Maximum tolerated dose28 days - dose-escalation; 4 months - dose-expansion
Dose limiting toxicity28 days - dose-escalation; 4 months - dose-expansion
Safety profile28 days - dose-escalation; 4 months - dose-expansion
Secondary Outcome Measures
NameTimeMethod
Evaluation of plasma pharmacokinetics and pharmacodynamics28 days - dose-escalation; 4 months - dose-expansion

Trial Locations

Locations (1)

The University of Texas, M.D. Anderson Cancer Center

🇺🇸

Houston, Texas, United States

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