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A Study To Assess The Safety And Efficacy Of SU11248 In Patients With Gastrointestinal Stromal Tumor(GIST)

Phase 3
Completed
Conditions
Gastrointestinal Stromal Tumor
Interventions
Drug: Placebo
Registration Number
NCT00075218
Lead Sponsor
Pfizer
Brief Summary

A study to assess the safety and efficacy of SU11248 in patients with gastrointestinal stromal tumor (GIST) whose disease has failed imatinib therapy or who were intolerant to imatinib treatment.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
361
Inclusion Criteria
  • Histologically-proven diagnosis of malignant GIST not amenable to surgery, radiation or combined modality treatment with curative intent
  • Failed Gleevec treatment or intolerant to Gleevec therapy

Key

Exclusion Criteria
  • Treatment with any chemotherapy, chemoembolization therapy, immunotherapy, or investigational agent since the last dose of Gleevec

Study & Design

Study Type
INTERVENTIONAL
Study Design
CROSSOVER
Arm && Interventions
GroupInterventionDescription
BPlacebo-
ASU011248-
Primary Outcome Measures
NameTimeMethod
Time to Tumor Progression (TTP) as Assessed by Imaging Studies at End of Double-blind Treatment PhaseDay 28 of each 6-week cycle : duration of double-blind treatment phase

Time from randomization to first documentation of objective tumor progression based on the assessment of an independent, third-party imaging laboratory using RECIST (Response Evaluation Criteria in Solid Tumors).

Time to Tumor Progression (TTP) as Assessed in the Double-blind Treatment Phase at End of StudyDay 28 of each 6-week cycle : duration of double-blind treatment phase after Last Subject Last Visit (LSLV)

Time from randomization to first documentation of objective tumor progression based on the assessment of an independent, third-party imaging laboratory using RECIST (Response Evaluation Criteria in Solid Tumors).

Secondary Outcome Measures
NameTimeMethod
Time to Tumor Response (TTR)Day 28 of each cycle : duration of double-blind treatment phase

Time from date of randomization to first documentation of objective tumor response that was subsequently confirmed. TTR was only calculated for the subgroup of subjects with a confirmed objective tumor response.

Duration of Performance Status MaintenanceDay 28 of each cycle : duration of double-blind treatment phase

Time from randomization until the last time the performance status was no worse than at baseline or to death due to cancer in the absence of previous documentation of performance status worsening.

Time to Pain Progression Using McGill Pain Questionnaire-present Pain Intensity (MPQ-PPI)Day 1 & 28 of each cycle : duration of double-blind treatment phase

25th Quartile: Time to Progression. Progression: a) No change (NC) in MPQ-PPI score (0=no pain to 5=excruciating pain) with increase total analgesic use \>= 50% over baseline OR b) Increase score \>= 1 point with either NC in total analgesic use or increase total analgesic use \>= 50% over baseline. (50th Quartile not achieved.)

Overall Survival Status of Subjectsclinic visit or telephone contact every 2 months for up to 3 years from the last dose of study drug

Number of subjects alive at end of study.

Overall Survivalclinic visit or telephone contact every 2 months for up to 3 years from the last dose of study drug

Time from date of randomization to date of death due to any cause.

Overall Survival Based on the Rank Preserving Structural Failure Time Methodclinic visit or telephone contact every 2 months for up to 3 years from the last dose of study drug

time from date of randomization to date of death due to any cause (rank preserving structural failure time method).

Best Overall Tumor Response During Double-blind Treatment PhaseDay 28 of each cycle : duration of double-blind treatment phase

Tumor response according to Response Evaluation Criteria in Solid Tumors (RECIST).

Confirmed Objective Response (CR or PR) in SubjectsDay 28 of each cycle : duration of double-blind treatment phase

Overall confirmed objective response = confirmed Complete Response (CR) OR confirmed Partial Response (PR) according to RECIST. Confirmed responses were those that persisted on repeat imaging study ≥ 4 weeks after initial documentation of response.

Progression Free Survival (PFS)Day 28 of each cycle : duration of double-blind treatment phase

Time from randomization to first documentation of objective tumor progression or to death due to any cause (on treatment or within 28 days of last dose).

Subjects With Pain Relief Response Using McGill Pain Questionnaire-present Pain Intensity (MPQ-PPI)Day 1 & 28 of each cycle : duration of double-blind treatment phase

MPQ-PPI: 0=no pain to 5= excruciating pain. Pain Relief Response= 1) Decrease by \>= 1 points in MPQ-PPI score with either Decrease or No Change in total analgesic use \>= 50% over baseline OR 2) No change in MPQ-PPI score with Decrease total analgesic use \>= 50% over baseline.

Change From Baseline Score in EuroQoL Visual Analog Scale (EQ-VAS)Day 1 & 28 of each cycle : duration of double-blind treatment phase

Change: median score at observation minus median score at baseline. EQ-VAS score on the self-rated "thermometer," indicating the patient's own assessment of their health status from 0 (worst) to 100 (best) imaginable health state.

Change From Baseline in EQ-5D Health State Profile IndexDay 1 & 28 of each cycle : duration of double-blind treatment phase

Change: median index score at observation minus median index score at baseline. EQ-5D is a generic instrument that describes health status in 5 dimensions (mobility, self-care, pain/discomfort, anxiety/depression, usual activities) with a weighted health Index based on general population values where where 0.0 = death and 1.0 = perfect health.

Trial Locations

Locations (1)

Pfizer Investigational Site

🇬🇧

Newcastle-Upon-Tyne, United Kingdom

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