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Umbilical Cord Mesenchymal Stem Cells for Patients With Liver Cirrhosis

Phase 1
Completed
Conditions
Liver Cirrhosis
Interventions
Drug: conventional plus MSC treatment
Drug: conventional plus placebo treatment
Registration Number
NCT01220492
Lead Sponsor
Beijing 302 Hospital
Brief Summary

Liver cirrhosis (LC) represents a late stage of progressive hepatic fibrosis characterized by distortion of the hepatic architecture and formation of regenerative nodules. The liver transplantation is one of the only effective therapies available to such patients. However, lack of donors, surgical complications, rejection, and high cost are it's serious problems. The potential for stem cells to differentiate into hepatocytes cells was recently confirmed. Particularly, autologous bone marrow-derived mesenchymal stem cell (BM-MSC) has been demonstrated to decrease MELD score and increase serum albumin in the patients with decompensated liver cirrhosis. Therefore, the investigators propose a hypothesis that umbilical cord-derived MSCs (UC-MSC) can also improve the disease conditions of LC patients, particularly reducing the decompensated conditions in these patients.

Detailed Description

Liver cirrhosis (LC) represents a late stage of progressive hepatic fibrosis characterized by distortion of the hepatic architecture and formation of regenerative nodules. The liver transplantation is one of the only effective therapies available to such patients. However, lack of donors, surgical complications, rejection, and high cost are it's serious problems.

The potential for stem cells to differentiate into hepatocytes cells was recently confirmed. In particular, bone marrow-derived mesenchymal stem cell (BM-MSC) transplantation has been applicated in the clinic for treat several human diseases such as GVHD, cardiac injury and brain injury, and displayed good tolerance and efficiency. BM-MSC has also been used to treat human liver diseases such as liver failure and liver cirrhosis. In a phase 1 study, autologous BM-MSC transplantation has potential to decrease MELD score and increase serum albumin in the patients with decompensated liver cirrhosis.

The purpose of this study is to learn whether and how umbilical cord-derived MSCs (UC-MSC) can improve the longer term survival in patients with liver cirrhosis. This study will also look at how well BM-MSC is tolerated and its safety in LC patients.

Participants in the study will be randomly assigned to one of two treatment arms:

Arm A: Participants will receive conserved treatment plus three times UC-MSC treatment at 4-week intervals.

Arm B: Participants will receive conserved treatment plus three times saline infusions at 4-week intervals.

UC-MSC will be prepared according to standard procedures and is collected in plastic bags containing anti coagulant. MSCs are infused intravenously. After cell therapy, patients are followed up for 75 months. The evaluation of some clinical parameters such as the level of serum alanine aminotransferase (ALT), total bilirubin (TB),prothrombin time (PT), albumin (ALB), prealbumin(PA), the rountin blood test are detected at week 12, 24, 48 timepoints. Clinical symptoms as well as complication were also observed simultaneously.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
266
Inclusion Criteria
  1. Liver cirrhosis
  2. Negative pregnancy test (female patients in fertile age)
  3. written consent
Exclusion Criteria
  1. Hepatocellular carcinoma or other malignancies
  2. Pregnancy
  3. sepsis
  4. Presence of significant extrahepatic biliary disease (e.g. CBD stone, PSC, etc.)
  5. Cardiac, renal or respiratory failure
  6. Active thrombosis of the portal or hepatic veins

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
conventional plus MSC treatmentconventional plus MSC treatmentparticipants will receive conventional treatment plus a dose of MSC from day 0 through the week 8 study visit. Participants will then be followed until the 75 months study visit.
conventional plus placebo treatmentconventional plus placebo treatmentparticipants will receive conventional plus placebo treatment from day 0 through the week 8 study visit. Participants will then be followed until the 75 months study visit.
Primary Outcome Measures
NameTimeMethod
survival time75 months
incidence of HCC events75 months
Secondary Outcome Measures
NameTimeMethod
The levels of serum albumin48 weeks
The levels of serum total bilirubin48 weeks
The levels of serum prothrombin activity48 weeks
complications48 weeks
the levels of serum cholinesterase48 weeks

Trial Locations

Locations (1)

Beijing 302 Hospital

🇨🇳

Beijing, Beijing, China

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