MedPath

Eltrombopag therapy for low platelets in patients on azacitidine treatment for myelodysplastic syndrome and acute myeloid leukaemia

Phase 2
Recruiting
Conditions
Myelodysplastic Syndromes (MDS)
Cancer - Leukaemia - Acute leukaemia
Low marrow blast count acute myeloid leukaemia (AML)
Blood - Haematological diseases
Registration Number
ACTRN12610000641099
Lead Sponsor
Peter Mac Callum Cancer Centre
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
All
Target Recruitment
25
Inclusion Criteria

Patients with low platelet count (<=150 x109/L) and in addition disease diagnosis of either MDS (by World Health Organization Criteria, those with refractory anemia with high blast counts and refractory anemia with ringed sideroblasts to also have at least one clinically significant cytopenia), nonproliferative Chronic Myelomonocytic Leukaemia (CMML) or low marrow blast count AML not suitable for induction chemotherapy; Eastern Cooperative Oncology Group (ECOG) 2 or less with life expectancy at least 3 months, adequate contraception and adequate renal and hepatic function; written informed consent

Exclusion Criteria

Subjects with the diagnosis acute promyelocytic leukaemia; Prior treatment with 5-azacitidine or any other methyl-transferase inhibitor, eltrombopag, romiplostim, or other Trombopoietin T (TPO)-receptor agonist;AML or MDS requiring cytoreductive therapy (eg hydroxyurea, ara-c, thioguanine etc) in the month prior to study entry; known pro-thrombotic condition; history of Ischaemic neurological event (Transient Ischaemic Attack (TIA) or stroke) within the preceding 2 years;active or uncontrolled infections

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Grade III/IV non-haematological toxicity possibly, probably or definitely related to the combination of eltrombopag and azacitidine based on clinical assessments.[At 6 cycles of therapy (approx 6 months)]
Secondary Outcome Measures
NameTimeMethod
Secondary outcome 1:<br>To gather preliminary evidence of the clinical efficacy of eltrombopag to improve platelet counts in this setting, and the appropriate dose at which this may be achieved based on data obtained from clinical assessments, up to 4 bone marrow biopsies, and peripheral blood tests.[Time point: approximately 2.5 years after the last accrued patient completes study treatment];To explore laboratory findings to correlate with the response of the combination of 5-azacitidine and eltrombopag in patients with MDS and low marrow blast count AML[Time point: approximately 2.5 years after last accrued patient completes study treatment]
© Copyright 2025. All Rights Reserved by MedPath