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Study of CTO1681 for the Prevention and Treatment of CRS in DLBCL Patients Receiving CAR T-Cell Therapy

Phase 1
Recruiting
Conditions
Cytokine Release Syndrome
Interventions
Drug: CTO1681 20 μg
Drug: CTO1681 10 μg
Drug: CTO1681 30 μg
Registration Number
NCT05905328
Lead Sponsor
CytoAgents, Inc.
Brief Summary

This is an interventional study to evaluate the use of CTO1681 in preventing or reducing CAR T-cell-induced toxicities like cytokine release syndrome (CRS). This study will enroll adult patients with DLBCL who are scheduled to receive CD19-directed CAR T-cell therapy.

The first phase of the study will be open label with dose escalation. Participants will start taking CTO1681 just prior to receiving their CAR T-cell therapy and continue to take the study drug three times daily for a total of 15 days.

Detailed Description

The first phase of the study will be an open-label, dose escalation, safety assessment in a group of patients, and will also collect data to investigate the potential benefit of CTO1681, initiated prior to CAR T-cell therapy, in preventing or reducing certain toxicities or side effects associated with CAR T-cell therapy, such as cytokine release syndrome (CRS).

Participants will start taking CTO1681 just prior to receiving their CAR T-cell therapy and continue to take the study drug three times daily for a total of 15 days.

Participants will provide blood samples at specified points throughout the study. In addition, urine samples, ECGs, scans, and other medical evaluations will be performed that are associated with the CAR T-cell therapy and/or necessary to verify study eligibility. Participants will be monitored for safety and efficacy for 43 days, and then will have follow-up to continue to monitor for safety and monitor for tumor response for up to 6 months for phase 1.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
54
Inclusion Criteria
  1. Age 18 years or older.

  2. Undergone leukapheresis and is scheduled to receive protocol-specified commercially available axicabtagene ciloleucel CD19-directed CAR T-cell therapy for DLBCL without corticosteroid prophylaxis for CRS and/or ICANS. Patients eligible for study must have relapsed or refractory DLBCL after at least one prior line of systemic therapy.

  3. Met all inclusion criteria for CAR T-cell therapy per institutional guidelines.

  4. Adequate organ function defined as:

    1. Estimated Creatinine Clearance per Cockroft Gault formula ≥ 60 mL/min.
    2. Serum alanine aminotransferase/aspartate aminotransferase ≤ 2.5 × ULN.
    3. Total bilirubin ≤ 1.5 × ULN.
    4. Left ventricular ejection fraction ≥ 40% on echocardiogram or multigated acquisition and no clinically significant pericardial effusion.
    5. Platelets ≥ 50,000/mm3.
    6. Absolute neutrophil count > 1000/μL.
    7. Absolute lymphocyte count > 100/μL.
  5. Documented measurable lymphoma disease adequate to judge by Lugano Criteria.

  6. Eastern Cooperative Oncology Group performance status 0 to 1.

  7. Female participants of childbearing potential and all male participants must agree to use Investigator-approved methods of birth control while on study drug and for 30 days thereafter.

  8. Patients who are willing to provide written informed consent before the predose procedures, or patients who have a legal representative capable of providing informed consent on their behalf.

Exclusion Criteria
  1. Any cytotoxic chemotherapy within 14 days prior to leukapheresis.

  2. Clinically significant malabsorption syndromes and swallowing difficulties which are inadequately controlled with medication (eg, odynophagia, dysphagia, gastroesophageal reflux disease) as per Investigator assessment.

  3. Grade 2 or greater electrolyte imbalance, per CTCAE v5.0:

    1. Potassium < 3.0 or > 5.5 mmol/L
    2. Sodium < 130 or > 150 mmol/L
    3. Calcium < 8.0 or > 11.5 mg/dL
    4. Magnesium < 0.5 or > 1.23 mmol/L
  4. Clinically significant ECG abnormality at Screening or Baseline (Day -1), including but not limited to, a confirmed QTcF value > 470 msec. Patients with QTcF readings that are borderline or difficult to interpret because of a condition such as bundle branch block, or in those where the end of the T wave is difficult to measure will be excluded. This also includes any Grade 2 or greater conduction block disorder, atrial, or ventricular arrythmia.

  5. History of clinically significant arrhythmia and/or requiring anticoagulation/antiplatelet treatment at therapeutic dose.

  6. Any clinically significant (ie, active) cardiovascular disease, including cerebral vascular accident/stroke (< 6 months before enrollment), myocardial infarction (< 6 months before enrollment) or unstable angina, and congestive heart failure ≥ New York Heart Association Classification Class III.

  7. Uncontrolled thromboembolic events or recent severe hemorrhage within the last 6 months.

  8. Known history of any bleeding disorder.

  9. Requirement for ongoing therapeutic doses of anticoagulant therapy, antiplatelet or fibrinolytic agents (low molecular weight heparin prophylaxis is allowed).

  10. Baseline systolic blood pressure <100 mmHg.

  11. History of autoimmune disease/ graft versus host disease requiring immunosuppressive therapy within the last 2 years. However, physiologic steroids (prednisone equivalent) may be given at a dose of 5 mg or less.

  12. Patients who, in the opinion of the Investigator, would be unlikely to comply with study procedures or are otherwise unsuitable for enrollment.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
CTO1681 60 μg Total Daily DoseCTO1681 20 μgParticipants receive 20 μg CTO1681 orally 3 times daily (total daily dose of 60 μg) for 15 days.
CTO1681 30 μg Total Daily DoseCTO1681 10 μgParticipants receive 10 μg CTO1681 orally 3 times daily (total daily dose of 30 μg) for 15 days.
CTO1681 90 μg Total Daily DoseCTO1681 30 μgParticipants receive 30 μg CTO1681 orally 3 times daily (total daily dose of 90 μg) for 15 days.
Primary Outcome Measures
NameTimeMethod
Incidence of adverse events (AEs)6 months following start of treatment

AEs graded by CTCAE v5.0

Secondary Outcome Measures
NameTimeMethod
Use of other anticytokine therapies6 months following the start of treatment

Use of cytokine mitigating therapies other than CTO1681

Incidence of CRS (any grade)6 months following the start of treatment

CRS graded by ASTCT Consensus Grading

Incidence of ICANS (any grade)6 months following the start of treatment

ICANS graded by ASTCT Consensus Grading

Incidence of hospitalizations6 months following the start of treatment

Unplanned hospitalizations

Proinflammatory cytokine levels6 months following the start of treatment

Concentration of proinflammatory cytokines in the blood

Concentration of CTO1681Baseline, Day 0, Day 2, Day 4, Day 6, Day 13

Concentration of CTO1681 in the blood

CAR T-cell concentration in blood6 months following the start of treatment

Concentration of CAR T-cell measured using ddPCR

CAR T-cell antitumor response6 months following the start of treatment

Antitumor response assessment using the Lugano Criteria

Trial Locations

Locations (12)

University of California, Irvine - Chao Family Comprehensive Cancer Center

🇺🇸

Orange, California, United States

Georgia Cancer Center at Augusta University

🇺🇸

Augusta, Georgia, United States

Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

Duke Cancer Institute

🇺🇸

Durham, North Carolina, United States

University of Pittsburgh Medical Center

🇺🇸

Pittsburgh, Pennsylvania, United States

Fred Hutchinson Cancer Center

🇺🇸

Seattle, Washington, United States

University of California, Irvine - Chao Family Comprehensive Cancer Center

🇺🇸

Orange, California, United States

Georgia Cancer Center at Augusta University

🇺🇸

Augusta, Georgia, United States

Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

Duke Cancer Institute

🇺🇸

Durham, North Carolina, United States

University of Pittsburgh Medical Center

🇺🇸

Pittsburgh, Pennsylvania, United States

Fred Hutchinson Cancer Center

🇺🇸

Seattle, Washington, United States

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