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Empagliflozin and Cardiac Remodelling in People Without Diabetes

Phase 4
Completed
Conditions
Cardiovascular Diseases
Left Ventricular Hypertrophy
Interventions
Drug: Placebo
Registration Number
NCT04461041
Lead Sponsor
Unity Health Toronto
Brief Summary

The purpose of this study is to evaluate the effects of empagliflozin on cardiac structure, function and circulating biomarkers in patients with cardiovascular risk factors, but without diabetes. Empagliflozin is an antihyperglycemic agent approved by Health Canada and the FDA for the treatment of type 2 diabetes. Previous post-marketing clinical trials demonstrated a reduction in cardiovascular deaths and heart failure in patients with type 2 diabetes treated with empagliflozin. In the first EMPA-HEART trial, we demonstrated that empagliflozin reduces cardiac mass in patients with type 2 diabetes, as seen through cardiac magnetic resonance imaging (cMRI). Therefore, the aim of this study, EMPA-HEART 2, is to determine whether empagliflozin can similarly impact cardiac structure in patients without diabetes, but with various cardiovascular risk factors.

Detailed Description

Sodium-glucose cotransporter 2 (SGLT2) inhibitors (empagliflozin, canagliflozin and dapagliflozin) are approved medications to improve glycemic control in adult patients with type 2 diabetes. When added to current standard-of-care diabetes treatment, SGLT2 inhibitors are associated with clinically meaningful reductions in major adverse cardiovascular events, reduced rates of hospitalization for heart failure and a decrease in major adverse kidney outcomes. Importantly, these benefits were observed consistently in people with and without type 2 diabetes and across all levels of baseline glycemic control. These data point towards a glucose-independent, cardioprotective effect of SGLT2 inhibition. How SGLT2 inhibition might reduce cardiac outcomes in people without diabetes remains unclear, and this is the specific objective of EMPA-HEART 2.

The study drug, empagliflozin (marketed as Jardiance), belongs to a class of medications that lowers blood glucose (sugar) by preventing glucose from entering back into blood circulation and ensures it is eliminated in urine. Empagliflozin is approved by the FDA and Health Canada for the treatment of type 2 diabetes.

This is a double-blind, randomized, placebo-controlled, parallel-group study of empagliflozin vs. placebo in patients without diabetes but with various cardiovascular risk factors. The purpose is to determine the effects of empagliflozin on cardiac structure by using cMRI. Patients who have given informed consent will undergo a baseline cMRI and will then be randomly assigned in a 1:1 basis to either empagliflozin 10 mg once daily or matching placebo. An end of study cMRI will be performed at 26 weeks (6 months after starting the study drug).

The study subjects will be followed for 6 months. The patients will be assessed using cMRI, which is considered the "gold standard" for measuring left ventricular (LV) volume, mass, and ejection fraction. The investigators will assess changes from baseline in LV mass, LV end-diastolic volume, end-systolic volume, LV ejection fraction, LV diastolic and systolic function, and LV wall stress via cMRI in enrolled patients treated with empagliflozin compared to those who receive placebo. Additionally, changes from baseline in blood pressure, hematocrit, and biomarkers involved in the pathophysiology of heart failure, namely NT-proBNP, will be evaluated at 6 months.

Study assessments and potential adverse events reporting will be undertaken at each study visit.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
169
Inclusion Criteria
  1. Female Not of childbearing potential and male subjects ≥ 18 and ≤ 85 years of age (Women Not of childbearing potential are females who are permanently sterile or postmenopausal. Postmenopausal is defined as 12 consecutive months with no menses without an alternative medical cause or ≥6 weeks post-surgical bilateral oophorectomy prior to Screening.)

  2. ≥1 of the major criteria or ≥2 of the minor criteria below:

    Major criteria

    • Increased LVMi of ≥96 g/m2 for women and ≥116 g/m2 for men (as calculated by echocardiogram); or LVMi ≥81 g/m2 for women and ≥85 g/m2 for men (as calculated by cMRI)
    • ECG evidence of LV hypertrophy (as per the Sokolow-Lyon criteria)
    • Structural heart disease defined as interventricular septal thickness or posterior wall thickness at end-diastole of ≥11 mm (as measured by 2D echocardiography or cMRI)
    • Persistent hypertension (defined as office blood pressure ≥140/90 mmHg) despite being on ≥3 antihypertensive medications

    Minor criteria

    • Prior history of a myocardial infarction (≥3 months ago)
    • eGFR ≥30 and ≤60 mL/min/1.73 m2 (as measured by the CKD-EPI formula)
    • Body mass index (BMI) ≥27 kg/m2
  3. Willing and able to comply with scheduled visits, treatment plan, laboratory tests, and other trial procedures

Exclusion Criteria
  1. Female subjects who are pregnant, lactating or of childbearing potential, or are pre-menopausal
  2. Known type 1 or type 2 diabetes
  3. Hemoglobin A1C (A1C) ≥6.5%
  4. eGFR <30 mL/min/1.73m2
  5. Known history of severe liver disease (e.g. Child Pugh Class B or C)
  6. Known history of severe symptomatic untreated anemia in the last 3 months (e.g. hemoglobin < 90 g/L)
  7. History of ketoacidosis, or increased chance of developing diabetic ketoacidosis (DKA) e.g. patients who suffer from excessive vomiting, diarrhea, or sweating; subjects who are on a very low carbohydrate diet; or subjects who drink a lot of alcohol.
  8. Systolic blood pressure <95mmHg (as measured at the office/clinic visit)
  9. Subjects in whom coronary revascularization by either percutaneous coronary intervention or bypass surgery is being contemplated within the next 6 months, or who have undergone coronary revascularization in the prior 3 months
  10. Significant allergy or known intolerance to SGLT2is or any ingredient in the formulations
  11. Subjects currently experiencing any clinically significant or unstable medical condition that in the opinion of the investigator might limit their ability to complete the study, or to comply with the requirements of the protocol, including: dermatologic disease, hematological disease, pulmonary disease, hepatic disease, gastrointestinal disease, genitourinary disease, endocrine disease, neurological disease, and psychiatric disease
  12. Any malignancy not considered cured (except basal cell carcinoma of the skin). A subject is considered cured if there has been no evidence of cancer recurrence for the 5 years prior to screening
  13. Subjects who have participated in other interventional studies which may affect any of the primary or secondary outcomes of the study within 30 days of the screening visit
  14. Contraindications or inability to undergo magnetic resonance imaging such as severe obesity (e.g. weight >500 lbs) or the presence of metallic fragments, clips, or devices
  15. Known history of infiltrative cardiomyopathy such as cardiac amyloidosis or cardiac sarcoidosis
  16. Severe aortic stenosis
  17. Severe aortic regurgitation
  18. Severe mitral stenosis
  19. Severe mitral regurgitation
  20. Low voltage on ECG limb leads defined by the amplitude of the QRS complex in each limb lead ≤0.5 mV

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
EmpagliflozinEmpagliflozinSingle 10 mg tablet, administered orally once daily for 6 months
PlaceboPlaceboSingle 10 mg tablet, administered orally once daily for 6 months
Primary Outcome Measures
NameTimeMethod
Left Ventricular (LV) mass6 months

Change in Left Ventricular (LV) mass (indexed to body surface area (BSA)) at 6 months. This will be measured using CMRI.

Secondary Outcome Measures
NameTimeMethod
LV end-diastolic volume6 months

Change in LV end-diastolic volume (indexed to BSA) at 6 months. This will be measured using CMRI.

LV end-systolic volume6 months

Change in LV end-systolic volume (indexed to BSA) at 6 months. This will be measured using CMRI.

LV wall stress6 months

Change in LV wall stress at 6 months. This will be measured using CMRI.

LV diastolic function6 months

Change in LV diastolic function at 6 months. This will be measured using CMRI.

Left Ventricular Ejection Fraction (LVEF)6 months

Change in LVEF at 6 months. This will be measured using CMRI.

LV systolic function6 months

Change in LV systolic function at 6 months. This will be measured using CMRI.

NT-proBNP6 months

Change in circulating NT-proBNP at 6 months.

Systolic and diastolic blood pressure6 months

Change in systolic and diastolic blood pressure at 6 months.

Hematocrit6 months

Change in hematocrit at 6 months in patients.

Trial Locations

Locations (4)

St. Michael's Hospital

🇨🇦

Toronto, Ontario, Canada

Chang Gung Memorial Hospital

🇨🇳

Keelung, Taiwan

North York Diagnostic and Cardiac Centre

🇨🇦

Toronto, Ontario, Canada

Diagnostic Assessment Centre (AMS Diagnostics)

🇨🇦

Toronto, Ontario, Canada

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