Clinical features of long-term survivors over 40 years old with Duchenne muscular dystrophy
Not Applicable
- Conditions
- Duchenne muscular dystrophy (DMD)
- Registration Number
- JPRN-UMIN000017322
- Lead Sponsor
- ational Hospital Organization
- Brief Summary
Mean age at study time is 43.6(SD 3.0) years. Mean age of loss of independent ambulation is 10.6 (SD1.5) years. Mean age of introduction of artificial ventilation is 24.1 (SD 5.5) years. Cases with NPPV and those with TIV are comparable. Mean EF of echocardiograph is 45.0 (SD 15.4) %. Twenty one cases are administered >=3 agents for cardiomyopathy, while 9 cases no agent. Seventy three percent of patients preserved oral nutritional function.
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Complete: follow-up complete
- Sex
- Male
- Target Recruitment
- 118
Inclusion Criteria
Not provided
Exclusion Criteria
DMD patients under 40 years of age at the time of the database search in July 2013 are excluded.
Study & Design
- Study Type
- Observational
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method
- Secondary Outcome Measures
Name Time Method