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Dose-Ranging Study of Telintra® Tablets + Revlimid® in Patients With Non-Deletion (5q) Low to Intermediate-1 Risk Myelodysplastic Syndrome (MDS)

Phase 1
Completed
Conditions
Myelodysplastic Syndrome
Interventions
Registration Number
NCT01062152
Lead Sponsor
Telik
Brief Summary

This is an open label, multicenter Phase 1 dose escalation study evaluating five doses of ezatiostat in combination with lenalidomide in patients with non-del(5q) low to intermediate 1 risk MDS. The HI-E, HI-N, HI-P rates \[by International Working Group (IWG) 2006 criteria\] and safety of each treatment group will be evaluated to select the optimal dose of ezatiostat in combination with lenalidomide for future studies.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
19
Inclusion Criteria
  • Histologic diagnosis of primary or de novo MDS using WHO classification
  • Non-del(5q) low or Intermediate-1risk MDS
  • ECOG performance status of 0-1
  • Documented significant cytopenia for at least 2 months
  • Must have discontinued growth factors (EPO, G-CSF, GM-CSF) for at least 21 days prior to study entry
  • All study participants must be registered into the mandatory RevAssist® program and be willing and able to comply with the requirements of RevAssist®
  • Females of childbearing potential should have two negative serum pregnancy tests with a sensitivity of at least 50 mIU/mL. The first test should be performed within 10-14 days, and the second test within 24 hours of prescribing lenalidomide (prescriptions must be filled within seven days)
Exclusion Criteria
  • Known hypersensitivity to Telintra™ (intravenous or oral)

  • Known prior therapy with or hypersensitivity to thalidomide or lenalidomide

  • Prior allogenic bone marrow transplant for MDS

  • History or prior malignancy

    • Except for treated carcinoma of uterine cervix, basal cell or squamous cell skin cancer, or other cancers (e.g. breast, prostate) for which patient has been disease-free for at least 3 years.
  • MDS evolving from:

    • A pre-existing myeloproliferative disorder
    • An autoimmune disease
    • Secondary to prior treatment with radiation or chemotherapy
  • History of MDS IPSS score>1.0

  • Pregnant or lactating women

  • Leptomeningeal or leukemic meningitis

  • Prior treatment with DNA methyltransferase inhibitors (DMTI) [e.g., azacitadine, decitabine, etc.]

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Revlimid® in Combination with Telintra ®Ezatiostat HydrochlorideLenalidomide (Revlimid®) followed by Telintra® until MDS progression or lack of efficacy.
Revlimid® in Combination with Telintra ®Lenalidomide (Revlimid®)Lenalidomide (Revlimid®) followed by Telintra® until MDS progression or lack of efficacy.
Primary Outcome Measures
NameTimeMethod
To establish the maximum tolerated dose (MTD) of ezatiostat in combination with lenalidomide2 years
To determine the safety of ezatiostat in combination with lenalidomide2 years
Secondary Outcome Measures
NameTimeMethod
To determine the efficacy of ezatiosate in combination wiht lenalidomide in patients with non-del(5q) low to intermediate-1 risk of MDS2 years
Hematologic Improvement-Erythroid (HI-E) rate2 years
Hematologic Improvement-Neutrophil (HI-N) rate2 years
Hematologic Improvement-Platelet (HI-P) rate2 years

Trial Locations

Locations (9)

University of Rochester Medical Center

🇺🇸

Rochester, New York, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

Loyola University Chicago Cardinal Benardin Cancer Center

🇺🇸

Maywood, Illinois, United States

Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Cancer Care Centers of South Texas

🇺🇸

San Antonio, Texas, United States

Mayo Clinic

🇺🇸

Phoenix, Arizona, United States

Center for Cancer and Blood Disorders

🇺🇸

Bethesda, Maryland, United States

MDAnderson

🇺🇸

Houston, Texas, United States

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