MedPath

Temozolomide in Treating Young Patients With Refractory or Recurrent Leukemia

Phase 1
Completed
Conditions
Leukemia
Interventions
Registration Number
NCT00083070
Lead Sponsor
Children's Oncology Group
Brief Summary

RATIONALE: Drugs used in chemotherapy, such as temozolomide, work in different ways to stop cancer cells from dividing so they stop growing or die.

PURPOSE: This phase I trial is studying the side effects and best dose of temozolomide in treating young patients with refractory or recurrent leukemia.

Detailed Description

OBJECTIVES:

Primary

* Determine the maximum tolerated dose and recommended phase II dose of temozolomide in pediatric patients with refractory or recurrent leukemia.

* Determine the toxic effects of this drug in these patients.

* Determine the pharmacokinetics of this drug in these patients.

Secondary

* Determine the antitumor activity of this drug in these patients.

* Determine the biologic activity and mechanism(s) of resistance to this drug in these patients.

OUTLINE: This is an open-label, dose-escalation, multicenter study.

Patients receive oral temozolomide once daily on days 1-5. Treatment repeats every 28 days for up to 12 courses in the absence of disease progression or unacceptable toxicity.

Cohorts of 3-6 patients receive escalating doses of temozolomide until the maximum tolerated dose (MTD) is determined. The MTD is defined as the dose preceding that at which 2 of 6 patients experience dose-limiting toxicity.

PROJECTED ACCRUAL: A total of 3-36 patients will be accrued for this study within 18-24 months.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
16
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Temozolomide Therapytemozolomide-
Primary Outcome Measures
NameTimeMethod
Toxicity as assessed by CTCAE 3.0
Maximum tolerated dose and recommended phase II dose
Pharmacokinetics as assessed by CI, area under the curve (AUC), and half-life (T ½)
Secondary Outcome Measures
NameTimeMethod
Antitumor activity
Biologic activity and mechanisms of resistance

Trial Locations

Locations (16)

Stanford Cancer Center at Stanford University Medical Center

🇺🇸

Stanford, California, United States

Indiana University Cancer Center

🇺🇸

Indianapolis, Indiana, United States

Fairview University Medical Center - University Campus

🇺🇸

Minneapolis, Minnesota, United States

Mayo Clinic Cancer Center

🇺🇸

Rochester, Minnesota, United States

University of Mississippi Medical Center

🇺🇸

Jackson, Mississippi, United States

Herbert Irving Comprehensive Cancer Center at Columbia University

🇺🇸

New York, New York, United States

SUNY Upstate Medical University Hospital

🇺🇸

Syracuse, New York, United States

Cincinnati Children's Hospital Medical Center

🇺🇸

Cincinnati, Ohio, United States

Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

Children's Hospital of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

Scroll for more (6 remaining)
Stanford Cancer Center at Stanford University Medical Center
🇺🇸Stanford, California, United States

MedPath

Empowering clinical research with data-driven insights and AI-powered tools.

© 2025 MedPath, Inc. All rights reserved.