MedPath

A Study of Ponsegromab in People With Heart Failure

Phase 2
Terminated
Conditions
Heart Failure
Registration Number
NCT05492500
Lead Sponsor
Pfizer
Brief Summary

The primary purpose of this clinical trial is to compare the effects of study medicine (Ponsegromab/PF-06946860) with a placebo (an injection that looks like the study medicine but does not contain the active medicine) to find out if the study medicine is better than the placebo (an injection that looks like the study medicine but does not contain the active medicine) for treatment of symptoms related to heart failure. Participants will not know which treatment group they are assigned to. Most participants in this study will receive the study medicine or placebo by shots under the skin every four weeks. People may be able to participate in this study if they have heart failure. Participants will take part in this study for about 9 months. During this time participants will visit the study clinic once a month.

A separate PK cohort within this clinical trial will receive open-label study medicine (Ponsegromab/PF-06946860) only. Participants in this open-label, PK cohort will not receive placebo. These participants will receive the study medicine by shots under the skin every four weeks. People may be able to participate in this study cohort if they also have heart failure. Participants will take part in the open-label, PK cohort for about 7 months.

Detailed Description

The primary purpose of this study is to assess the effect of repeated subcutaneous administration of ponsegromab (PF-06946860) compared to placebo on frequency, severity, and burden of symptoms as well as physical limitations in participants with heart failure and different ranges of circulating GDF-15 concentrations. The study will also assess the safety, tolerability, PK, PD, and immunogenicity of ponsegromab.

A separate, open-label, PK cohort, with more frequent PK and GDF-15 collection after single and multiple subcutaneous administration of ponsegromab (PF-06946860), will be enrolled at certain sites to facilitate a more comprehensive assessment of PK characteristics and PK/PD relationship for GDF-15 in participants with heart failure and elevated circulating GDF-15 concentrations.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
456
Inclusion Criteria
  • Male and female participants aged 18 years or older

    -. Clinical evidence of HF with each of the following criteria:

    1. LVEF <50% on most recent measurement, within 12 months of screening. Note: An assessment of LVEF in the prior 12 months is not required in situations where LVEF has been persistently <50% on prior assessments obtained at least 3 months apart (including the most recent measurement).
    2. NYHA class II-IV at screening.
    3. NT-proBNP ≥400 pg/mL at screening (Note: Does not apply to open-label, PK Cohort [Cohort B]).
  • Serum GDF-15 concentration ≥2000 pg/mL at screening.

  • Cohort D only: Serum GDF-15 concentration <2000 pg/mL at screening.

  • KCCQ-23 CSS <75 at screening (Note: Does not apply to open-label, PK Cohort [Cohort B]).

  • Evidence of cachexia or fatigue or functional impairment, as demonstrated by at least one of the following at screening (Note: Does not apply to open-label, PK Cohort [Cohort B]):

    1. Non-edematous unintentional weight loss ≥5% in the last 6 months or current BMI <20 kg/m2, associated with subjective fatigue or anorexia; or
    2. Fatigue at least 3 times per week AND at least moderately bothersome fatigue in the past 2 weeks based on the KCCQ-23 administered at screening; or
    3. A score of <60 on the Physical Limitations Domain of the KCCQ 23 administered at screening.
Exclusion Criteria
  • Acute decompensated HF within 1 month prior to Screening Visit 1 or during the screening period.
  • Implantation of a cardiac resynchronization therapy device or valve repair or replacement within 3 months prior to randomization or intent to do so during the trial.

For the open-label, PK cohort (Cohort B) only: implantation of a cardiac resynchronization therapy device more than 1 month prior to randomization is permitted.

  • History of heart transplantation, currently listed for heart transplant, current/planned mechanical circulatory support, or current/planned use of intravenous inotropes (eg, dobutamine, milrinone).
  • Acute coronary syndrome within 1 month prior to randomization.
  • Coronary revascularization (percutaneous coronary intervention or coronary artery bypass grafting) within 3 months prior to randomization or intent to undergo coronary revascularization during the trial.

For the open-label, PK cohort (Cohort B) only: coronary revascularization more than 1 month prior to randomization is permitted.

  • Untreated indication for an implantable cardiac defibrillator or pacemaker to treat a cardiac rhythm abnormality (ie, tachyarrhythmia or bradyarrhythmia).
  • Previous administration with an investigational product (drug or vaccine) within 30 days (or as determined by the local requirement) or 5 half lives (whichever is longer) preceding the first dose of study intervention used in this study. Treatment with an investigational biologic agent within 6 months or 5 half-lives (whichever is longer) of Day 1.
  • Previous exposure to ponsegromab in a prior clinical study.
  • Renal disease requiring ongoing dialysis.
  • Cirrhosis with evidence of portal hypertension not due to HF, or the following LFT abnormalities at the time of screening, confirmed by a repeat test if deemed necessary: AST or ALT level ≥ 3 x ULN, or total bilirubin level ≥ 2 x ULN (unless history of Gilbert's syndrome).

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Primary Outcome Measures
NameTimeMethod
Main cohort (Cohort A): Change from baseline in Kansas City Cardiomyopathy Questionnaire 23 Clinical Summary Scorebaseline, 22 weeks

To compare the effect of high dose ponsegromab versus placebo, on heart failure disease-specific health status in participants with HF and elevated serum GDF-15 concentrations

Secondary Outcome Measures
NameTimeMethod
Main cohort (Cohort A): Responses as defined by a ≥5 point increase from baseline in Kansas City Cardiomyopathy Questionnaire 23 Clinical Summary Scorebaseline, 22 weeks

To compare the effect of ponsegromab versus placebo on HF disease-specific health status in participants with HF and elevated serum GDF-15 concentrations

Main cohort (Cohort A): Change from baseline in Kansas City Cardiomyopathy Questionnaire 23 Overall Summary Scorebaseline, 22 weeks

To compare the effect of ponsegromab versus placebo on HF disease-specific overall health status in participants with HF and elevated serum GDF-15 concentrations

Main cohort (Cohort A): Change from baseline in Kansas City Cardiomyopathy Questionnaire 23 Total Symptom Scorebaseline, 22 weeks

To compare the effect of ponsegromab versus placebo on HF disease-specific overall health status in participants with HF and elevated serum GDF-15 concentrations

Main cohort (Cohort A): Change from baseline in Kansas City Cardiomyopathy Questionnaire 23 physical limitations domainbaseline, 22 weeks

To compare the effect of ponsegromab versus placebo on HF disease-specific overall health status in participants with HF and elevated serum GDF-15 concentrations

Main cohort (Cohort A): Responses as defined by a ≥5 point increase from baseline in Overall Summary Scorebaseline, 22 weeks

To compare the effect of ponsegromab versus placebo on HF disease-specific health status in participants with HF and elevated serum GDF-15 concentrations

Main cohort (Cohort A): Responses as defined by a ≥5 point increase from baseline in Total Symptom Scorebaseline, 22 weeks

To compare the effect of ponsegromab versus placebo on HF disease-specific health status in participants with HF and elevated serum GDF-15 concentrations

Main cohort (Cohort A): Responses as defined by a ≥5 point increase from baseline in physical limitationbaseline, 22 weeks

To compare the effect of ponsegromab versus placebo on HF disease-specific health status in participants with HF and elevated serum GDF-15 concentrations

Main cohort (Cohort A): Change from baseline in 6-Minute Walk Distancebaseline, 22 weeks

To compare the effect of ponsegromab versus placebo on the physical function of participants with HF and elevated serum GDF-15 concentrations

Main cohort (Cohort A): Change from baseline in PROMIS-Fatigue 7a which will be completed by study participants on an electronic device, so as to compare the effect of ponsegromab versus placebo on fatigue as reported by participants with HFbaseline, 22 weeks

To compare the effect of ponsegromab versus placebo on fatigue reported by participants with HF and elevated serum GDF-15 concentrations

Main cohort (Cohort A)/Cohort C/Cohort D: Incidence of treatment-emergent adverse events32 weeks

To describe the safety and tolerability of ponsegromab in participants with HF

Main cohort (Cohort A)/Cohort C/Cohort D: Incidence of treatment-emergent serious adverse events32 weeks

To describe the safety and tolerability of ponsegromab in participants with HF

Main cohort (Cohort A)/Cohort C/Cohort D: Incidence of abnormal laboratory results32 weeks

To describe the safety and tolerability of ponsegromab in participants with HF

Main cohort (Cohort A)/Cohort C/Cohort D: Incidence of abnormal vital signs32 weeks

To describe the safety and tolerability of ponsegromab in participants with HF

Open-Label, PK Cohort (Cohort B): Incidence of treatment-emergent adverse events22 weeks

To describe the safety and tolerability of ponsegromab in participants with HF

Open-Label, PK Cohort (Cohort B): Incidence of treatment-emergent serious adverse events22 weeks

To describe the safety and tolerability of ponsegromab in participants with HF

Open-Label, PK Cohort (Cohort B): Incidence of abnormal laboratory results22 weeks

To describe the safety and tolerability of ponsegromab in participants with HF

Open-Label, PK Cohort (Cohort B): Incidence of abnormal vital signs22 weeks

To describe the safety and tolerability of ponsegromab in participants with HF

Trial Locations

Locations (121)

Vseobecna fakultni nemocnice v Praze

🇨🇿

Praha 2, Czechia

Ustredni vojenska nemocnice

🇨🇿

Praha 6, Czechia

Universitätsklinikum Frankfurt Goethe-Universität

🇩🇪

Frankfurt, Hessen, Germany

SPZOZ Centralny Szpital Kliniczny Uniwersytetu Medycznego w Lodzi

🇵🇱

Lodz, Poland

Polsko Amerykanskie Kliniki Serca

🇵🇱

Tychy, Poland

Hospital Universitario Virgen de la Victoria

🇪🇸

Málaga, Spain

Lincoln County Hospital

🇬🇧

Lincoln, United Kingdom

CardioVasc HR Inc

🇨🇦

Saint-Jean-sur-Richelieu, Quebec, Canada

Kawartha Cardiology Clinical Trials

🇨🇦

Peterborough, Ontario, Canada

Corcare

🇨🇦

Toronto, Ontario, Canada

Unity Health Toronto, St. Michael's Hospital

🇨🇦

Toronto, Ontario, Canada

Community Care Building

🇨🇦

Winchester, Ontario, Canada

Winchester District Memorial Hospital

🇨🇦

Winchester, Ontario, Canada

Pécsi Tudományegyetem Klinikai Központ

🇭🇺

Pécs, Baranya, Hungary

Private Practice - Dr. Lakatos Ferenc

🇭🇺

Békéscsaba, Békés, Hungary

Eastern shore Research Institute LLC

🇺🇸

Fairhope, Alabama, United States

Keck Medical Center of USC

🇺🇸

Los Angeles, California, United States

MedStar Washington Hospital Center

🇺🇸

Washington, District of Columbia, United States

Emory University School of Medicine-Grady Campus

🇺🇸

Atlanta, Georgia, United States

Chicago Medical Research

🇺🇸

Hazel Crest, Illinois, United States

Reid Physician Associates

🇺🇸

Richmond, Indiana, United States

Brigham and Women's Hospital

🇺🇸

Boston, Massachusetts, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

Traverse Heart & Vascular

🇺🇸

Traverse City, Michigan, United States

M Health Fairview Clinics and Surgery Center

🇺🇸

Minneapolis, Minnesota, United States

M Health Fairview University of Minnesota Investigational Drug Services

🇺🇸

Minneapolis, Minnesota, United States

M Health Fairview University of Minnesota Medical Center-East Bank

🇺🇸

Minneapolis, Minnesota, United States

University of Minnesota/Lillehei Clinical Research Unit

🇺🇸

Minneapolis, Minnesota, United States

Saint Luke's Hospital of Kansas City

🇺🇸

Kansas City, Missouri, United States

Washington University in St. Louis Center for Outpatient Health (COH)

🇺🇸

Saint Louis, Missouri, United States

Washington University in St. Louis Center for Advanced Medicine (CAM)

🇺🇸

Saint Louis, Missouri, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

Holy Name Medical Center

🇺🇸

Teaneck, New Jersey, United States

University of North Carolina Medical Center

🇺🇸

Chapel Hill, North Carolina, United States

Clinical and Translational Research Center

🇺🇸

Chapel Hill, North Carolina, United States

South Oklahoma Heart Research, LLC

🇺🇸

Oklahoma City, Oklahoma, United States

Texas Health Physicians Group

🇺🇸

Dallas, Texas, United States

Concord Repatriation General Hospital

🇦🇺

Concord, New South Wales, Australia

Core Research Group

🇦🇺

Brisbane, Queensland, Australia

The Prince Charles Hospital

🇦🇺

Chermside, Queensland, Australia

Lyell McEwin Hospital

🇦🇺

Elizabeth Vale, South Australia, Australia

The Alfred Hospital

🇦🇺

Melbourne, Victoria, Australia

Fraser Clinical Trials Inc

🇨🇦

New Westminster, British Columbia, Canada

QEII Health Sciences Centre - Victoria General Site

🇨🇦

Halifax, Nova Scotia, Canada

Saul Vizel Professional Medicine Corporation dba Vizel Cardiac Research

🇨🇦

Cambridge, Ontario, Canada

University Hospital - London Health Sciences Centre

🇨🇦

London, Ontario, Canada

North York Diagnostic and Cardiac Centre

🇨🇦

North York, Ontario, Canada

Private Practice - Dr. James Cha

🇨🇦

Oshawa, Ontario, Canada

Institut de Cardiologie de Montreal

🇨🇦

Montreal, Quebec, Canada

Centre Hospitalier de l'Université de Montréal

🇨🇦

Montréal, Quebec, Canada

Centre intégré de santé et de services sociaux du Bas Saint-Laurent- Hôpital régional de Rimouski

🇨🇦

Rimouski, Quebec, Canada

Centre intégré de santé et de services sociaux de Lanaudière - Hopital Pierre-Le Gardeur.

🇨🇦

Terrebonne, Quebec, Canada

Diex Recherche Trois-Rivieres

🇨🇦

Trois-Rivieres, Quebec, Canada

Guangdong Provincial People's Hospital

🇨🇳

Guangzhou, Guangdong, China

The First Affiliated Hospital, Sun Yat-sen University

🇨🇳

Guangzhou, Guangdong, China

The Second Xiangya Hospital of Central South University

🇨🇳

Changsha, Hunan, China

The First Affiliated Hospital of University of South China

🇨🇳

Hengyang, Hunan, China

China-Japan Union Hospital

🇨🇳

Changchun, Jilin, China

The First Affiliated Hospital of Xi'an Jiaotong University

🇨🇳

Xi'an, Shaanxi, China

Qilu Hospital of Shandong University

🇨🇳

Jinan, Shandong, China

Zhongshan Hospital,Fudan University

🇨🇳

Shanghai, Shanghai, China

Yuncheng Central Hospital

🇨🇳

Yuncheng, Shanxi, China

Tianjin People' s Hospital

🇨🇳

Tianjin, Tianjin, China

Peking University First Hospital

🇨🇳

Beijing, China

Fakultni Nemocnice u sv. Anny v Brne

🇨🇿

Brno, Jihomoravský KRAJ, Czechia

EDUMED - Jaroměř

🇨🇿

Jaroměř, Náchod, Czechia

Institut Klinicke a Experimentalni Mediciny

🇨🇿

Prague, Praha 4, Czechia

Fakultni nemocnice Kralovske Vinohrady

🇨🇿

Praha 10, Czechia

Universitätsmedizin Göttingen - Georg-August-Universität

🇩🇪

Göttingen, Niedersachsen, Germany

Herz - und Diabeteszentrum Nordrhein - Westfalen, Bad Oeynhausen

🇩🇪

Bad Oeynhausen, Nordrhein-westfalen, Germany

Hausärztlich-Kardiologisches MVZ am Felsenkeller GmbH/Zentrum für klinische Studien

🇩🇪

Dresden, Sachsen, Germany

Universitätsklinikum Jena

🇩🇪

Jena, Thüringen, Germany

TaNa Med

🇭🇺

Mosonmagyaróvár, Győr-moson-sopron, Hungary

Medifarma 98 Kft

🇭🇺

Nyiregyhaza, Nyíregyháza, Hungary

Somogy Vármegyei Kaposi Mór Oktató Kórház

🇭🇺

Kaposvár, Somogy, Hungary

Dél-Pesti Centrumkórház Orszagos Hematologiai es Infektologiai Intezet

🇭🇺

Budapest, Hungary

Semmelweis Egyetem

🇭🇺

Budapest, Hungary

Kanizsai Dorottya Korhaz

🇭🇺

Nagykanizsa, Hungary

Hyogo Prefectural Amagasaki General Medical Center

🇯🇵

Amagasaki, Hyogo, Japan

Hyogo Prefectural Harima-Himeji General Medical Center

🇯🇵

Himeji, Hyogo, Japan

Higashi Takarazuka Satoh Hospital

🇯🇵

Takarazuka, Hyogo, Japan

Iwate Prefectural Central Hospital

🇯🇵

Morioka, Iwate, Japan

National Hospital Organization Sendai Medical Center

🇯🇵

Sendai, Miyagi, Japan

Kishiwada Tokushukai Hospital

🇯🇵

Kishiwada, Osaka, Japan

National Cerebral and Cardiovascular Center

🇯🇵

Suita, Osaka, Japan

National Hospital Organization Saitama Hospital

🇯🇵

Wako, Saitama, Japan

Keio University Hospital

🇯🇵

Shinjuku-ku, Tokyo, Japan

Osaka General Medical Center

🇯🇵

Osaka, Japan

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wrocławiu

🇵🇱

Wrocław, Dolnośląskie, Poland

Uniwersytecki Szpital Kliniczny w Białymstoku

🇵🇱

Białystok, Podlaskie, Poland

Miejski Szpital Zespolony w Olsztynie

🇵🇱

Olsztyn, Warmińsko-mazurskie, Poland

Uniwersytecki Szpital Kliniczny w Poznaniu

🇵🇱

Poznan, Wielkopolskie, Poland

Uniwersyteckie Centrum Kliniczne Warszawskiego Uniwersytetu Medycznego Centralny Szpital Kliniczny

🇵🇱

Warsaw, Poland

Kardio Brynow

🇵🇱

Katowice, Śląskie, Poland

CHUAC-Complejo Hospitalario Universitario A Coruña

🇪🇸

A Coruña, A Coruña [LA Coruña], Spain

CHUS - Hospital Clinico Universitario

🇪🇸

Santiago de Compostela, A Coruña [LA Coruña], Spain

Parc de Salut Mar - Hospital del Mar

🇪🇸

Barcelona, Barcelona [barcelona], Spain

Hospital Universitari Vall d'Hebron

🇪🇸

Barcelona, Barcelona [barcelona], Spain

Hospital Universitari de Bellvitge

🇪🇸

L'Hospitalet de Llobregat, Barcelona, Spain

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Catalunya [cataluña], Spain

Hospital Universitario Ramón y Cajal

🇪🇸

Madrid, Madrid, Comunidad DE, Spain

Hospital Universitario Puerta de Hierro Majadahonda

🇪🇸

Majadahonda, Madrid, Comunidad DE, Spain

Hospital Clínico Universitario Virgen de la Arrixaca

🇪🇸

El Palmar, Murcia, Región DE, Spain

Hospital Clinico de Valencia

🇪🇸

Valencia, Valenciana, Comunitat, Spain

Hospital Universitario Virgen Nieves

🇪🇸

Granada, Spain

Hospital Universitario La Paz

🇪🇸

Madrid, Spain

Hospital Universitario Central de Asturias

🇪🇸

Oviedo, Spain

Hospital Universitario Virgen Del Rocio

🇪🇸

Sevilla, Spain

Hospital General Universitario de Valencia

🇪🇸

Valencia, Spain

Hospital Universitari i Politecnic La Fe

🇪🇸

Valencia, Spain

Wycombe General Hospital

🇬🇧

High Wycombe, Buckinghamshire, United Kingdom

Ninewells Hospital and Medical School

🇬🇧

Dundee, Dundee CITY, United Kingdom

St. George's Hospital

🇬🇧

London, England AND Wales, United Kingdom

Northwick Park Hospital

🇬🇧

Harrow, London, CITY OF, United Kingdom

Glasgow Royal Infirmary

🇬🇧

Glasgow, Scotland, United Kingdom

Barnet Hospital

🇬🇧

Barnet, United Kingdom

Royal Papworth Hospital NHS Foundation Trust

🇬🇧

Cambridge, United Kingdom

Golden Jubilee National Hospital

🇬🇧

Clydebank, United Kingdom

Liverpool University Hospitals NHS Foundation Trust

🇬🇧

Liverpool, United Kingdom

Northern General Hospital

🇬🇧

Sheffield, United Kingdom

University Hospital of North Tees

🇬🇧

Stockton-On-Tees, United Kingdom

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