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Clinical Trials/ISRCTN58752772
ISRCTN58752772
Active, Not Recruiting
N/A

on-interventional study to investigate the effectiveness of emicizumab under real-world conditions in pediatric, adolescent, adult and elderly patients with hemophilia A with and without FVIII inhibitors

Roche (Germany)0 sites168 target enrollmentFebruary 9, 2022

Overview

Phase
N/A
Intervention
Not specified
Conditions
Not specified
Sponsor
Roche (Germany)
Enrollment
168
Status
Active, Not Recruiting
Last Updated
2 years ago

Overview

Brief Summary

No summary available.

Registry
who.int
Start Date
February 9, 2022
End Date
January 31, 2025
Last Updated
2 years ago
Study Type
Observational
Sex
Male

Investigators

Sponsor
Roche (Germany)

Eligibility Criteria

Inclusion Criteria

  • 1\. Participants of any age with congenital severe haemophilia A with or without FVIII inhibitors
  • 2\. Participants undergoing treatment with emicizumab according to Summary of Product Characteristics (SPC) (start of treatment with emicizumab maximum 3 months prior to study entry)
  • 3\. Must sign informed consent by the legal representative or participant or both, as required
  • 4\. Selection criteria for Cohort A include participants diagnosed with severe congenital haemophilia A (\<1% FVIII activity) and no present FVIII inhibitor at the start of emicizumab treatment, patients who completed successful ITI before the start of Emicizumab treatment are eligible.
  • 5\. Selection criteria for Cohort B include participants diagnosed with congenital haemophilia A (any severity) with FVIII inhibitor activity at the start of emicizumab treatment or ongoing ITI at the start of emicizumab treatment

Exclusion Criteria

  • 1\. Participants having bleeding disorder other than congenital haemophilia A
  • 2\. Treatment with emicizumab outside of the SPC at study entry
  • 3\. Any contraindication for treatment with emicizumab according to current SPC
  • 4\. Current participation in an interventional study

Outcomes

Primary Outcomes

Not specified

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