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Study of TT-00420 (Tinengotinib) in Subjects With Cholangiocarcinoma Who Failed or Relapsed to Chemotherapy and FGFR Inhibitor

Phase 2
Recruiting
Conditions
Cholangiocarcinoma Metastatic
Interventions
Drug: TT-00420 (tinengotinib)
Registration Number
NCT06057571
Lead Sponsor
TransThera Sciences (Nanjing), Inc.
Brief Summary

A phase II, open-label, multicenter study to evaluate the efficacy and safety of oral TT-00420 (Tinengotinib) tablets in subjects with cholangiocarcinoma who failed or relapsed to prior treatment of chemotherapy and FGFR Inhibitor.

Detailed Description

Approximately 50 subjects will be enrolled. Eligible subjects will receive tinengotinib 10 mg QD orally as the initial dose level in 21-day cycles until confirmed disease progression, intolerable toxicity, death, or withdrawal of consent.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
50
Inclusion Criteria
  1. ≥ 18 years of age at the time of signing the informed consent form (ICF).
  2. Histologically or cytologically confirmed CCA/adenocarcinoma of biliary origin with radiological evidence of unresectable or metastatic disease.
  3. Subjects must have received one or two lines of prior systemic chemotherapy.
  4. Documentation of FGFR2 gene alteration and must have failed to prior treatment of exactly one FGFR inhibitor.
  5. At least one measurable lesion as defined by RECIST V1.1 criteria for solid tumors.
  6. ECOG≤ 1.
  7. Adequate organ and bone marrow function(without receiving any hematopoietic growth factor, blood or platelet therapy within 14 days before the first dose).
  8. Must agree to take sufficient contraceptive methods to avoid pregnancy during the study and until at least 3 months after ceasing study treatment.
  9. Able to sign informed consent and comply with the protocol.
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Exclusion Criteria
  1. Subjects with concomitant brain or central nervous system (CNS) metastases and imaging or clinically confirmed progression within 28 days prior to the start of treatment. Brain or central nervous system metastases that not treated with corticosteroids and remain stable within 14 days prior to screening are eligible for enrollment.
  2. Subjects with a known concurrent malignancy that is progressing or requires active treatment. Exceptions include basal cell carcinoma of the skin, carcinoma in situ of the cervix, or other noninvasive or indolent malignancy, including those that have previously undergone potentially curative therapy.
  3. Subjects who have received prior systemic therapy or investigational study drug ≤ 5 half-lives or 14 days, whichever is shorter, prior to starting the study drug or who have not recovered (grade ≤ 1 or at pretreatment baseline except tolerable grade 2 alopecia, fatigue/asthenia, and neuropathy due to trauma) from adverse events (AEs) of prior therapy.
  4. Concurrent anticancer therapy including chemo-, immune-, or radiotherapy. Hormone therapy may be allowed with Sponsor approval.
  5. Subjects who have received wide field radiotherapy ≤ 4 weeks or limited field radiation for palliation ≤ 2 weeks prior to starting the study drug or who have not recovered from AEs of prior therapy.
  6. Subjects who have underwent major surgery or have not recovered from adverse events of surgery within the 4 weeks prior to initiation of the investigational drug (grade ≤ 1 or at pretreatment baseline except tolerable grade 2 alopecia, fatigue/asthenia, and neuropathy due to trauma).
  7. Impaired cardiac function or significant diseases.
  8. Subjects who have received stable doses of antihypertensive drugs for at least 1 week with uncontrolled hypertension under at screening period (defined as blood pressure of ≥ 150 mm Hg systolic and/or ≥ 90 mm Hg diastolic despite adequate treatment with antihypertensive medications at screening).
  9. Subjects who have severe gastrointestinal disease or gastrointestinal dysfunction that may lead to absorption, metabolism or excretion of the study drug, enrollment eligibility will be based on the investigator's judgment (including but not limited to total gastrotomy, short bowel syndrome).
  10. Subjects who have bleeding disorders or thrombotic disorders or therapeutic anticoagulant therapy requiring INR monitoring.
  11. Subjects who have received a strong CYP3A inhibitor and inducer before starting the study drug, within an interval of ≤ 2 weeks or 5 half-lives (whichever is shorter); (except topical ketoconazole).
  12. Tested positive for the human immunodeficiency virus (HIV).
  13. Subjects who have an active HBV infection.
  14. Subjects who are pregnant or breastfeeding.
  15. Subjects who are unable to swallow or tolerate oral medication.
  16. The investigator determines that he or she is not eligible for study participation for any clinical or laboratory abnormalities, or any reason that could confuse the study results, interfere with participants' safe participation and compliance with the trial procedure.
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Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
TT-00420 (tinengotinib) Tablet MonotherapyTT-00420 (tinengotinib)TT-00420 (tinengotinib) tablets will be administered once daily in 21-day cycles with initial dosage of 10 mg QD.
Primary Outcome Measures
NameTimeMethod
Objective Response Rate (ORR) by BICRThrough study completion, an average of 1 year

The proportion of subjects who achieved a complete response (CR) or a partial response (PR) based on RECIST version 1.1.

Secondary Outcome Measures
NameTimeMethod
Duration of response (DOR)Through study completion, an average of 1 year

Duration of response for CR or PR based on RECIST version 1.1.

ORR by InvestigatorThrough study completion, an average of 1 year

The proportion of subjects who achieved a complete response (CR) or a partial response (PR) based on RECIST version 1.1.

Incidence, duration, and severity of adverse events (AEs)Up to 28 days from study discontinuation

As assessed per Common Terminology Criteria for Adverse Events (CTCAE) v5.0 (or the most current version).

Progression-free survival (PFS)Through study completion, an average of 1 year

From first study drug administration until the date of first documented progression or date of death from any cause, whichever came first

Disease control rate (DCR)Through study completion, an average of 1 year

The proportion of subjects who achieved a complete response (CR) or a partial response (PR) or a stable disease (SD) based on RECIST version 1.1.

Overall Survival (OS)Through study completion, an average of 1 year

From first study drug administration until the date of death from any cause

Trial Locations

Locations (28)

Shandong Cancer Hospital

🇨🇳

Jinan, Shandong, China

Shenzhen Qianhai Shekou Free Trade Zone hospital

🇨🇳

Shenzhen, Guangdong, China

Central Hospital Affiliated to Shangdong First Medical University

🇨🇳

Jinan, Shandong, China

Eastern Hepatobiliary Surgery Hospital

🇨🇳

Shanghai, Shanghai, China

Tianjin medical university cancer institute & hospital

🇨🇳

Tianjin, China

Anhui Provincial Hospital

🇨🇳

Hefei, Anhui, China

Peking Union Medical College Hospital

🇨🇳

Beijing, Beijing, China

Zhujiang Hospital of Southern Medical University

🇨🇳

Guangzhou, Guangdong, China

The Fourth Hospital of Hebei Medical University

🇨🇳

Shijiazhuang, Hebei, China

Harbin Medical University Cancer Hospital

🇨🇳

Harbin, Heilongjiang, China

The First Affiliated Hospital of Zhengzhou University

🇨🇳

Zhengzhou, Henan, China

Henan Cancer Hospital

🇨🇳

Zhengzhou, Henan, China

Hubei Cancer Hospital

🇨🇳

Wuhan, Hubei, China

Zhongnan hospital of Wuhan University

🇨🇳

Wuhan, Hubei, China

Nanjing Drum Tower Hospital

🇨🇳

Nanjing, Jiangsu, China

Hunan Cancer Hospital

🇨🇳

Changsha, Hunan, China

Hunan Provincial People's Hospital

🇨🇳

Changsha, Hunan, China

Jilin Cancer Hospital

🇨🇳

Changchun, Jilin, China

Liaoning Cancer Hospital

🇨🇳

Shenyang, Liaoning, China

Yunnan Cancer Hospital

🇨🇳

Kunming, Yunnan, China

Shanxi Cancer Hospital

🇨🇳

Taiyuan, Shanxi, China

Sichuan Cancer Hospital

🇨🇳

Chengdu, Sichuan, China

Zhejiang Cancer Hospital

🇨🇳

Hangzhou, Zhejiang, China

Beijing Cancer Hospital

🇨🇳

Beijing, China

Fudan University Shanghai Cancer Hospital

🇨🇳

Shanghai, China

Beijing Tsinghua Changgeng Hospital

🇨🇳

Beijing, China

Zhongshan Hospital

🇨🇳

Shanghai, China

Fujian Cancer Hospital

🇨🇳

Fuzhou, Fujian, China

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