MedPath

Efficacy and Safety of Idelalisib (GS-1101) in Combination With Bendamustine and Rituximab for Previously Treated Indolent Non-Hodgkin Lymphomas

Phase 3
Terminated
Conditions
Indolent Non-Hodgkin's Lymphomas
Interventions
Registration Number
NCT01732926
Lead Sponsor
Gilead Sciences
Brief Summary

The primary objective of this study is to evaluate the addition of idelalisib to bendamustine/rituximab on progression-free survival (PFS) in adults with previously treated indolent non-Hodgkin lymphoma (iNHL).

An increased rate of deaths and serious adverse events (SAEs) among participants with front-line chronic lymphocytic leukemia (CLL) and early-line iNHL treated with idelalisib in combination with standard therapies was observed by the independent data monitoring committee (DMC) during regular review of 3 Gilead Phase 3 studies. Gilead reviewed the unblinded data and terminated this study in agreement with the DMC recommendation and in consultation with the US Food and Drug Administration (FDA).

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
475
Inclusion Criteria
  • Histologically confirmed diagnosis of B-cell iNHL, with histological subtype limited to the following

    1. Follicular lymphoma (FL) Grade 1, 2, or 3a
    2. Small lymphocytic lymphoma (SLL)
    3. Lymphoplasmacytoid lymphoma/Waldenström macroglobulinemia (LPL/WM)
    4. Marginal zone lymphoma (MZL) (splenic, nodal, or extra-nodal)

Key

Exclusion Criteria
  • History of lymphoid malignancy other than those allowed per inclusion criteria.
  • Ongoing drug-induced liver injury, active hepatitis C, active hepatitis B, alcoholic liver disease, non-alcoholic steatohepatitis, primary biliary cirrhosis, extrahepatic obstruction caused by cholelithiasis, cirrhosis of the liver, or portal hypertension.
  • Prior treatment with bendamustine that was not effective.

Note: Other protocol defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Rituximab + Bendamustine + IdelalisibIdelalisibParticipants will receive rituximab + bendamustine + idelalisib.
Rituximab + Bendamustine + IdelalisibRituximabParticipants will receive rituximab + bendamustine + idelalisib.
Rituximab + Bendamustine + IdelalisibBendamustineParticipants will receive rituximab + bendamustine + idelalisib.
Rituximab + Bendamustine + PlaceboRituximabParticipants will receive rituximab + bendamustine + placebo.
Rituximab + Bendamustine + PlaceboPlaceboParticipants will receive rituximab + bendamustine + placebo.
Rituximab + Bendamustine + PlaceboBendamustineParticipants will receive rituximab + bendamustine + placebo.
Primary Outcome Measures
NameTimeMethod
Progression-free Survival (PFS)

PFS is defined as the interval from randomization to the earlier of the first documentation of definitive indolent non-Hodgkin lymphomas (iNHL) disease progression or death from any cause. Definitive iNHL disease progression is progression based on standard criteria. PFS was to be assessed by an independent review committee (IRC).

Secondary Outcome Measures
NameTimeMethod
Overall Response Rate (ORR)

Overall response rate is defined as the proportion of participants who achieve a complete response or partial response (or very good partial response (VGPR) or minor response (MR) for participants with Waldenstrom's). ORR was to be assessed by an IRC.

Lymph Node Response Rate

Lymph node response rate is defined as the proportion of participants who achieve ≥ 50% decrease from baseline in the sum of the products of the greatest perpendicular diameters of index lesions. Lymph node response rate was to be assessed by an IRC.

Overall Survival (OS)

Overall survival is defined as the interval from randomization to death from any cause.

Complete Response Rate (CR)

Complete response rate is defined as the proportion of participants who achieve a complete response. CR rate was to be assessed by an IRC.

Trial Locations

Locations (141)

Centre Hospitalier Universitaire de Sherbrooke

🇨🇦

Sherbrooke, Quebec, Canada

Cancer Center of Kansas

🇺🇸

Wichita, Kansas, United States

Azienda Ospedaliero-Universitaria di Bologna - Policlinico S.Orsola-Malpighi

🇮🇹

Bologna, Italy

Spedali Civili Di Brescia Azienda Ospedaliera

🇮🇹

Brescia, Italy

Azienda Ospedaliero Universitaria (AOU) "Maggiore della Carita" di Novara

🇮🇹

Novara, Italy

Azienda Ospedaliera Universitaria Senese - Policlinico S. Maria alle Scotte

🇮🇹

Siena, Italy

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Swedish Medical Center

🇺🇸

Seattle, Washington, United States

Christie Hospital NHS Foundation Trust

🇬🇧

Manchester, England, United Kingdom

State Budgetary Healthcare Institution "Volgograd Regional Clinical Oncology Dispensary #1"

🇷🇺

Volgograd, Russian Federation

Hospital Universitario Puerta de Hierro

🇪🇸

Majadahonda, Madrid, Spain

FSI "V.A. Almazov Federal Centre of Heart, Blood and Endocrinology of Rosmedtechnologies"

🇷🇺

Saint Petersburg, Russian Federation

Hospital Universitari Germans Trias i Pujol

🇪🇸

Badalona, Spain

Saint Jude Heritage Healthcare (TORI)

🇺🇸

Fullerton, California, United States

Pacific Shores Medical Group

🇺🇸

Long Beach, California, United States

Cancer Care Associates

🇺🇸

Redondo Beach, California, United States

San Luis Obispo Oncology and Hematology

🇺🇸

San Luis Obispo, California, United States

Cancer Center of Santa Barbara

🇺🇸

Santa Barbara, California, United States

Kaiser Permanente Vallejo Medical Center

🇺🇸

Vallejo, California, United States

Sylvester Comprehensive Cancer Center/UMHC

🇺🇸

Deerfield Beach, Florida, United States

Cancer Specialists of North Florida

🇺🇸

Jacksonville, Florida, United States

Northwest Georgia Oncology Centers, PC

🇺🇸

Marietta, Georgia, United States

Joliet Oncology Hematology Associates Ltd.

🇺🇸

Joliet, Illinois, United States

Rutgers Cancer Institute of New Jersey

🇺🇸

New Brunswick, New Jersey, United States

North Shore Hematology/Oncology Associates

🇺🇸

East Setauket, New York, United States

Weill Cornell Medical College

🇺🇸

New York, New York, United States

Signal Point Clinical Research Center, LLC

🇺🇸

Middletown, Ohio, United States

Hollings Cancer Center

🇺🇸

Charleston, South Carolina, United States

Texas Oncology, P.A.

🇺🇸

Weslaco, Texas, United States

Brooke Army Medical Center

🇺🇸

Fort Sam Houston, Texas, United States

Charles A. Sammons Cancer Center

🇺🇸

Dallas, Texas, United States

Northwest Medical Specialists

🇺🇸

Tacoma, Washington, United States

Royal Adelaide Hospital

🇦🇺

Adelaide, South Australia, Australia

Haematology and Oncology Clinics of Australia Gold Coast

🇦🇺

South Brisbane, Queensland, Australia

Adelaide Cancer Centre

🇦🇺

Kurralta Park, South Australia, Australia

Box Hill Hospital

🇦🇺

Box Hill, Victoria, Australia

Monash Medical Centre

🇦🇺

Clayton, Victoria, Australia

Saint Vincent's Hospital

🇦🇺

Fitzroy, Victoria, Australia

Royal Perth Hospital

🇦🇺

Perth, Western Australia, Australia

Tom Baker Cancer Center

🇨🇦

Calgary, Alberta, Canada

Royal Victoria Regional Health Centre

🇨🇦

Barrie, Ontario, Canada

Hôpital Charles Lemoyne

🇨🇦

Greenfield Park, Quebec, Canada

Sunnybrook Health Sciences Centre

🇨🇦

Toronto, Ontario, Canada

Centre Hospitalier Affilie Universitaire de Quebec

🇨🇦

Quebec, Canada

CancerCare Manitoba

🇨🇦

Winnipeg, Canada

Fakultní Nemocnice Ostrava

🇨🇿

Ostrava - Poruba, Severomoravsky KRAJ, Czechia

Fakultní nemocnice Brno

🇨🇿

Brno, Czechia

Fakultní nemocnice Hradec Králové

🇨🇿

Hradec Králové, Czechia

Institut Bergonié

🇫🇷

Bordeaux Cedex, Aquitaine, France

Centre Henri-Becquerel

🇫🇷

Rouen Cedex 1, Haute-normandie, France

Hôpital Necker-Enfants Malades

🇫🇷

Paris, Ile-de-france, France

Centre Hospitalier Lyon Sud

🇫🇷

Pierre Bénite Cedex, Rhone-alpes, France

Centre Hospitalier Universitaire Brest

🇫🇷

Brest Cedex, France

Centre Hospitalier Départmental La Roche sur Yon

🇫🇷

La Roche sur Yon, France

Centre Léon Bérard

🇫🇷

Lyon Cedex 08, France

Institut Paoli Calmettes

🇫🇷

Marseille, France

Hôpital Hôtel-Dieu

🇫🇷

Nantes cedex 1, France

Centre Hospitalier Universitaire de Poitiers

🇫🇷

Poitiers Cedex, France

Centre Hospitalier Régional et Universitaire - Hôpital Bretonneau

🇫🇷

Tours, France

Institut Gustave Roussy

🇫🇷

Villejuif, France

Schwarzwald-Baar Klinikum Villingen-Schwenningen GmbH

🇩🇪

Villingen-Schwenningen, Baden-wuerttemberg, Germany

Gemeinschaftspraxis Dres. Söling Und Siehl

🇩🇪

Kassel, Hessen, Germany

Vivantes Klinikum am Urban

🇩🇪

Berlin, Germany

Charite - Campus Virchow

🇩🇪

Berlin, Germany

Barzilai Medical Center

🇮🇱

Ashkelon, Israel

Soroka University Medical Center

🇮🇱

Beer Sheva, Israel

Centro di Riferimento Oncologico di Aviano

🇮🇹

Aviano, Italy

Hadassah Medical Organization, Ein Kerem

🇮🇱

Jerusalem, Israel

IRCCS Azienda Ospedaliera Universitaria San Martino

🇮🇹

Genova, Italy

Ospedale San Raffaele-IRCCS

🇮🇹

Milano, Italy

Azienda Ospedaliera Ospedale Niguarda Ca' Granda

🇮🇹

Milano, Italy

Azienda Ospedaliera Ospedali Riuniti Marche Nord

🇮🇹

Pesaro, Italy

Azienda Unità Sanitaria Locale di Piacenza-Ospedale Guglielmo da Saliceto

🇮🇹

Piacenza, Italy

Azienda Ospedaliera Città della Salute e della Scienza di Torino

🇮🇹

Torino, Italy

Dong-A University Medical Center

🇰🇷

Busan, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Uniwersyteckie Centrum Kliniczne

🇵🇱

Gdansk, Poland

Szpital Kliniczny nr 1, Katedra i Klinika Hematoonkologii i Transplantacji Szpiku

🇵🇱

Lublin, Poland

Wojewódzki Szpital Specjalistyczny im. Janusza Korczaka w Slupsku

🇵🇱

Slupsk, Poland

Sverdlovsk Regional Clinical Hospital #1

🇷🇺

Ekaterinburg, Russian Federation

Central City Hospital # 7

🇷🇺

Ekaterinburg, Russian Federation

Nizhny Novgorod Regional Clinical Hospital n.a. N.A. Semashko

🇷🇺

Nizhniy Novgorod, Russian Federation

Hospital Universitario La Princesa

🇪🇸

Madrid, Spain

Hospital General Universitario Gregorio Marañon

🇪🇸

Madrid, Spain

Hospital Clínico Universitario de Salamanca

🇪🇸

Salamanca, Spain

Hospital Universitario Virgen del Rocio

🇪🇸

Sevilla, Spain

Karolinska Universitetssjukhuset

🇸🇪

Huddinge, Stockholm, Sweden

Hospital Universitari i Politecnic La Fé de Valencia

🇪🇸

Valencia, Spain

Länssjukhuset Ryhov

🇸🇪

Jönköping, Sweden

China Medical University Hospital

🇨🇳

Taichung, Taiwan

National Cheng-Kung University Hospital

🇨🇳

Tainan, Taiwan

Kent and Canterbury Hospital

🇬🇧

Canterbury, England, United Kingdom

University Hospital Coventry

🇬🇧

Coventry, England, United Kingdom

Royal Bournemouth General Hospital

🇬🇧

Dorset, England, United Kingdom

Imperial College Healthcare NHS Trust

🇬🇧

London, England, United Kingdom

Mount Vernon Hospital

🇬🇧

Middlesex, United Kingdom

New Cross Hospital

🇬🇧

Wolverhampton, United Kingdom

Centre Jean Bernard

🇫🇷

Le Mans, PAYS DE LA Loire, France

Centre Hospitalier de Dunkerque

🇫🇷

Dunkerque, France

Western Hospital

🇦🇺

Footscray, Victoria, Australia

Wojewódzki Szpital Specjalistyczny im. Mikolaja Kopernika w Lodzi

🇵🇱

Lódz, Poland

Queen Elizabeth II Health Sciences Centre, Centre for Clinical Research

🇨🇦

Halifax, Nova Scotia, Canada

Rambam Health Corp.

🇮🇱

Haifa, Israel

Aurora BayCare Medical Center

🇺🇸

Green Bay, Wisconsin, United States

Bon Secours Saint Francis Hospital

🇺🇸

Greenville, South Carolina, United States

Fraser Clinical Trials, Inc.

🇨🇦

New Westminster, British Columbia, Canada

McGill University Health Centre

🇨🇦

Montréal, Quebec, Canada

Centre Hospitalier Universitaire de Strasbourg - Hôpital Hautepierre

🇫🇷

Strasbourg Cedex, Alsace, France

Samodzielny Publiczny Zaklad Opieki Zdrowotnej Ministerstwa Spraw Wewnetrznych z Warminsko-Mazurskim

🇵🇱

Olsztyn, Poland

Ryazan Regional Clinical Hospital

🇷🇺

Ryazan, Russian Federation

FGU Russian Scientific Research Institute of Hematology and Transfusiology

🇷🇺

Saint Petersburg, Russian Federation

Ironwood Cancer and Research Center

🇺🇸

Chandler, Arizona, United States

CHR Metz

🇫🇷

Metz Cedex 03, Alsace, France

Saint Petersburg I.P. Pavlov State Medical University

🇷🇺

Saint-Petersburg, Russian Federation

Froedtert Hospital and Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

BC Cancer Agency - Vancouver Centre

🇨🇦

Vancouver, British Columbia, Canada

Centralny Szpital Kliniczny MSW w Warszawie

🇵🇱

Warszawa, Poland

Instytut Hematologii i Transfuzjologii

🇵🇱

Warszawa, Poland

N. N. Blokhin Russian Cancer Research Center

🇷🇺

Moscow, Russian Federation

Malopolskie Centrum Medyczne S.C.

🇵🇱

Kraków, Poland

Centrum Onkologii i Hipertermii

🇵🇱

Warszawa, Poland

Maidstone Hospital

🇬🇧

Maidstone, England, United Kingdom

Saratov State Medical University

🇷🇺

Saratov, Russian Federation

Changhua Christian Hospital

🇨🇳

Changhua city, Taiwan

Guys and Saint Thomas NHS Foundation Trust

🇬🇧

London, England, United Kingdom

Southampton General Hospital

🇬🇧

Southampton, England, United Kingdom

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

Oxford University Hospitals NHS Trust

🇬🇧

Oxford, England, United Kingdom

Leeds Teaching Hospitals NHS Trust

🇬🇧

Leeds, England, United Kingdom

Barts and The London NHS Trust

🇬🇧

London, England, United Kingdom

University College London Hospitals National Health Society Foundation Trust

🇬🇧

London, England, United Kingdom

Klinikum der Ludwig-Maximilians-Universität München

🇩🇪

München, Germany

Clearview Cancer Institute

🇺🇸

Huntsville, Alabama, United States

Hospital Universitario de Canarias

🇪🇸

San Cristobal de La Laguna, Spain

Prince of Wales Hospital

🇦🇺

Randwick, New South Wales, Australia

Comprehensive Blood and Cancer Center (Bakersfield)

🇺🇸

Bakersfield, California, United States

Cross Cancer Institute

🇨🇦

Edmonton, Alberta, Canada

St Joseph Heritage Healthcare System

🇺🇸

Santa Rosa, California, United States

Central Coast Medical Oncology Group

🇺🇸

Santa Maria, California, United States

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