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A Double-blind Study to Assess 2 Doses of an Investigational Product for 16 Weeks in Participants With Non-alcoholic Fatty Liver Disease and Type 2 Diabetes Mellitus

Phase 2
Completed
Conditions
Non-alcoholic Steatohepatitis
Interventions
Drug: Placebo
Registration Number
NCT03969719
Lead Sponsor
Pfizer
Brief Summary

This is a double-blind, placebo-controlled study in adults with non-alcoholic steatohepatitis and Type 2 Diabetes Mellitis on stable dose of metformin monotherapy. Participants will be treated for 16 weeks with placebo or 1 of 2 doses of investigational product to determine the effect on liver fat, HbA1c, safety, tolerability and pharmacodynamics.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
164
Inclusion Criteria
  • Males, or females of nonchildbearing potential
  • 18 to 70 years of age
  • Type 2 Diabetes Mellitus
  • Liver fat >/=8% by MRI-PDFF
  • On stable dose of metformin monotherapy for at least 2 months (at a dose of at least 500 mg daily)
Exclusion Criteria
  • History of other liver disease
  • Unable to have an MRI performed
  • Significant weight loss in the previous month and/or participant in current weight loss program
  • History of diabetic complications with end-organ damage

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Low DosePF-06835919150 mg
PlaceboPlaceboPalacebo
High DosePF-06835919300 mg
Primary Outcome Measures
NameTimeMethod
Change From Baseline in Hemoglobin A1c (HbA1c) at Week 16Baseline, Week 16.

A sufficient amount of blood was collected for the analysis of plasma HbA1c.

Percent Change From Baseline in Whole Liver Fat at Week 16Baseline, Week 16.

Whole liver fat was measured by Magnetic Resonance Imaging-Proton Density Fat Fraction (MRI-PDFF).

Secondary Outcome Measures
NameTimeMethod
Number of Participants With Hypoglycemia TEAEsUp to 21 weeks.

Hypoglycemic AEs were routinely monitored during participation in the study. Hypoglycemic AE was defined as 1 of the following: 1. Asymptomatic hypoglycemia: an event not accompanied by typical symptoms of hypoglycemic AE but a plasma glucose value of \<70 milligram per deciliter (mg/dL) using glucometer; 2. Documented symptomatic hypoglycemia: an event during which typical symptoms of hypoglycemic AEs were accompanied with a glucose value of \<70 mg/dL using glucometer and the clinical picture included prompt resolution with food intake, subcutaneous glucagon or intravenous (IV) glucose; 3. Probable symptomatic hypoglycemia: an event during which symptoms of hypoglycemic AEs were not accompanied by a plasma glucose determination but was presumably caused by a plasma glucose concentration of \<70 mg/dL, and the clinical picture included prompt resolution with food intake, subcutaneous glucagon, or IV glucose.

Change From Baseline in Fasting Insulin Over 16 WeeksFrom Baseline to Week 2, Week, 4, Week 8, Week 12 and Week 16.

A sufficient amount of blood was collected for the analysis of plasma insulin. The unit of insulin is milli-international units per liter (mIU/L).

Number of Participants With Treatment-Emergent Adverse Events (TEAEs)Up to 21 weeks.

An adverse event (AE) was any untoward medical occurrence in a clinical study participant, temporally associated with the use of study intervention, whether or not considered related to the study intervention. A serious AE was any untoward medical occurrence at any dose that resulted in death; was life-threatening; required hospitalization or prolongation of existing hospitalization; resulted in persistent or significant disability/incapacity; resulted in congenital anomaly/birth defect or that was considered to be an important medical event. An AE was considered TEAE if the event occurred during the on-treatment period. The causality of AEs were assessed by the investigator using clinical judgement. A severe AE was an event that prevents normal everyday activities.

Number of Participants With Electrocardiogram (ECG) Data Meeting Pre-Specified CriteriaUp to 21 weeks.

ECG data meeting the following criteria were reported: PR interval value \>=300 msec, QRS interval percent change \>= 50%, QTcF interval value \>450 msec and \<=480 msec, or change \>30 msec and \<=60 msec, or change \>60 msec.

Change From Baseline in Fasting Glucose Over 16 WeeksFrom Baseline to Week 2, Week, 4, Week 8, Week 12 and Week 16.

A sufficient amount of blood was collected for the analysis of plasma glucose.

Cumulative Number of Participants With Clinical Laboratory AbnormalitiesUp to 21 weeks.

Clinical laboratory tests included hematology (hemoglobin, hematocrit, red blood cell count, mean corpuscular volume, mean cell hemoglobin, mean corpuscular hemoglobin concentration, platelet count, white blood cell count, total neutrophils, eosinophils, monocytes, basophils, lymphocytes); blood chemistry (blood urea nitrogen, creatinine, glucose, calcium, sodium, potassium, chloride, total bicarbonate, aspartate aminotransferase, alanine aminotransferase, gamma glutamyl transferase, total bilirubin, alkaline phosphatase, uric acid, albumin, total protein); urinalysis (pH, glucose, protein, blood, ketones, nitrites, leukocyte esterase, urobilinogen, urine bilirubin, microscopy). The abnormality criteria were standard sponsor reporting criteria.

Number of Participants With Vital Signs Data Meeting Pre-Specified CriteriaUp to 21 weeks.

Vital signs data meeting the following criteria were reported: sitting diastolic blood pressure (DBP) \<50 mmHg or \>= 20 mmHg increase or \>= 20 mmHg decrease, sitting systolic blood pressure (SBP) blood pressure \<90 mmHg or \>=30 mmHg increase or \>=30 mmHg decrease.

Percent Change From Baseline in High-Sensitivity C-Reactive Protein (Hs-CRP) Over 16 WeeksFrom Baseline to Week 2, Week, 4, Week 8, Week 12 and Week 16.

Blood samples were collected to ensure sufficient serum for the analysis of hs-CRP.

Change From Baseline in Fasting Homeostatic Model Assessment of Insulin Resistance (HOMA-IR) Over 16 WeeksFrom Baseline to Week 2, Week, 4, Week 8, Week 12 and Week 16.

HOMA-IR values were derived from fasting plasma insulin and glucose values. Greater reduction from baseline in HOMA-IR scale values shows greater effects on glycemic metabolism.

Percent Change From Baseline in Alanine Aminotransferase (ALT) Over 16 WeeksFrom Baseline to Week 2, Week, 4, Week 8, Week 12 and Week 16.

ALT was assessed as one of the clinical laboratory chemistry tests.

Change From Baseline in HbA1c at All Timepoints Other Than Week 16From Baseline to Week 2, Week, 4, Week 8, and Week 12.

A sufficient amount of blood was collected for the analysis of plasma HbA1c.

Trial Locations

Locations (104)

The Western Centre for Functional and Metabolic Mapping

🇨🇦

London, Ontario, Canada

Hope Clinical Research

🇺🇸

Canoga Park, California, United States

eStudySite

🇺🇸

La Mesa, California, United States

Clinical Trials Research

🇺🇸

Lincoln, California, United States

Sharp Coronado Hospital

🇺🇸

Coronado, California, United States

ICM Medical Group

🇺🇸

Inglewood, California, United States

Southern California Research Center

🇺🇸

Coronado, California, United States

Holy Trinity Medical Clinic

🇺🇸

Harbor City, California, United States

Diagnostic Radiological Imaging Sacramento

🇺🇸

Sacramento, California, United States

Huntington Medical Research Institute

🇺🇸

Pasadena, California, United States

Liberty Pacific Advanced Imaging

🇺🇸

Tarzana, California, United States

Encompass Clinical Research

🇺🇸

Spring Valley, California, United States

Advanced Gastroenterology

🇺🇸

Thousand Oaks, California, United States

Northwell Imaging of Garden City

🇺🇸

Garden City, New York, United States

PMG Research of Wilmington

🇺🇸

Wilmington, North Carolina, United States

Gastroenterology Associates of the Piedmont, PA

🇺🇸

Winston-Salem, North Carolina, United States

PMG Research of Winston Salem

🇺🇸

Winston-Salem, North Carolina, United States

RAS Health

🇺🇸

Marion, Ohio, United States

South Texas Radiology Imaging Centers

🇺🇸

Live Oak, Texas, United States

Northeast Clinical Research of San Antonio, LLC (NECRSA, LLC)

🇺🇸

Schertz, Texas, United States

Clinical Research Partners, LLC

🇺🇸

Richmond, Virginia, United States

Virginia Endoscopy Group

🇺🇸

Richmond, Virginia, United States

VCU Gateway Building Basement

🇺🇸

Richmond, Virginia, United States

Salem VA Medical Center

🇺🇸

Salem, Virginia, United States

Anaheim Clinical Trials LLC-Clinical Research

🇺🇸

Anaheim, California, United States

Anaheim Clinical Trials, LLC

🇺🇸

Anaheim, California, United States

National Research Institute

🇺🇸

Los Angeles, California, United States

Precision Research Institute

🇺🇸

San Diego, California, United States

Sharp and Children's MRI Center, LLC

🇺🇸

San Diego, California, United States

West Coast Radiology

🇺🇸

Santa Ana, California, United States

University Clinical Investigators, Incorporated

🇺🇸

Tustin, California, United States

Panax Clinical Research

🇺🇸

Miami Lakes, Florida, United States

Health Care Family Rehab and Research Center

🇺🇸

Miami, Florida, United States

CTI Clinical Research Center

🇺🇸

Cincinnati, Ohio, United States

Clinical Research of Miami

🇺🇸

Miami, Florida, United States

Finlay Medical Research

🇺🇸

Miami, Florida, United States

Pueblo Imaging

🇺🇸

Las Vegas, Nevada, United States

AA MRC

🇺🇸

Flint, Michigan, United States

Southwest Diagnostics Imaging Center

🇺🇸

Dallas, Texas, United States

ProScan

🇺🇸

Cincinnati, Ohio, United States

Dallas Diabetes and Endocrine Research Center

🇺🇸

Dallas, Texas, United States

PrimeCare Medical Group

🇺🇸

Houston, Texas, United States

Endocrine IPS, PLLC

🇺🇸

Houston, Texas, United States

The Endocrine Center

🇺🇸

Houston, Texas, United States

Texas Center for Drug Development

🇺🇸

Houston, Texas, United States

Clinical Trials of Texas

🇺🇸

San Antonio, Texas, United States

STRIC Northeast Imaging Center

🇺🇸

San Antonio, Texas, United States

Harborview Medical Center Investigational Drug Services

🇺🇸

Seattle, Washington, United States

Harborview Medical Center

🇺🇸

Seattle, Washington, United States

Toronto Liver Centre

🇨🇦

Toronto, Ontario, Canada

East-West Medical Research Institute

🇺🇸

Honolulu, Hawaii, United States

Alliance Multispecialty Research, LLC

🇺🇸

Wichita, Kansas, United States

Innovative Clinical Research, Inc.

🇺🇸

Harbor City, California, United States

Renaissance Imaging Medical Associates

🇺🇸

Northridge, California, United States

Inland Empire Clinical Trials, LLC

🇺🇸

Rialto, California, United States

Sharp & Children's MRI Center, LLC

🇺🇸

San Diego, California, United States

MD Clinical LLC

🇺🇸

Hallandale Beach, Florida, United States

Unique Imaging

🇺🇸

Miami, Florida, United States

Suncoast Research Group, LLC

🇺🇸

Miami, Florida, United States

Qps-Mra, Llc

🇺🇸

South Miami, Florida, United States

Ctmd Research Inc

🇺🇸

Palm Springs, Florida, United States

Physicians Research Associates , LLC

🇺🇸

Lawrenceville, Georgia, United States

Excel Clinical Research

🇺🇸

Las Vegas, Nevada, United States

Northwell Health - Center for Liver Diseases and Transplantation

🇺🇸

Manhasset, New York, United States

Houston Medical Imaging

🇺🇸

Houston, Texas, United States

University of Washington Medical Center

🇺🇸

Seattle, Washington, United States

Nova Scotia Health Authority - Queen Elizabeth II Health Sciences Centre

🇨🇦

Halifax, Nova Scotia, Canada

Centre de Recherche Saint-Louis

🇨🇦

Quebec, Canada

IRM Quebec

🇨🇦

Quebec, Canada

ALPHA Recherche Clinique Lebourgneuf

🇨🇦

Quebec, Canada

Horizon Clinical Research Associates, PLLC

🇺🇸

Gilbert, Arizona, United States

Clinical Research Consortium an AMR company

🇺🇸

Tempe, Arizona, United States

Life Radiology

🇺🇸

Doral, Florida, United States

Borland Groover

🇺🇸

Jacksonville, Florida, United States

Independant Imaging

🇺🇸

Atlantis, Florida, United States

Twin Lakes Imaging

🇺🇸

Daytona Beach, Florida, United States

Multi-Specialty Research Associates, Inc.

🇺🇸

Lake City, Florida, United States

Y & L Advance Health Care, Inc D/B/A Elite Clinical Research

🇺🇸

Miami, Florida, United States

Discovery Clinical Services Ltd.

🇨🇦

Victoria, British Columbia, Canada

Oxford Medical Imaging

🇨🇦

Mississauga, Ontario, Canada

Resonance Magnetique du Saguenay-Lac-Saint-Jean

🇨🇦

Chicoutimi, Quebec, Canada

Ecogene-21

🇨🇦

Chicoutimi, Quebec, Canada

Clinique de Medecine Urbaine du Quartier Latin

🇨🇦

Montreal, Quebec, Canada

McGill University Health Centre (MUHC)

🇨🇦

Montreal, Quebec, Canada

MRI TTT Philips Radiation Oncology

🇨🇦

Montreal, Quebec, Canada

Radiologie Varad

🇨🇦

Montreal, Quebec, Canada

Stand Up MRI of Miami

🇺🇸

Miami, Florida, United States

Vital Imaging Center

🇺🇸

Miami, Florida, United States

Nebraska Medicine

🇺🇸

Omaha, Nebraska, United States

Vital Imaging

🇺🇸

Miami, Florida, United States

International Research Associates

🇺🇸

Miami, Florida, United States

West Coast Medical Imaging

🇨🇦

Victoria, British Columbia, Canada

Aggarwal and Associates Limited

🇨🇦

Brampton, Ontario, Canada

St. Michael's Hospital

🇨🇦

Toronto, Ontario, Canada

Advanced Gastroenterology Associates, LLC

🇺🇸

Palm Harbor, Florida, United States

Rose Radiology

🇺🇸

Palm Harbor, Florida, United States

Progressive Medical Research

🇺🇸

Port Orange, Florida, United States

Alliance for Multispecialty, LLC

🇺🇸

Las Vegas, Nevada, United States

Desert Radiology

🇺🇸

Las Vegas, Nevada, United States

Nova Scotia Health Authority QE II Health Sciences Centre

🇨🇦

Halifax, Nova Scotia, Canada

Castillo & Torres MD PA

🇺🇸

Palm Springs, Florida, United States

Bluewater Clinical Research Group, Inc.

🇨🇦

Sarnia, Ontario, Canada

University of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

San Diego Imaging SDI

🇺🇸

Chula Vista, California, United States

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