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Evaluation of Repeat Administration of Purified Poloxamer 188

Phase 3
Completed
Conditions
Sickle Cell Disease
Interventions
Registration Number
NCT02449616
Lead Sponsor
Mast Therapeutics, Inc.
Brief Summary

The purpose of this study is to evaluate the safety of repeat administration of MST-188 during vaso-occlusive crisis of sickle cell disease. Additionally, this study will evaluate the development of acute chest syndrome during VOC and re-hospitalization for recurrence of VOC.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
16
Inclusion Criteria
  • Completed participation in study MST-188-01 (EPIC study)
  • Subject age 4 through 65 years
  • Subject is experiencing acute pain typical of VOC and requires treatment with parenteral opioid analgesia
  • Subject requires hospitalization
Exclusion Criteria
  • Subject has acute chest syndrome
  • Subject's laboratory results indicate inadequate organ function
  • Subject is pregnant or nursing an infant
  • Subject had a painful crisis requiring hospitalization within the preceding 14 days
  • Subject has been transfused within the past 14 days
  • Subject has complications related to SCD

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Study DrugMST-188MST-188
Primary Outcome Measures
NameTimeMethod
Safety as measured as the incidence of adverse events30 days after administration of study drug
Secondary Outcome Measures
NameTimeMethod
Rate of re-hospitalization for recurrence of VOCWithin 14 days of the date of discharge
Occurrence of acute chest syndromeWithin 120 hours of registration

Trial Locations

Locations (9)

T. C. Thompson Children's Hospital

🇺🇸

Chattanooga, Tennessee, United States

Rady Children's Hospital

🇺🇸

San Diego, California, United States

Joe Dimaggio Children's Hospital

🇺🇸

Hollywood, Florida, United States

Rutgers University

🇺🇸

New Brunswick, New Jersey, United States

Ann and Robert H. Lurie Children's Hospital of Chicago

🇺🇸

Chicago, Illinois, United States

University of Iowa Children's Hospital

🇺🇸

Iowa City, Iowa, United States

Children's Hospital of Southwest Florida

🇺🇸

Fort Myers, Florida, United States

Our Lady of the Lake Children's Hospital

🇺🇸

Baton Rouge, Louisiana, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

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