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Yield of Diagnostic Tests and Effects of Crofelemer for Chronic Idiopathic Diarrhea in Non-HIV Patients

Phase 4
Completed
Conditions
Chronic Diarrhea of Unknown Origin
Interventions
Diagnostic Test: Diagnostic tests for cause of chronic diarrhea
Registration Number
NCT03898856
Lead Sponsor
The University of Texas Health Science Center, Houston
Brief Summary

The purpose of this study is to evaluate the effectiveness of the drug Crofelemer in the treatment of non-HIV patients with chronic idiopathic diarrhea; to determine the prevalence of identifiable causes of chronic diarrhea in a non-HIV patients; to assess the diagnostic yield, in terms of identification of treatable etiologies, of commercially available diagnostic evaluations in adult, non-HIV patients with chronic idiopathic diarrhea, that is, evaluate which tests, among the standard diagnostic tests commonly conducted as part of the evaluation of chronic idiopathic diarrhea, are most likely to identify a treatable cause of the diarrhea; and to analyze the relationship between chronic idiopathic diarrhea and health-related quality of life and assess the impact of crofelemer treatment on health-related quality of life.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
93
Inclusion Criteria
  • Patients with chronic diarrhea (defined as 3 non-bloody loose stools per day or more than 20 non-bloody loose stools per week for more ≥ 4 weeks) and Bristol Stool Form Scale for stool consistency of 6/7 with >50% stool without an obvious cause after evaluation for organic etiologies.
  • Patients from any ethnicity
Exclusion Criteria
  • Hematochezia (potentially related to an organic cause).
  • Subjects less than 18 years of age more than 75 years of age (safety and effectiveness of crofelemer has not been established in these age groups).
  • Pregnant females (crofelemer is a Category C drug due to lack of well-controlled studies to study its effects in this population).
  • Lactating females (it is unknown if crofelemer is excreted in the human milk and thus may have unknown adverse effects on the nursing infants).
  • HIV positive individuals.
  • Persons within ability to provide consent and understand the study
  • Persons with history of alcohol abuse or binge drinking.
  • Persons with history of surgical bowel resection or bariatric surgery in the past 12 months.
  • Persons who have undergone cholecystectomy (open or laparoscopic) in the past 3 months.
  • Persons receiving antibiotics currently or have received antimicrobials in the past 4 weeks.
  • Persons with end-organ failures including end-stage renal disease, end-stage liver disease, or severe heart failure.
  • Persons with metastatic hematologic and oncologic malignancies.
  • Persons receiving chemo-radiation or immune-modulators for oncologic or rheumatologic conditions.
  • Persons with any other known organic gastrointestinal or non-gastrointestinal disease process in which diarrhea is a recognized clinical feature.
  • Gluten free diet for previous 3 months and refusal to ingest gluten.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Crofelemer and Diagnostic tests for cause of chronic diarrheaCrofelemer125 mg tablets taken by mouth twice daily for 28 days
Crofelemer and Diagnostic tests for cause of chronic diarrheaDiagnostic tests for cause of chronic diarrhea125 mg tablets taken by mouth twice daily for 28 days
Primary Outcome Measures
NameTimeMethod
Number of participants with a 50 percent decrease in mean stool count per weekWeek 4
Secondary Outcome Measures
NameTimeMethod
Change in participant diary descriptors as measured by number of anti-diarrheal medication taken per 24-hr periodBaseline,week 4 of treatment
Change in participant diary descriptor of daily time of administration of crofelemerBaseline,week 4 of treatment

Time

Change in participant diary descriptors as measured by the presence of urgency with each bowel movementBaseline,week 4 of treatment

0-4 visual analog scale (0=none; 4=incontinence)

Change in participant diary descriptors as measured by supportive anti-diarrheal medication takenBaseline,week 4 of treatment

Yes or no

Change in participant diary descriptors as measured by dose of supportive anti-diarrheal medication takenBaseline,week 4 of treatment
Number of participants with an improvement in stool consistency by more than 2 levels as measured by the Bristol stool form scaleweek 4

The Bristol stool form scale is a validated 1-7 scale that correlates to stool form. Type 1 is pebble like stool, type 2 lumpy and hard, type 3 like a sausage with cracks on the surface type 4 like a sausage but smooth and soft, type 5 soft blobs with clear cut edges, type 6 fluffy pieces with ragged edges, mushy stool, type 7watery, no solid pieces Types 5-7 are consistent with diarrhea and for this study a movement to lower types is considered an improvement

Change in physical, psychological, and social functioning as measured by the Health-related quality of life (HRQOL) questionnaireBaseline,week 4 of treatment

The Medical Outcomes Trust short form questionnaire with 36 questions, most often referred to as SF-36, is a measure of general health status relevant across age, disease and treatment groups, widely used and tested in a range of conditions and settings. The items in SF-36 are divided into eight different domains with overall physical and mental health component summary scores. Domains are physical functioning, role limitations physical, bodily pain, social functioning, general mental health, role limitations emotional, vitality and general health. The SF-36 consists of eight scaled scores, which are the weighted sums of the questions in their section. Each scale is directly transformed into a 0-100 scale on the assumption that each question carries equal weight. The lower the score the more disability. The higher the score the less disability i.e., a score of zero is equivalent to maximum disability and a score of 100 is equivalent to no disability.

Number of participants with any abnormal diagnostic test results leading to the identification of the cause of chronic diarrheaBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-EsophagogastroduodenoscopyBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-ColonoscopyBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Biopsy of duodenumBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Biopsy of ColonBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Prometheus IBcause Chronic Diarrhea panelBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Thyroid Function TestsBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Stool osmolalityBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Stool Ova and ParasitesBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Stool CultureBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Stool Qualitative Stool FatBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Stool Reducing SubstancesBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Laxative ScreeningBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Lactulose Hydrogen Breath TestBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-Gastrin LevelBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-. Calcitonin LevelBaseline
Number of participants with abnormal diagnostic test results leading to the identification of the cause of chronic diarrhea-VIP LevelBaseline
Change in participant diary descriptors as measured by time of bowel movements per 24 hr periodBaseline,week 4 of treatment
Change in participant diary descriptors as measured by number of loose stools per 24 hr periodBaseline,week 4 of treatment
Change in participant diary descriptors as measured by consistency of each bowel movement as per the Bristol Stool Form ScaleBaseline,week 4 of treatment

The Bristol stool form scale is a validated 1-7 scale that correlates to stool form. Type 1 is pebble like stool, type 2 lumpy and hard, type 3 like a sausage with cracks on the surface type 4 like a sausage but smooth and soft, type 5 soft blobs with clear cut edges, type 6 fluffy pieces with ragged edges, mushy stool, type 7watery, no solid pieces Types 5-7 are consistent with diarrhea and for this study a movement to lower types is considered an improvement

Change in participant diary descriptor of any new symptomsBaseline,week 4 of treatment

Trial Locations

Locations (1)

The University of Texas Health Science Center at Houston

🇺🇸

Houston, Texas, United States

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