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Radiotherapy of Multiple Brain Metastases Using AGuIX®

Phase 2
Active, not recruiting
Conditions
Brain Metastases, Adult
Radiotherapy
Interventions
Radiation: Whole Brain Radiation Therapy
Registration Number
NCT03818386
Lead Sponsor
University Hospital, Grenoble
Brief Summary

This is a Prospective Randomized Open Blinded Endpoint phase II clinical trial. The study will be adaptive: an interim analysis is planned after enrolment of 20 patients in each arm of treatment (WBRT and AGuIX® + WBRT), to select and continue the study with group(s) that present the best response rate to the experimental treatment (AGuIX® + WBRT).

The main endpoint will be evaluated by a blinded endpoint committee.

Detailed Description

The occurrence of brain metastases is a common event in the history of cancer and negatively affects the life expectancy of patients. Their incidence varies between 15 and 50% according to the histologic types. Surgery, stereotactic radiosurgery, radiotherapy and chemotherapy are the main treatments currently proposed.

For patients with multiple brain metastases, whole brain radiation therapy (WBRT) remains the standard of care. However, the median overall survival is less than 6 months and new approaches need to be developed to improve treatment of these patients.

In this context, the weak control of the disease comes from three main factors: the multiplicity of the brain lesions, the radioresistance of certain histologies and the poor distribution of cytotoxic agents in brain metastases.

The use of radiosensitizing agents is here of great interest. The radiosensitizing agent chosen in this study is AGuIX®. It is a Gadolinium-chelated polysiloxane based nanoparticle developed by NH TherAguix company for its theranostic properties (radiosensitization and diagnosis by multimodal imaging). Preclinical studies have demonstrated the radiosensitizing effect of AGuIX® in vivo in 8 tumor models xenografted in rodents, and particularly in brain tumors.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
100
Inclusion Criteria
  • Patients with brain metastases, from a histologically confirmed solid tumor, eligible for WBRT

  • At least 18 years old

  • Signed informed consent after informing the patient

  • ECOG (Eastern Cooperative Oncology Group) performance status 0-2

  • Extracranial disease:

    • Complete or partial response or stability under systemic treatment
    • No extracranial disease
    • Or first line of treatment
  • Life expectancy greater than 6 weeks

  • Effective contraceptive method for all patient of childbearing potential

  • Affiliated to a social security regimen

Exclusion Criteria
  • Leptomeningeal metastasis
  • Evidence of metastasis with recent large hemorrhage
  • Progressive and threatening extracranial disease under systemic treatment
  • Previous cranial irradiation (except stereotactic irradiation)
  • Known contra-indication, sensitivity or allergy to gadolinium
  • Known contra-indication for Magnetic Resonance Imaging
  • Renal insufficiency (glomerular filtration rate ≤ 50 mL/min/1.73m²)
  • Pregnancy or breastfeeding
  • Subject under administrative or judicial control

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
AGuIX® + Whole Brain Radiation TherapyAGuIX®Intervention: Drug: AGuIX® + WBRT Other Names: Gadolinium-chelated polysiloxane based nanoparticles 3 intravenous injections at 100mg/kg * D0: AGuIX® injection followed by MRI (within 7 days before commencement of WBRT) * Fr1: AGuIX® injection before the first radiation session * Fr6: AGuIX® injection before the sixth radiation session 30 Gy in 10 fractions of 3 Gy over 2-3 weeks
Whole Brain Radiation TherapyWhole Brain Radiation TherapyIntervention: Radiation: Whole Brain Radiation Therapy ( WBRT) 30 Gy in 10 fractions of 3 Gy over 2-3 weeks
AGuIX® + Whole Brain Radiation TherapyWhole Brain Radiation TherapyIntervention: Drug: AGuIX® + WBRT Other Names: Gadolinium-chelated polysiloxane based nanoparticles 3 intravenous injections at 100mg/kg * D0: AGuIX® injection followed by MRI (within 7 days before commencement of WBRT) * Fr1: AGuIX® injection before the first radiation session * Fr6: AGuIX® injection before the sixth radiation session 30 Gy in 10 fractions of 3 Gy over 2-3 weeks
Primary Outcome Measures
NameTimeMethod
Best objective intracranial response rate - intent-to-treatat 3 months

Evaluation of brain metastases response, according to RECIST v1.1 criteria (or modified RECIST) by MRI, with MRI centralized reading

Secondary Outcome Measures
NameTimeMethod
Evaluation of the quality of lifeat day 0, 6 weeks, 3, 6, 9, 12 months

Quality of life test score EORTC QLQ BN20

Incidence of adverse eventsat 6 weeks and 3, 6, 9 and 12 months

Reporting of adverse events by type, frequency and severity for both treatments (WBRT and AGuIX® + WBRT)

MRI study of the distribution of the product in brain metastasesDay 0

MRI evaluation of contrast enhancement at D0 after AGuIX® injection

Best objective intracranial response rate - per-protocolat 6 weeks and 3 months

Evaluation of brain metastases response on per-protocol population, according to RECIST v1.1 criteria (or modified RECIST), by MRI with centralized reading

Evaluation of the intracranial response ratefor 12 months

Evaluation of brain metastases response, according to RANO, to RECIST v1.1 criteria, and as the evolution of the sum of longest diameters (for all metastases with a sum of diameters \> 1cm), by MRI, at 6 weeks and 3, 6, 9 and 12 months

Overall survivalat 12 months

Death

Change in steroid dependenceat 6 weeks and 3, 6, 9 and 12 months

Reporting of daily steroid dose

Neurocognitive evaluationat Day 0, 6 weeks, 3, 6, 9, 12 months

Neurocognitive test (MoCA)

Intracranial progression-free survivalat 12 months

Evaluation of the time between the start of the treatment and the occurence of intracranial progression or neuriologic death

Evaluation of individual metastasis responseat 6 weeks and 3, 6, 9 and 12 months

Evaluation of individual brain metastasis response, for all metastases with the sum of diameters \> 1cm, by MRI rate

Intracranial progression-free survival, brain survivalat 12 months

Death related to brain metastases progression

Trial Locations

Locations (14)

Centre Hospitalier Annecy Genevois

🇫🇷

Annecy, Rhones-Alpes, France

Centre Leon Berard Lyon

🇫🇷

Lyon, Rhones Alpes, France

Centre Hospitalier Universitaire Grenoble-Alpes

🇫🇷

Grenoble, Rhones-Alpes, France

CRLCC - Institut Bergonié

🇫🇷

Bordeaux, France

Crlcc Francois Baclesse

🇫🇷

Caen, France

Centre Georges François Leclerc

🇫🇷

Dijon, France

Hôpital Européen Georges Pompidou

🇫🇷

Paris, France

La Pitié Salpêtrière - Charles Foix

🇫🇷

Paris, France

Institut Curie Saint Cloud

🇫🇷

Saint-Cloud, France

Crlcc Paul Strauss

🇫🇷

Strasbourg, France

Institut de Cancérologie de Lorraine ALEXIS VAUTRIN

🇫🇷

Vandœuvre-lès-Nancy, France

Institut Régional du Cancer

🇫🇷

Montpellier, Occitanie, France

Institut Claudius Regaud Institut Universitaire du Cancer Toulouse Oncopole Radiothérapie

🇫🇷

Toulouse, Occitanie, France

Hospices Civils de Lyon-Hôpital Lyon Sud

🇫🇷

Lyon, France

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