MedPath

Study to Evaluate Safety and Antiviral Activity of Doses of JNJ-53718678 in Children (>=28 Days to <=3 Years) With Respiratory Syncytial Virus Infection

Phase 2
Terminated
Conditions
Respiratory Syncytial Virus Infections
Interventions
Drug: JNJ-53718678
Drug: Placebo
Registration Number
NCT03656510
Lead Sponsor
Janssen Research & Development, LLC
Brief Summary

The purpose of this study is to evaluate the antiviral activity, clinical outcomes, safety, tolerability, and pharmacokinetic/pharmacodynamic relationships of different oral dose levels of JNJ-53718678 in children greater than or equal to 28 days and less than or equal to 3 years of age with respiratory syncytial virus (RSV) disease (hospitalized participants \[Cohort 1\] or outpatients \[Cohort 2\]).

Detailed Description

JNJ-53718678 is an investigational respiratory syncytial virus (RSV) specific fusion inhibitor and is under development for the treatment of RSV infection, which results in an upper and/or lower respiratory tract illness. The primary hypothesis of this study is that JNJ-53718678 has antiviral activity against RSV (that is, results in a decrease in RSV nasal viral load from immediately prior to first dose of study drug until Day 5). This will be assessed by a positive dose-response relationship of JNJ-53718678 compared to placebo. Besides the RSV nasal viral load through day 5, other timepoints will also be evaluated as well as other nasal viral load related parameters. In addition, the evolution of signs and symptoms of RSV disease will be evaluated. Participants' safety will be monitored throughout the study by evaluating the occurrence and severity of adverse events and by laboratory and electrocardiogram measurements. Study participants will be identified when they are hospitalized or expected to be hospitalized within 24 hours after presentation to the hospital (Cohort 1) or present for medical care as outpatients (Cohort 2) with symptoms of an acute respiratory illness supporting a diagnosis of RSV infection. Eligible participants will be randomized 1:1:1 to receive either a low or a high dose of JNJ 53718678 or placebo and will be receiving study treatment for 7 days. They will be followed up for 3 weeks after the last dose. The total study duration for each participant will be approximately 29 days.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
246
Inclusion Criteria
  • Informed consent form (ICF) must be given
  • Laboratory diagnosis of respiratory syncytial virus (RSV) infection
  • The participant has an acute respiratory illness
  • The time of onset of RSV symptoms to the anticipated time of randomization must be less than or equal to (<=) 5 days
  • Except for the RSV-related illness, the Participant must be medically stable in case of allowed co-morbid conditions
  • The participant must have been assessed per local public health practice and considered not to have Severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2) infection during this respiratory infection
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Exclusion Criteria
  • The participant is less than (<) 3 months postnatal age at screening and was born prematurely (i.e, <37 weeks and 0 days of gestation) OR if the participant weighs <2.4 kilogram (kg) or greater than (>) 16.8 kg
  • Participant is considered by the investigator to be immunocompromised within the past 12 months
  • Participant unwilling or unable to undergo mid-turbinate nasal swab procedures
  • Participant is receiving chronic home oxygen therapy at screening
  • Participant has other clinically significant abnormal electrocardiogram (ECG) findings not consistent with the present risk factor for severe RSV disease (if applicable) in the study population, as judged by the investigator based on the machine read ECG results at screening
  • The participant has a QTcF interval greater than (>)450 millisecond (ms) per the machine read (mean of triplicate) parameter result confirmed by repeat triplicate ECG recording during screening
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Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Low Dose: JNJ-53718678JNJ-53718678Participants will be randomized to receive JNJ-53718678 0.85 mg/kg (Age Group 1: \>=28 days and \<3 months of age), 1 mg/kg (Age Group 2: \>=3 months and \<6 months of age) and 1.5 mg/kg (Age Group 3: \>=6 months and 3 years of age) orally twice daily for 7 days.
High Dose: JNJ-53718678JNJ-53718678Participants will be randomized to receive JNJ-53718678 2.5 milligram per kilogram (mg/kg) (Age Group 1: greater than or equal to \[\>=\] 28 days and less than \[\<\] 3 months of age), 3 mg/kg (Age Group 2: \>=3 months and \<6 months of age) and 4.5 mg/kg (Age Group 3: \>=6 months and less than or equal to \[\<=3\] years of age) orally twice daily for 7 days.
PlaceboPlaceboParticipants will be randomized to receive matching placebo (i.e. high volume placebo or low volume placebo to match the calculated volume of the JNJ-53718678 for the high dose or low dose) orally twice daily for 7 days.
Primary Outcome Measures
NameTimeMethod
Respiratory Syncytial Virus (RSV) Viral Load Area Under Curve (AUC) From Immediately Prior to First Dose of Study Drug (Baseline) Through Day 5 (AUC[Day 5])Baseline through Day 5

RSV viral load AUC from immediately prior to first dose of study drug through Day 5 was determined. The RSV viral load was measured by quantitative reverse transcription polymerase chain reaction (qRT-PCR) assay in mid-turbinate nasal swab specimens. As planned, combined data for both the cohorts was collected, analyzed and reported for this outcome measure.

Secondary Outcome Measures
NameTimeMethod
RSV Viral Load Over TimeBaseline, Days 3, 5, 8, 14, and 21

RSV viral load actual values over time were measured by qRT-PCR in the nasal swab specimens collected at the clinic visits and at home. As planned, combined data for both the cohorts was collected, analyzed and reported for this outcome measure.

Change From Baseline in RSV Viral Load Over TimeBaseline up to Days 3, 5, 8, 14, and 21

Change from baseline in RSV viral load over time was measured by qRT-PCR in the nasal swab specimens collected at the clinic visits and at home. As planned, combined data for both the cohorts was collected, analyzed and reported for this outcome measure.

Least Squares (LS) Mean RSV Viral Load on Days 3, 8 and 14Baseline through Days 3, 8, and 14

LS mean RSV viral load on Days 3, 8, and 14 was reported. LS mean viral load (log10 copies/mL) was estimated per time point. The difference in RSV viral Load AUC (log10 copies\*day/mL) from immediately prior to first dose of study drug (baseline) through Day 3, 8 and 14 was determined from the model estimating the LS Mean Viral Load per time point, and is presented in the statistical analysis. The RSV viral load was measured by qRT-PCR assay in mid-turbinate nasal swab specimens. As planned, combined data for both the cohorts was collected, and analyzed for this outcome measure at Days 3 and 8, however combined Cohort 1 and Cohort 2 data were not analyzed for this outcome measure at Day 14, due to the premature study termination.

Time to Undetectable RSV Viral LoadUp to Day 21

Time to undetectable RSV viral load (as measured by qRT-PCR) was defined as the time in hours from first dose of study drug to first post-baseline timepoint at which the virus was undetectable and after which there were no more detectable virus assessments. As planned, combined data for both the cohorts was collected, analyzed and reported for this outcome measure.

Percentage of Participants With Undetectable RSV Viral Load at Each Timepoint Throughout the StudyBaseline, Days 3, 5, 8, 14 and 21

Percentage of participants with undetectable RSV viral load (as measured by qRT-PCR) at each timepoint throughout the study was reported. As planned, combined data for both the cohorts were collected, analyzed and reported for this outcome measure.

Change From Baseline in Parent(s)/Caregiver(s) Pediatric RSV Electronic Severity and Outcomes Rating System (PRESORS) ScoresBaseline up to Days 3, 5, 8, 14 and 21

PRESORS is a questionnaire recording presence and severity of signs and symptoms of RSV disease (fever, cough, sputum, wheezing, difficulty breathing, nasal congestion, and feeding issues). PRESORS overall RSV symptoms summary parameter consisted of 12-items, each item score ranges from 0 to 3. A summary score was derived (mean of the item scores) which also ranges from 0 to 3. The higher the score, the worse the symptom.

Change From Baseline in Clinician PRESORS ScoreBaseline, up to Days 3, 5, 8, 14 and 21

Change from baseline in clinician PRESORS scores (for concepts: activity level, sleep disturbance, breathing problems, retractions, tachypnea, feeding problem, cough, nasal secretions, wheezing, dehydration) was assessed. Clinician PRESORS is a questionnaire recording presence and severity of signs and symptoms of RSV disease and consisted of 10-items, each item score ranges from 0 to 3. Overall RSV symptoms summary parameter was derived (mean of the item scores) which also ranges from 0 to 3. The higher the score, the worse the symptom.

Time to Resolution of RSV Symptoms Based on PRESORS Caregiver (ObsRO)Up to Day 21

Time to resolution is defined as time from first dose of study drug until the first time of resolution of all RSV symptoms (breathing problems, retractions, tachypnea, breathing sounds, cough, tachycardia, nasal secretions, sleep disturbance, crying, illness behavior, feeding problems, and dehydration). Resolution occurs when all symptoms from the caregiver reported outcomes (ObsRO) are scored as none or mild (score of 0 or 1, respectively) for at least 24 hours.

Time to Improvement on Overall HealthUp to Day 21

Time to improvement based on general questions on overall health was assessed. Time from first dose of study drug until first time status of improvement of RSV symptoms reported as "very much improved" or "much improved" based on response to question 'Would you say the child's RSV symptoms have improved, are about the same or are worse than when the child entered the study'.

Percentage of Participants by Status of RSV Symptoms Based on PRESORS Caregiver (ObsRO) General Question Over TimeBaseline, Days 3, 5, 8, 14, and 21

Percentage of participants by status of RSV symptoms based on PRESORS caregiver (ObsRO) general question over time was assessed. PRESORS is a questionnaire recording presence and severity of signs and symptoms of RSV disease (fever, cough, sputum, wheezing, difficulty breathing, nasal congestion, and feeding issues). Status of RSV symptoms was assessed by a question (how would you rate the child's RSV symptoms now?) of PRESORS questionnaire and responses were categorized as: 1) none, 2) very mild, 3) mild, 4) moderate, 5) severe, and 6) very severe.

Percentage of Participants by Health Status Assessment Based on PRESORS Caregiver (ObsRO) General Question Over TimeBaseline, Days 3, 5, 8, 14, and 21

Percentage of participants by health status assessment based on PRESORS caregiver (ObsRO) general question over time was assessed. PRESORS is a questionnaire recording presence and severity of signs and symptoms of RSV disease (fever, cough, sputum, wheezing, difficulty breathing, nasal congestion, and feeding issues). Health status was assessed by a question (how is the child's health now) of PRESORS questionnaire and responses were categorized as: 1) excellent, 2) very good, 3) good, 4) fair, 5) poor, and 6) very poor.

Percentage of Participants With Worsening or Improvement Status of RSV DiseaseDays 14 and 21

Percentage of participants with worsening or improvement of RSV disease based on general questions of overall health was assessed. Improvement or worsening was assessed by a question 'Would you say the child's RSV symptoms have improved, are about the same or are worse than when the child entered the study' and responses were categorized as: 1) very much improved, 2) much improved, 3) a little improved, 4) about the same, 5) a little worse, 6) much worse, and 7) very much worse".

Percentage of Participants by Return to Pre-RSV Disease Health Status Assessment Based on PRESORS Caregiver (ObsRO) General Question Over TimeBaseline, Days 3, 5, 8, 14, and 21

Percentage of participants by return to pre-RSV disease health status assessment based on PRESORS caregiver (ObsRO) general question over time was assessed by a question (Has the child's health returned to normal \[how it was before RSV?\]) of PRESORS questionnaire and responses were categorized as: 1) No, and 2) Yes. PRESORS is a questionnaire recording presence and severity of signs and symptoms of RSV disease (fever, cough, sputum, wheezing, difficulty breathing, nasal congestion, and feeding issues). Below results are reported for category 'Yes'.

Change From Baseline in Heart RateBaseline to Days 3, 5, 8, 14 and 21

Change from baseline in heart rate was assessed.

Respiratory Rate (RR) Over TimeBaseline, Days 3, 5, 8, 14 and 21

Respiratory rate (RR) was measured by the investigator over time.

Change From Baseline in Respiratory RateBaseline to Days 3, 5, 8, 14 and 21

Change from baseline in respiratory rate was derived based on the reported measurements of respiratory rate over time. The respiratory rate over time was reported by the investigator.

Heart Rate Over TimeBaseline, Days 3, 5, 8, 14 and 21

Heart rate was measured by the investigator over time.

Peripheral Capillary Oxygen Saturation (SpO2) Over TimeBaseline, Days 3, 5, 8, 14 and 21

Peripheral capillary oxygen saturation was measured by the investigator over time.

Percentage of Participants Who Required (re)Hospitalization During Treatment and Follow-upUp to Day 28

Percentage of participants who required (re)hospitalization during treatment and follow-up was assessed. Percentage of participants requiring re-hospitalization following the initial hospital discharge was assessed in Cohort 1 participants (hospitalized cohort) whilst percentage of participants requiring hospitalization after first dose of study drug was assessed in Cohort 2 participants (outpatient cohort).

Cohort 1: Time to Return to Age-adjusted Normal Values for Vital SignsUp to Day 28

Time to return to age-adjusted normal values from first dose of study drug based on the reported vital signs (respiratory rate, heart rate, SpO2 \>=92%, and SpO2 \>=95%) values was assessed. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Cohort 1: Time to Clinical Stability Evaluated by the InvestigatorUp to Day 21

Time to clinical stability was derived based on vital signs(SpO2 \>= 92%, SpO2 \>=95% on room air) assessments and supplementation end dates as collected. Time to clinical stability=time from initiation of study treatment until time at which following criteria were met: Time to return to age-adjusted normal value for otherwise healthy, pre-RSV infection status for participant with risk factor for severe RSV disease,no more oxygen supplementation in otherwise healthy participant, participant with risk factor for severe RSV disease and no more IV administered/nasogastric tube feeding/hydration supplementation in otherwise healthy participant or pre-RSV status of IV/nasogastric tube feeding/hydration in participant with risk factor for severe RSV disease. As per protocol and study design,this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Body Temperature Over TimeBaseline, Days 3, 5, 8, 14 and 21

Body temperature was reported over time (either investigator or caregiver measured).

Change From Baseline in Body TemperatureBaseline to Days 3, 5, 8, 14 and 21

Change from baseline in body temperature (either investigator or caregiver measured) was assessed.

Change From Baseline in Peripheral Capillary Oxygen Saturation (SpO2)Baseline to Days 3, 5, 8, 14, and 21

Change from baseline in peripheral capillary oxygen saturation levels was derived based on reported values over time.

Cohort 1: Time to Discharge From HospitalUp to Day 28

Time to discharge from hospital was derived from the reported discharge date/time and from first dose date/time. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Cohort 1: Percentage of Participants Who Required Admission to the Intensive Care Unit (ICU)Up to Day 21

Percentage of participants who required admission to the ICU was assessed. This outcome measure was applicable for those participants that were not in ICU before first dose of study drug. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Cohort 1: Duration of ICU StayUp to Day 21

Duration of ICU stay was derived based on the reported admission/discharge date/time for ICU. Duration defined as total number of hours a participant was in ICU from first dose of study drug until study termination. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Cohort 1: Percentage of Participants Who Required Supplemental OxygenUp to Day 21

Percentage of participants who required supplemental oxygen after first dose of study drug was reported. This parameter was only for participants that did not require oxygen supplementation before first dose of study drug. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Cohort 1: Duration of Supplemental OxygenUp to Day 28

Duration of supplemental oxygen was assessed. Duration was defined as total number of hours a participant used supplemental oxygen from first dose of study drug until study termination. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Cohort 1: Percentage of Participants Who Required Non-invasive Mechanical Ventilation SupportUp to Day 21

Percentage of participants who required non-invasive mechanical ventilation support (example: continuous positive airway pressure) after first dose of study drug was assessed. This parameter was only for participants who did not require non-invasive mechanical ventilation support before first dose of study drug. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Cohort 1: Percentage of Participants Who Required Invasive Mechanical Ventilation SupportUp to Day 21

Percentage of participants who required invasive mechanical ventilation support (example: endotracheal-mechanical ventilation) after first dose of study drug was assessed. This parameter was only for participants who did not require invasive mechanical ventilation support before first dose of study drug. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Cohort 1: Percentage of Participants Who Required Non-invasive Non-mechanical Ventilation SupportUp to Day 21

Percentage of participants who required non-invasive non-mechanical ventilation support (example: nasal cannula) after first dose of study drug was assessed. This parameter was only for participants who did not require non-invasive non-mechanical ventilation support before first dose of study drug. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Cohort 1: Time to End of Supplemental Oxygen up to 72 Hours From First Hospital DischargeUp to end of supplemental oxygen including supplemental oxygen within 72 hours after first hospital discharge (up to Day 28)

Time to end of supplemental oxygen up to 72 hours from first hospital discharge was assessed. Time to end of supplemental oxygen was defined as time (hours) from first dose of study drug to last end date/time of any oxygen supplementation received, but within 72 hours following first hospital discharge. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Percentage of Participants With Categorized Change From Baseline in ECG Parameters (QT, QTcB, QTcF)Baseline to Day 28

Percentage of participants with categorized change from Baseline in ECG parameters (QT/ QTcB/ QTcF interval) was assessed. Abnormal ECG change from baseline in QTc and QTcB Interval is categorized as borderline QTc change: 30 ms (milliseconds) to \<60 ms, and abnormally high QTc change: greater than \[\>\] 60 ms), and QTcF Interval is categorized as borderline QTc change: 30 ms to \<60 ms, and abnormally high QTc change: \>60 ms.

Cohort 1: Area Under the Plasma Concentration-Time Curve From Timepoint 0 Hours Until 24 Hours Post Dose (AUC[0-24 Hours])0 to 24 hours post dose on Days 1 and 7

AUC (0-24) is defined as area under the plasma concentration-time curve from timepoint 0 hours until 24 hours post dose estimated by population PK model.

Cohort 1: Maximum Plasma Concentration (Cmax) of JNJ-53718678Days 1 and 7

Cmax is the maximum plasma concentration of JNJ-53718678 estimated by population PK model.

Cohort 1: Trough Plasma Concentration (Ctrough) of JNJ-53718678Days 1 and 7

Ctrough is the trough plasma concentration of JNJ-53718678 estimated by population PK model.

Cohort 2: Plasma Concentration of JNJ-53718678Once daily dosing: Day 3 and Day 8 pre- or post-dose. Twice daily dosing: Day 1 at least 1 hour post-dose, and Days 3 or 5 (combined in one timepoint) at least 4 hours after morning dose but prior to evening dose

Plasma concentration of JNJ-53718678 was measured for Cohort-2. As per planned analysis in the protocol, PK sampling was performed on either Day 3 or Day 5 for participants receiving twice daily dosing, resulting in one combined timepoint of Day 3 or Day 5. Hence, the data collected on either Day 3 or Day 5 was pooled and is reported here collectively.

Number of Participants With Emerging Variations in the Viral Genome Potentially Associated With Resistance to JNJ-53718678Up to Day 21

Number of participants with emerging variations in the viral genome potentially associated with resistance to JNJ-53718678 was reported. Number of participants with F gene sequencing data available and with emerging genetic variations post-baseline as compared to baseline, considering 24 RSV F protein positions of interest (positions 127, 137, 138, 140, 141, 143, 144, 323, 338, 339, 392, 394, 396, 397, 398, 399, 400, 401, 474, 486, 487, 488, 489, and 517) was reported.

Cohort 1: Duration of Non-invasive Ventilation SupportUp to Day 21

For the subset of participants who received non-invasive ventilation post dose, duration for non-invasive ventilation could not be derived by individual type as start/end dates and times were not collected in full to allow breakdown of duration derivation by ventilation type and only overall duration of oxygen supplementation (overall ventilation support) could be derived which is reported in the outcome measure "Duration of Supplemental Oxygen". As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure could only have been reported for Cohort 1.

Percentage of Participants With Vital Signs AbnormalitiesUp to Day 28

Percentage of participants with vital signs (SBP,DBP, pulse rate, respiratory rate, body temperature and SpO2) abnormalities (abnormally low \[ABL\] and abnormally high \[ABH\]) were reported. DBP: ABL: \<35 mmHg:0-3 months (mths), \<40 mmHg:3 mths- \<3.5 years,ABH: \>65 mmHg:0-3 mths, \>85 mmHg:3-12 mths, \>90 mmHg:1-2 years, \>70 mmHg: 2- \<3.5 years; SBP:ABL: \<60 mmHg:0-12 mths,\<75 mmHg:1-2 years, \<80:2- \<3.5 years,ABH: \>110:0-12 mths, \>120 mmHg:1-2 years, \>10 mmHg:2- \<3.5 years; Pulse rate:ABL: \<80 bpm:0-3 mths, \<70 bpm:3 mths-12 mth,\<60 bpm:1-2 years, \<90 bpm:2- \<3.5 years,ABH: \>180 bpm:0-3 mths, \>150 bpm:3 mths-12 mths, \>140 bpm:1-2 years, \>130:2- \<3.5 years; Respiratory rate:ABL: \<25 bpm:0-3 mths, \<20 bpm: 3 mths-12 mths,\<18 bpm:1-2 years, \<20 bpm:2- \<3.5 years, ABH:\>70 bpm:0-3 mths, \>60 bpm:3 mths-12 mths, \>50 bpm:1-2 years, \>35 bpm:2- \<3.5 years; SpO2: ABL: \<92%: 0-\<3.5 years; Temperature (Celsius): ABH:\>37.8:Tympanic, \>38.0:forehead, oral, axillary, \>37.2:rectal.

Cohort 1: Duration of Invasive Ventilation SupportUp to Day 21

For the subset of participants who received invasive ventilation post dose, duration for invasive ventilation could not be derived by individual type as start/end dates and times were not collected in full to allow breakdown of duration derivation by ventilation type and only overall duration of oxygen supplementation (overall ventilation support) could be derived which is reported in the outcome measure "Duration of Supplemental Oxygen". As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure could only have been reported for Cohort 1.

Cohort 1: Percentage of Participants Who Needed Hydration and/or Feeding by Intravenous (IV) Administration or Nasogastric TubeUp to Day 28

Percentage of participants who needed hydration and/or feeding by IV Administration or nasogastric tube after the first dose of study drug was assessed. This parameter was only for participants who didn't require supplemental feeding/hydration before first dose of study drug. As per the study protocol and study design, this outcome measure was planned to be analyzed for participants who were hospitalized only. Only participants in Cohort 1 were hospitalized, hence this outcome measure is only reported for Cohort 1.

Percentage of Participants With Adverse EventsUp to Day 28

Percentage of participants with adverse events was assessed. An AE is any untoward medical occurrence in clinical study participants administered a medicinal (investigational or non-investigational) product. An adverse event does not necessarily have a causal relationship with the intervention.

Percentage of Participants With Abnormal Laboratory FindingsUp to Day 28

Percentage of participants with abnormal laboratory findings (chemistry and hematology) worst toxicity grade was assessed based on Division of Microbiology and Infectious Diseases (DMID) toxicity grading scale. DMID toxicity grades range from 1 to 4. Grade 1 = mild: transient or mild discomfort (\<48 hours); no medical intervention/therapy required. Grade 2 = moderate: mild to moderate limitation in activity - some assistance may be needed; no or minimal medical intervention/therapy required. Grade 3 = severe: marked limitation in activity, some assistance usually required; medical intervention/therapy required, hospitalizations possible. Grade 4 = life-threatening or death: Extreme limitation in activity, significant assistance required; significant medical intervention/therapy required, hospitalization or hospice care probable.

Percentage of Participants With Abnormal Electrocardiograms (ECGs) FindingsUp to Day 28

Percentage of participants with abnormal ECG (PR interval \[for age 0 to 2 years: \>150 msec is abnormally high, for age group 2 to \<3.5 years: \<100 msec is abnormally low and \>150 msec is abnormally high\]; QRS interval \[for 0 to 2 years: \>79 msec is abnormally high, for age group 2 to \<3.5 years: \<40 msec is abnormally low and \>79 msec is abnormally high\]; QT interval \[for age 0 to 2 years: \>500 msec is abnormally high, for age group 2 to \<18 years: \<320 msec is abnormally low and \>450 msec is abnormally high\]; RR interval \[for age 0 to 3 months: \<333 msec is abnormally low and \>750 msec is abnormally high; for age group 3 to 12 months: \<400 msec is abnormally low and \>860 msec is abnormally high; for age 1 to 2 years: \<430 msec is abnormally low and \>1000 msec is abnormally high; for age group 2 to \<18 years: \<600 msec is abnormally low and \>1200 msec is abnormally high\]) findings were assessed.

Percentage of Participants With Medical Resource Utilization (MRU)Up to Day 28

Percentage of participants with MRU (any medical care encounters) was reported.

Percentage of Participants With Acceptability and Palatability of the JNJ-53718678 Formulation as Assessed by Parent(s)/Caregiver(s)Day 8

Percentage of participants with acceptability and palatability of the JNJ-53718678 formulation was assessed through a questionnaire asking about the child's reaction when given the medicine, completed by parent(s)/caregiver(s) after last dosing that categorized as 1) child took medicine easily, 2) disgusted expressions after tasting medicine, 3) cried after tasting medicine, 4) would not open mouth or turned head away to avoid medicine, 5) spit out or coughed out medicine, 6) gagged, and 7) vomited (within 2 minutes of swallowing medicine). Below results are based on response to "child took medicine easily".

Trial Locations

Locations (169)

Madera Family Medical Group

🇺🇸

Madera, California, United States

Saltzer Medical Group

🇺🇸

Nampa, Idaho, United States

SUNY Upstate Medical University - Upstate Golisano Children's Hospital (GCH)

🇺🇸

Syracuse, New York, United States

Hospital Italiano Regional Del Sur

🇦🇷

Bahía Blanca, Argentina

Hospital Universitario Austral

🇦🇷

Pilar, Argentina

UZ Antwerpen

🇧🇪

Edegem, Belgium

C.H.R. Citadelle

🇧🇪

Liège, Belgium

UMHAT 'Sveti Georgi'-Plovdiv

🇧🇬

Plovdiv, Bulgaria

UMHAT 'Aleksandrovska' EAD

🇧🇬

Sofia, Bulgaria

Research Institute for Health Sciences

🇹🇭

Chiang Mai, Thailand

CMPC - Consultoria Médica e Pesquisa Clínica

🇧🇷

Sorocaba, Brazil

Hopitaux pediatriques CHU Lenval

🇫🇷

Nice, France

Santa Casa de Misericórdia de Votuporanga

🇧🇷

Votuporanga, Brazil

Universidade Federal De Minas Gerais - Hospital das Clínicas

🇧🇷

Belo Horizonte, Brazil

Futurenest Klinikai Kutato Kft.

🇭🇺

Miskolc, Hungary

ASST Fatebenefratelli Sacco / Ospedale dei Bambini V. Buzzi

🇮🇹

Milano, Italy

CHU de Montpellier - Arnaud de Villeneuve

🇫🇷

Montpellier, France

Praxiszentrum Triftplatz

🇩🇪

Schönau am Königssee, Germany

Centro de Estudos e Pesquisas em Moléstias Infecciosas - CEPCLIN

🇧🇷

Natal, Brazil

Nucleo de Pesquisa do Hospital Pequeno Princípe

🇧🇷

Curitiba, Brazil

Sociedade Campineira de Educacao e Instrucao - Hospital e Maternidade Celso Pierro

🇧🇷

Campinas, Brazil

Secretaria da Saude do Estado do Ceara - Hospital Doutor Carlos Alberto Studart Gomes

🇧🇷

Fortaleza, Brazil

Associacao Hospitalar Beneficente Sao Vicente de Paulo - Hospital Sao Vicente de Paulo

🇧🇷

Passo Fundo, Brazil

Irmandade Santa Casa de Misericordia de Porto Alegre

🇧🇷

Porto Alegre, Brazil

DCC 'Sv. Vrach and Sv. Sv. Kuzma and Damyan', OOD

🇧🇬

Sofia, Bulgaria

Acibadem City Clinic Tokuda Hospital

🇧🇬

Sofia, Bulgaria

CHU de Caen

🇫🇷

Caen, France

Medical Center-1-Sevlievo EOOD

🇧🇬

Sevlievo, Bulgaria

Hôpital Necker-Enfants Malades

🇫🇷

Paris, France

Kinderarztpraxis Bramsche

🇩🇪

Bramsche, Germany

Kinderärztliche Gemeinschaftspraxis

🇩🇪

Wolfsburg, Germany

Hürthpark Kinder & Jugendärzte

🇩🇪

Hürth, Germany

A.O.U Sant'Orsola-Malpighi

🇮🇹

Bologna, Italy

Università degli Studi di Milano, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

🇮🇹

Milan, Italy

Azienda Ospedaliera di Padova

🇮🇹

Padova, Italy

Szegedi Tudomanyegyetem

🇭🇺

Szeged, Hungary

Dipartimento di Pediatria dell'Ospedale Luigi Sacco

🇮🇹

Milano, Italy

Fejer Varmegyei Szent Gyorgy Egyetemi Oktatokorhaz

🇭🇺

Székesfehérvár, Hungary

Ospedale degli Infermi

🇮🇹

Ponderano, Italy

Hosaka Kodomo Clinic

🇯🇵

Bunkyo-Ku, Japan

Nowon Eulji Medical Center, Eulji University

🇰🇷

Seoul, Korea, Republic of

Inje University Sanggye Paik Hospital

🇰🇷

Seoul, Korea, Republic of

Josha Research

🇿🇦

Bloemfontein, South Africa

OOO 'Medical Technologies'

🇷🇺

St. Petersburg, Russian Federation

Hosp. Univ. Pta. de Hierro Majadahonda

🇪🇸

Majadahonda, Spain

Astrid Lindgrens barnsjukhus Solna

🇸🇪

Stockholm, Sweden

Hosp. Clinico Univ. de Santiago

🇪🇸

Santiago de Compostela, Spain

Ankara Bilkent Sehir Hastanesi

🇹🇷

Ankara, Turkey

The Catholic University of Korea, Incheon St. Mary's Hospital

🇰🇷

Incheon, Korea, Republic of

Children's Hospital Colorado

🇺🇸

Aurora, Colorado, United States

Ann & Robert H. Lurie Children's Hospital of Chicago

🇺🇸

Chicago, Illinois, United States

Tufts Medical Center

🇺🇸

Boston, Massachusetts, United States

Santiago Reyes, MD

🇺🇸

Oklahoma City, Oklahoma, United States

Hopital Charles Nicolle

🇫🇷

Rouen, France

Istanbul University Istanbul Medical Faculty

🇹🇷

Istanbul, Turkey

The Adam Practice

🇬🇧

Poole, United Kingdom

FOMAT Medical Research

🇺🇸

Ventura, California, United States

Elite Clinical Trials

🇺🇸

Blackfoot, Idaho, United States

Craig A. Spiegel, MD

🇺🇸

Bridgeton, Missouri, United States

Hospital Pedro de Elizalde

🇦🇷

City of Buenos Aires, Argentina

Clinica Mayo de UMCB

🇦🇷

San Miguel de Tucuman, Argentina

Hospital del Niño Jesús

🇦🇷

San Miguel de Tucumán, Argentina

ULB Hôpital Erasme

🇧🇪

Anderlecht, Belgium

Fundacao para o Desenvolvimento Medico Hospitalar (UNESP Botucatu)

🇧🇷

Botucatu, Brazil

Fundacao Faculdade Regional de Medicina de Sao Jose do Rio Preto - Hospital de Base

🇧🇷

Sao Jose do Rio Preto, Brazil

Associacao Hospitalar Moinhos de Vento

🇧🇷

Porto Alegre, Brazil

UMHAT 'Dr. Georgi Stranski', EAD

🇧🇬

Pleven, Bulgaria

UMHAT 'Kanev' EAD

🇧🇬

Ruse, Bulgaria

Fundacao Jose Luiz Egydio Setubal

🇧🇷

Sao Paulo, Brazil

Hopital Antoine Beclere

🇫🇷

CLAMART Cedex, France

CHU de Nantes hôtel-Dieu

🇫🇷

Nantes, France

Siberian State Medical University

🇷🇺

Tomsk, Russian Federation

Universitätsklinikum Würzburg

🇩🇪

Würzburg, Germany

Department of Pediatrics University of Pavia, Policlinico San Matteo

🇮🇹

Pavia, Italy

Kobayashi Pediatric Clinic

🇯🇵

Fujieda, Japan

Momotaro Clinic

🇯🇵

Okayama City, Japan

National Hospital Organization Saitama National Hospital

🇯🇵

Saitama, Japan

Kangbuk Samsung Hospital

🇰🇷

Seoul, Korea, Republic of

Hospital Tuanku Fauziah

🇲🇾

Pusat Bandar Kangar, Malaysia

Hospital Infantil de Mexico Federico Gomez

🇲🇽

Ciudad De Mexico, Mexico

Osrodek Badan Klinicznych In-Vivo Sp. z o.o.

🇵🇱

Bydgoszcz, Poland

Krakowski Szpital Specjalistyczny im. Jana Pawla II, Oddzial Pediatrii i Neurologii Dzieciecej

🇵🇱

Krakow, Poland

NZOZ Salmed

🇵🇱

Leczna, Poland

OOO MDP-Medical Group

🇷🇺

Odintsovo, Russian Federation

Bashkir State Medical University

🇷🇺

Ufa, Russian Federation

LLC Kurator

🇷🇺

St. Petersburg, Russian Federation

Tygrberg Hospital

🇿🇦

Bellville, South Africa

VX Pharma

🇿🇦

Pretoria, South Africa

Two Military Hospital

🇿🇦

Wynberg, South Africa

Hosp. Univ. Germans Trias I Pujol

🇪🇸

Badalona, Spain

Hosp. Del Mar

🇪🇸

Barcelona, Spain

Hosp. Univ. de Burgos

🇪🇸

Burgos, Spain

Hosp. Univ. de Getafe

🇪🇸

Getafe, Spain

Hosp. Univ. Fund. Jimenez Diaz

🇪🇸

Madrid, Spain

Hosp. Regional Univ. de Malaga

🇪🇸

Malaga, Spain

Hosp. Univ. 12 de Octubre

🇪🇸

Madrid, Spain

Hosp. Univ. La Paz

🇪🇸

Madrid, Spain

Hosp. Quiron Madrid Pozuelo

🇪🇸

Pozuelo de Alarcon, Spain

Hosp. Puerta Del Sur

🇪🇸

Mostoles, Spain

Hosp. Clinico Univ. de Salamanca

🇪🇸

Salamanca, Spain

Barn- Och Ungdomsmedicin

🇸🇪

Malmö, Sweden

Sachsska barn-och ungdomssjukhuset

🇸🇪

Stockholm, Sweden

Hsinchu MacKay Memorial Hospital

🇨🇳

Hsinchu, Taiwan

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

Taichung Veterans General Hospital

🇨🇳

Taichung, Taiwan

Queen Sirikit National Institute of Child Health

🇹🇭

Bangkok, Thailand

Tropical Medicine Hospital, Mahidol University

🇹🇭

Bangkok, Thailand

Siriraj Hospital Mahidol University

🇹🇭

Bangkok, Thailand

Taipei Municipal Wanfang Hospital

🇨🇳

Taipei, Taiwan

Chang Gung Memorial Hospital- Linkou

🇨🇳

Taoyuan City, Taiwan

Chiang Mai University

🇹🇭

Chiang Mai, Thailand

Srinagarind Hospital

🇹🇭

Khon Kaen, Thailand

Cukurova University Medical Faculty Balcali Hospital

🇹🇷

Adana, Turkey

Ankara University Medical Faculty

🇹🇷

Ankara, Turkey

Hacettepe University Medical Faculty

🇹🇷

Ankara, Turkey

Gazi University Medical Faculty

🇹🇷

Ankara, Turkey

Ege University Medical Faculty

🇹🇷

Izmir, Turkey

Saglik Bilimleri University Sariyer Hamidiye Etfal Training and Research Hospital

🇹🇷

Sarıyer, Turkey

Whipps Cross University Hospital

🇬🇧

London, United Kingdom

Karadeniz Teknik University Medical Faculty

🇹🇷

Trabzon, Turkey

Royal Devon & Exeter Hospital

🇬🇧

Exeter, United Kingdom

OOO 'Arsvite North-West'

🇷🇺

St. Petersburg, Russian Federation

Yaroslavl State Medical University Based On Children Polyclinics #5

🇷🇺

Yaroslavl, Russian Federation

Fundación Respirar

🇦🇷

Ciudad Autonoma de Buenos Aires, Argentina

SHATCD 'Prof. Ivan Mitev' EAD

🇧🇬

Sofia, Bulgaria

National Hospital Organization Kanazawa Medical Center

🇯🇵

Kanazawa, Japan

INAMI Pediatric clinic

🇯🇵

Tokyo, Japan

Hospital Universitario 'Dr. Jose Eleuterio Gonzalez'

🇲🇽

Monterrey, Mexico

ALERGO-MED Specjalistyczna Przychodnia Lekarska Sp. z o.o.

🇵🇱

Tarnow, Poland

Szpital im. Swietej Jadwigi Slaskiej, Oddział Pediatryczny z Pododdziałem Niemowlęcym

🇵🇱

Trzebnica, Poland

City Children Clinical Outpatient Clinic #5

🇷🇺

Perm, Russian Federation

Hospital Central Militar Cirujano Mayor Dr Cosme Argerich

🇦🇷

Buenos Aires, Argentina

Csolnoky Ferenc Korhaz

🇭🇺

Veszprém, Hungary

Hospital Selayang

🇲🇾

Batu Caves, Malaysia

RM Pharma Specialists

🇲🇽

Benito Juarez, Mexico

Hospital Civil de Guadalajara

🇲🇽

Guadalajara, Mexico

Instytut Gruzlicy i Chorob Pluc Oddzial Terenowy im. Rudnikow w Rabce-Zdroj, Oddzial Pulmonologii

🇵🇱

Rabka-Zdroj, Poland

Children Outpatient Clinic 45 Of Nevskiy Region

🇷🇺

St. Petersburg, Russian Federation

Sanford Health

🇺🇸

Sioux Falls, South Dakota, United States

Infectious Clinical Hospital #1 Of The Moscow City Health Department

🇷🇺

Moscow, Russian Federation

Hospital Italiano de La Plata

🇦🇷

Ciudad De La Plata, Argentina

Debreceni Egyetem Klinikai Kozpont

🇭🇺

Debrecen, Hungary

National Hospital Organization Fukuyama Medical Center

🇯🇵

Fukuyama, Japan

Kagoshima Children's Hospital

🇯🇵

Hioki, Japan

Shirao Clinic of Pediatrics and Pediatric Allergy

🇯🇵

Hiroshima, Japan

Okawa Children & Family Clinic

🇯🇵

Tokyo, Japan

Hospital Miri

🇲🇾

Miri, Malaysia

Kaohsiung Chang Gung Memorial Hospital

🇨🇳

Kaohsiung, Taiwan

West Virginia University

🇺🇸

Morgantown, West Virginia, United States

CEMIC (Centro de Educación Médica e Investigaciones Clínicas)

🇦🇷

City of Buenos Aires, Argentina

National Hospital Organization Hirosaki General Medical Center

🇯🇵

Hirosaki, Japan

Daido Hospital

🇯🇵

Nagoya, Japan

KKR Sapporo Medical Center

🇯🇵

Sapporo, Japan

Instituto Nacional de Pediatría

🇲🇽

Coyoacan, Mexico

LLC Pitercliniсa

🇷🇺

St. Petersburg, Russian Federation

Coastal Pediatric Research

🇺🇸

Summerville, South Carolina, United States

Semmelweis Egyetem, II. sz. Gyermekgyógyászati Klinika

🇭🇺

Budapest, Hungary

Debreceni Egyetem Klinikai Központ,Infektológiai Klinika

🇭🇺

Debrecen, Hungary

Kanizsai Dorottya Kórház

🇭🇺

Nagykanizsa, Hungary

Fukui-ken Saiseikai Hospital

🇯🇵

Fukui City, Japan

Fukuyama City Hospital

🇯🇵

Fukuyama, Japan

Tanabe Pediatrics Clinic

🇯🇵

Hatsukaichi, Japan

Kojunkai Daido Clinic

🇯🇵

Nagoya, Japan

National Hospital Organization Beppu Medical Center

🇯🇵

Oita, Japan

Tsuda Pediatrics Clinic

🇯🇵

Setagaya-ku, Japan

Hospital Sibu

🇲🇾

Sibu, Malaysia

Zespol Opieki Zdrowotnej w Debicy, Oddzial Dzieciecy

🇵🇱

Debica, Poland

Dél-pesti Centrumkórház - Országos Hematológiai és Infektológiai Intézet, Szent László Telephely

🇭🇺

Budapest, Hungary

Children's Hospital of Richmond at VCU

🇺🇸

Richmond, Virginia, United States

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