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A randomized phase II multicenter study with a safety run-in to assess the tolerability and efficacy of the addition of oral lenalidomide to standard induction therapy in AML and RAEB ≥ 66 years and very poor risk AML ≥ 18 years.

Recruiting
Conditions
Acute Myeloid leukemia (AML), RAEB
Registration Number
NL-OMON25046
Lead Sponsor
HOVON foundation
Brief Summary

/A

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
Not specified
Target Recruitment
200
Inclusion Criteria

1. Patients eligible for standard chemotherapy;

2. Patients ≥ 66 years with a cytopathologically confirmed diagnosis according WHO classification of:

Exclusion Criteria

1. Acute promyelocytic leukemia;

2. Patients previously treated for AML (any antileukemic therapy including investigational agents)- a short treatment period (< 2 weeks) with Hydroxyurea is allowed;

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Part A of the study (if applicable):<br /><br>1. To assess the safety and tolerability of lenalidomide added to standard induction chemotherapy for AML (frequency and severity of toxicities and the durations of neutropenia and thrombocytopenia) and select the feasible dose level for part B of the study;<br /><br>2. To assess in a randomized comparison the effect of lenalidomide on the CR rate.<br /><br>Part B of the study:<br /><br>1. To assess the safety and tolerability of lenalidomide added to standard induction chemotherapy for AML (frequency and severity of toxicities and the durations of neutropenia and thrombocytopenia) as regards the selected dose level of lenalidomide;<br /><br>2. To assess in a randomized comparison the effect of the in Part A selected dose of lenalidomide on the CR rate.
Secondary Outcome Measures
NameTimeMethod
For part B:<br /><br>1. To determine the efficacy profile (event free survival (EFS), disease free survival (DFS) and overall survival (OS)) associated with the two therapy regimens;<br /><br>2. To measure MRD by immunophenotyping in relation to clinical response parameters;<br /><br>3. To identify potential biomarkers predictive of response, EFS, DFS and OS by exploratory genomic analysis (microarray, gene mutations).
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