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An open label, single dose study to assess the pharmacokinetics of a microdose of recombinant human placental alkaline phosphatase (hRESCAP, part 1) followed by a randomized, double-blind, placebo-controlled, parallel, single ascending dose, first-in-human study to assess safety and tolerability of hRESCAP (part 2) in healthy male volunteers

Completed
Conditions
inflammation
10003816
10004018
Registration Number
NL-OMON38993
Lead Sponsor
Centre for Human Drug Research
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Not specified
Target Recruitment
15
Inclusion Criteria

1. Healthy male subjects, 18 - 45 years of age, inclusive. Healthy status is defined by absence of evidence of any active or chronic disease following a detailed medical and surgical history, a complete physical examination including vital signs, 12-lead ECG, haematology, blood chemistry, and urinalysis;
2. Body mass index (BMI) between 18 and 30 kg/m2, inclusive;
3. Ability to communicate well with the investigator in the Dutch language;
4. Able to participate and willing to give written informed consent and to comply with the study restrictions;
5. Venous access sufficient to allow blood sampling as per protocol.

Exclusion Criteria

1. Any clinically significant abnormality as determined by medical history taking and physical examinations obtained during the screening visit that in the opinion of the investigator would interfere with the study objectives or compromise subject safety;
2. History of a surgical event that may significantly affect the study outcome;
3. History of allergy or other inflammatory indications;
4. History of asthma or other inflammatory disease;
5. Use of prescription medications within 21 days prior to study drug administrations, or less than 5 half-lives, whichever is longer, and during the course of the study.
6. Alkaline Phosphatase levels in plasma of < 30 IU/L or > 115 IU/L;
7. Clinically relevant abnormal laboratory results, ECG, vital signs, or physical findings at screening that in the opinion of the investigator would interfere with the study objectives or compromise subject safety;
8. Participation in an investigational drug study within 3 months prior to screening or more than 4 times in the past year;
9. Any psychological conditions which, in the opinion of the investigator, might create undue risk to the subject or interfere with the subject's ability to comply with the protocol;
10. History of alcohol or illicit drug abuse (alcohol abuse defined as alcohol consumption > 28 units/week);
11. Reported unexplained weight loss or weight gain of > 2 kg in the month prior to screening;
12. Positive test results for Hepatitis B, Hepatitis C or HIV;
13. Donation of blood within 3 months prior to screening or donation of plasma within 14 days prior to screening;
14. Not having a general practitioner;
15. Not willing to accept information transfer which concerns participation in the study, or information regarding health, like laboratory results, findings at anamnesis or physical examination and eventual adverse events to and from his general practitioner;
16. Not willing to give permission to have the general practitioner to be notified upon participation in this study;
17. Prior participation in part 1 for subjects participating in part 2 of the study;
18. Not willing to use effective (double barrier) contraception until at least 3 months after dose administration.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
<p>Tolerability / Safety endpoint<br /><br>- Assessment of adverse events, local tolerability, vital signs, clinical<br /><br>chemistry and haematology parameters.<br /><br><br /><br>Pharmacokinetic endpoints<br /><br>- Assessment of PK after microdose administration of 53 µg [14C]-hRESCAP;<br /><br>- Determination of the half-life of [14C]-hRESCAP within pharmacological<br /><br>relevant dose-range (414-5300 µg).<br /><br><br /><br>Pharmacodynamic endpoints<br /><br>- Assessment of the total alkaline phosphatase activity by standard assay;<br /><br>- Determination of placental alkaline phosphatase activity with an assay<br /><br>specific for placental alkaline phosphatase.</p><br>
Secondary Outcome Measures
NameTimeMethod
<p>N/A</p><br>
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