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Investigating the safety and efficacy of a Universal CAR-T cell immunotherapy in patients with relapse and refractory T-cell acute lymphoblastic leukemia and T lymphoblastic lymphoma

Phase 1
Conditions
Relapse and Refractory T cell acute lymphoblastic leukaemia (T-ALL), Relapse and Refractory T cell lymphoblastic lymphoma (T-LBL)
Acute lymphoblastic leukaemia, lymphoblastic T-cell lymphoma
Cancer
Registration Number
ISRCTN19144142
Lead Sponsor
Gracell Biotechnologies Co., Ltd
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Ongoing
Sex
All
Target Recruitment
15
Inclusion Criteria

1. 2 to 70 years
2. Diagnosed with relapsed and refractory CD7 + T cell acute lymphocytic leukemia (T-ALL) or relapsed and refractory CD7 + T lymphoblastic lymphoma (T-LBL)
3. Quantifiable tumor burden
4. Eastern cooperative oncology group (ECOG) performance status of 0 to 2
5. Life expectancy =12 weeks
6. Adequate organ function defined as:
a. Serum ALT/AST =2.5 ULN
b. Creatinine clearance (as estimated by Cockcroft Gault) =60 mL/min
c. PT and APTT=1.5 ULN
d. Total bilirubin =1.5 ULN
e. Cardiac ejection fraction =45%
f. No clinically significant ECG findings
g. Baseline oxygen saturation >90% on room air
7. Recovered from acute toxic effects of prior chemotherapy =one week before entering this study
8. Agreement to use of medical-approved-contraception during the period of trial and in 1 year after cell transfusion therapy
9. Signed informed consent form

Exclusion Criteria

1. Diagnosis of other malignancy (except non-melanoma and cervical carcinoma in situ, bladder cancer, breast cancer that have a disease-free survival of more than 5 years)
2. Severe mental disorders
3. History of hereditary diseases, including but not limited to: Fanconi anemia, Shut-Dai syndrome, Costman syndrome or any other known bone marrow failure syndrome
4. Grade 2-4 acute graft-versus-host disease (GVHD) (Glucksberg criteria) or extensive chronic GVHD (Seattle criteria)
5. Grade III-IV heart failure or myocardial infarction, angioplasty or stent placement, unstable angina pectoris, or other clinically prominent heart disease within one year before enrollment
6. History or presence of CNS disorder, including but not limited to: seizure disorder, cerebrovascular ischemia/hemorrhage, dementia, cerebellar disease, or any autoimmune disease with CNS involvement
7. Positive for any of the following etiological tests: HIV, HBV, HCV, TPPA
8. Presence of fungal, bacterial, viral, or other infection that is uncontrolled
9. Severe allergies
10. History of autoimmune disease resulting in end organ injury or requiring systemic immunosuppression/systemic disease modifying agents within the last 2 years
11. History or diagnosis of pulmonary fibrosis
12. Participation in other clinical trials =4 weeks prior to enrollment
13. Concomitant disease that require systemic steroids or other immune suppressive therapy during the study period in researcher's judgement
14. Patients who are contraindicated to cyclophosphamide, fludarabine, or melphalan
15. Allogeneic cell therapy (such as donor lymphocyte infusion, DLI) =6 weeks prior to enrollment
16. Poor adherence due to physical, family, social, geographic, and other factors, who cannot follow the research plan and follow-up plan
17. Pregnant and lactating women
18. Any other conditions that researcher think it is inappropriate for the subject to anticipate the trial

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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