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Isavuconazole in the Treatment of Renally Impaired Aspergillosis and Rare Fungi

Phase 3
Completed
Conditions
Aspergillosis
Invasive Fungal Infections
Interventions
Registration Number
NCT00634049
Lead Sponsor
Astellas Pharma Inc
Brief Summary

The purpose of this study is to investigate the efficacy and safety of isavuconazole in the treatment of renally impaired participants with invasive fungal infections caused by Aspergillus and participants with invasive fungal disease caused by rare fungi.

Detailed Description

Acute invasive fungal infections caused by aspergillus, rare moulds, yeasts or dimorphic fungi are life threatening diseases. Early treatment with highly effective anti-fungals reduces mortality. This study investigates the safety and efficacy of isavuconazole in participants with aspergillosis and renal impairment, and in participants suffering from invasive infections from rare fungi.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
149
Inclusion Criteria

•Participants meeting EORTC/MSG (European Organization for the Research and Treatment of Cancer/Mycoses Study Group) definition of proven or culture positive probable IFD (invasive fungal disease) caused by rare moulds, yeasts, or dimorphic fungi (i.e. fungal pathogens other than Aspergillus fumigatus or Candida species) whether renally impaired or not (including dialysis) who require primary therapy for their IFD at the time of enrollment.

OR

•Participants who had proven or probable zygomycosis, whether renally impaired or not (including dialysis), who require primary therapy. Zygomycosis must be documented by culture or histology / cytology.

OR

•Participants meeting EORTC/MSG definition of proven or culture positive probable IFD caused by rare moulds, yeasts, or dimorphic fungi (i.e., fungal pathogens other than Aspergillus fumigatus or Candida species), whether RI or not (including dialysis), who were refractory to current treatment defined as,

  • Clear documentation of progression of disease. Note: radiological progression only in association with white blood cell (WBC) count recovery was not acceptable.
  • Failure to improve clinically despite receiving at least 7 days of standard antifungal regimen. Prior to enrolling patients who fell into this category, the Medical Monitor was contacted for approval.

OR

• Participants meeting EORTC/MSG definition of proven or culture positive probable IFD caused by rare moulds, yeasts, or dimorphic fungi (i.e., fungal pathogens other than Aspergillus fumigatus or Candida species), whether RI or not (including dialysis), who were intolerant to current treatment for example:

  • Doubling of serum creatinine value to higher than the upper limit of normal (ULN) within 48 hours.
  • Serum creatinine > 2.0 mg/mL and current treatment with polyene or IV voriconazole.
  • Other significant drug-related adverse reaction(s) to the current antifungal agent, resulting in discontinuation of the treatment, e.g., persistence of visual disturbance, allergic reaction, phototoxicity or severe infusion reaction (hypertensive crisis, severe chills or shock).
  • Documented inability to achieve adequate blood levels of posaconazole, voriconazole or itraconazole.
Exclusion Criteria
  • A known condition of the participants that may jeopardize adherence to the protocol requirements
  • Participants who are unlikely to survive 30 days
  • Participants with a body weight < 40 kg
  • Women who are pregnant or breastfeeding

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
IsavuconazoleisavuconazoleAdministration of isavuconazole 3 times a day in the vein (IV) or oral as a capsule for 2 days followed by daily administration of isavuconazole (IV) or oral
Primary Outcome Measures
NameTimeMethod
Crude Success Rate of Overall Outcome of Treatment Evaluated by the Data Review Committee (DRC) at Day 42, 84 and End of Treatment (EOT).Day 42, 84 and End of Treatment (EOT [Day 180])

The DRC assessed overall response based on individual clinical, mycological and radiological response assessments. Overall response outcomes were described as Success (complete or partial). Complete success was defined as a resolution of all clinical symptoms and physical findings associated with IFD. Partial success was defined as a resolution of at least some clinical symptoms and physical findings associated with IFD End of treatment (EOT) is the last day of study drug administration, with an estimated duration up to 180 days.

Secondary Outcome Measures
NameTimeMethod
Crude Success Rate of Clinical Response to Treatment Evaluated by the Data Review Committee (DRC) at Day 42, 84 and EOTDay 42, 84 and End of Treatment (EOT [Day 180])

The DRC evaluated clinical response to treatment at day 42, day 84 and EOT. Clinical response outcomes were described as Success \[Resolution of all attributable clinical symptoms and physical findings and Partial resolution of attributable clinical symptoms and physical findings\]. End of treatment (EOT) is the last day of study drug administration, with an estimated duration up to 180 days.

Crude Success Rate of Mycological Response to Treatment Evaluated by the Data Review Committee (DRC) at Day 42, 84 and EOTDay 42, 84 and End of Treatment (EOT [Day 180])

The DRC evaluated mycological response to treatment at day 42, day 84 and EOT. Mycological response outcomes were described as Success \[Eradication and Presumed eradication\]. End of treatment (EOT) is the last day of study drug administration, with an estimated duration up to 180 days.

Crude Success Rate of Radiological Response to Treatment Evaluated by the Data Review Committee (DRC) at Day 42, 84 and EOTDay 42, 84 and End of Treatment (EOT [Day 180])

The DRC evaluated radiological response to treatment at at day 42, day 84 and EOT. Radiological response outcomes were described as Success \[Improvement of at least 25% from baseline for invasive aspergillosis and other filamentous mold infections\], \[Improvement of at least 50% from baseline for invasive aspergillosis and other filamentous mold infections\]; and \[Improvement of at least 25% from baseline if EOT occurs prior to day 42 and at least 50% improvement from baseline if EOT occurs after day 42 for invasive aspergillosis and other filamentous mold infections\]. End of treatment (EOT) is the last day of study drug administration, with an estimated duration up to 180 days.

Crude Success Rate of Clinical Response to Treatment Evaluated by the Investigator at Day 42, Day 84 and EOTDay 42, Day 84 and End of Treatment (EOT [Day 180])

The Investigator evaluated clinical response to treatment at day 42, day 84 and EOT. Clinical response outcomes were described as Success \[Resolution of all attributable clinical symptoms and physical findings\] and \[Resolution of some attributable clinical symptoms and physical findings\]. End of treatment (EOT) is the last day of study drug administration, with an estimated duration up to 180 days.

Crude Success Rate of Mycological Response to Treatment Evaluated by the Investigator at Day 42, Day 84 and EOTDay 42, Day 84 and End of Treatment (EOT [Day 180])

The Investigator evaluated mycological response to treatment at day 42, day 84 and EOT. Mycological response outcomes were described as Success \[Eradication,Presumed eradication\]. End of treatment (EOT) is the last day of study drug administration, with an estimated duration up to 180 days.

Crude Success Rate of Radiological Response to Treatment Evaluated by the Investigator at Day 42, Day 84 and EOTDay 42, Day 84 and End of Treatment (EOT [Day 180])

The Investigator evaluated radiological response to treatment at day 42, day 84 and EOT. Radiological response outcomes were described as Success \[≥ 90% improvement,≥ 50% to \< 90% improvement and ≥ 25% to \< 50% improvement (for day 42 and EOT, if EOT occurs prior to day 42)\]. End of treatment (EOT) is the last day of study drug administration, with an estimated duration up to 180 days.

All-cause Mortality Through Day 42 and Day 84Baseline to End of Treatment (EOT [Day 180])

All-cause Mortality was assessed through Day 42 and Day 84 and summarized for ITT population End of treatment (EOT) is the last day of study drug administration, with an estimated duration up to 180 days.

Safety - Overall Number of TEAEsFrom the first study drug administration until 28 days after the last dose of study drug

A Treatment Emergent Adverse Events (TEAE) is any adverse event that starts after the first administration of study drug until 28 days after the last dose of study drug.

Trial Locations

Locations (96)

UMASS Memorial Medical Center

🇺🇸

Worcester, Massachusetts, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

Upstate Infectious Diseases Association LLP

🇺🇸

Albany, New York, United States

Instituto Medico Especializado Alexander Fleming

🇦🇷

Ciudad Autonoma, Argentina

Hospital Nuestra Senora de la Misericordia

🇦🇷

Cordoba, Argentina

Hospital San Roque

🇦🇷

Cordoba, Argentina

Centro Polivalente de Asistencia e Investigación Clínica - CER San Juan

🇦🇷

San Juan, Argentina

Institut Jules Bordet

🇧🇪

Brussels, Belgium

Erasme Hospital

🇧🇪

Bruxelles, Belgium

Universitaire Ziekenhuizen Leuven

🇧🇪

Leuven, Belgium

Hôpital Maisonneuve - Rosemont

🇨🇦

Montréal, Quebec, Canada

National Cancer Institute

🇪🇬

Cairo, Egypt

Hospital Universitario Dr Jose Eleuterio Gonzalez

🇲🇽

Monterrey, Mexico

Ramathibodi Hospital

🇹🇭

Ratchathewi, Thailand

University of California Davis Health System

🇺🇸

Sacramento, California, United States

Emory Hospital

🇺🇸

Atlanta, Georgia, United States

Temple University Health Sciences

🇺🇸

Philadelphia, Pennsylvania, United States

Hamilton Health Sciences - Henderson Site

🇨🇦

Hamilton, Ontario, Canada

Hospital Professor Edmundo Vasconcelos

🇧🇷

São Paulo, Brazil

University of Chicago, Division of Infectious Diseases

🇺🇸

Chicago, Illinois, United States

Institut Paoli Calmette - Marseille

🇫🇷

Marseille Cedex 9, France

Hôpital de Brabois Adultes

🇫🇷

Vandoeuvre les Nancy, France

Stanford University Hospital

🇺🇸

Stanford, California, United States

Mater Medical Centre

🇦🇺

South Brisbane, Australia

Indiana BMT

🇺🇸

Beech Grove, Indiana, United States

Regional Infection Diseases Infusion Center Inc.

🇺🇸

Lima, Ohio, United States

City Of Hope National Medical Center

🇺🇸

Duarte, California, United States

Hospital das Clinicas da UFPR

🇧🇷

Curitiba, Brazil

Hospital de Clinicas da FMUSP - Ribeirao Preto

🇧🇷

Ribeirao Preto, Brazil

Hospital Universitario de Santa Maria

🇧🇷

Santa Maria, Brazil

Medanta Medicity Hospital

🇮🇳

Gurgaon, Haryan, India

Universitair Ziekenhuis Gent

🇧🇪

Gent, Belgium

Tata Memorial Hopital, Department of Anesthesia

🇮🇳

Mumbai, Mahara, India

Nasser Institute

🇪🇬

Cairo, Egypt

Santa Casa de Misericordia de Belo Horizonte

🇧🇷

Belo Horizonte, Brazil

Hospital Felicio Rocho

🇧🇷

Belo Horizonte, Brazil

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

University of Pittsburgh Medical Center Health System

🇺🇸

Pittsburgh, Pennsylvania, United States

Hospital Italiano de Buenos Aires

🇦🇷

Ciudad Autonoma, Argentina

The Ottawa Hospital - General Campus

🇨🇦

Ottawa, Ontario, Canada

Hospital Universitario Clementino Fraga Filho

🇧🇷

Rio de Janeiro, Brazil

Alexandria University Hospital

🇪🇬

Alexandria, Egypt

Maharaj Nakorn Chiang Mai Hospital

🇹🇭

Muang, Thailand

Ochsner Clinic Foundation

🇺🇸

New Orleans, Louisiana, United States

California Pacific Medical Center

🇺🇸

San Francisco, California, United States

Infectious Disease of Indiana

🇺🇸

Indianapolis, Indiana, United States

University of Minnesota

🇺🇸

Minneapolis, Minnesota, United States

University of Texas MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Fred Hutchinson Cancer Research Center, Clinical Research

🇺🇸

Seattle, Washington, United States

Rabin MC

🇮🇱

Petah Tikva, Israel

Chaim Sheba Medical Center

🇮🇱

Ramat-Gan, Israel

Soonchunhyang University Bucheon Hospital

🇰🇷

Buchon-si, Korea, Republic of

Rambam Health Care Campus

🇮🇱

Haifa, Israel

University of California at San Francisco

🇺🇸

San Francisco, California, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

University Of Colorado Health Sciences Center

🇺🇸

Aurora, Colorado, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

Brigham & Womens Hospital

🇺🇸

Boston, Massachusetts, United States

Wayne State University School of Medicine

🇺🇸

Detroit, Michigan, United States

Princess Alexandria Hospital

🇦🇺

Woolloongabba, Australia

Hadassah Universtiy Hospital - Ein Kerem

🇮🇱

Jerusalem, Israel

Hospital Clinico San Borja Arriaran

🇨🇱

Santiago, Chile

Hôpital Edouard Herriot

🇫🇷

Lyon cedex 3, France

Hotel Dieu

🇫🇷

Nantes, France

Hôpital Saint-Louis

🇫🇷

Paris Cedex 10, France

Universitaetsklinikum Aachen

🇩🇪

Aachen, Germany

Hopital Hautepierre

🇫🇷

Strasbourg Cedex, France

Charite-Campus Benjamin Franklin

🇩🇪

Berlin, Germany

Universitaet Koeln

🇩🇪

Köln, Germany

Klinikum Neuperlach

🇩🇪

Muenchen, Germany

Medizinische Klinik und Polyklinik II

🇩🇪

Würzburg, Germany

Shirdi Sai Baba Cancer Hospital K. M. C. Hospital

🇮🇳

Manipal, Kama, India

Deenanath Mangeshkar Hospital & Research Centre

🇮🇳

Pune, Mahara, India

Global Hospitals & Health City

🇮🇳

Chennai, Tamilna, India

Sterling Hospital

🇮🇳

Ahmedabad, India

Apollo Hospitals

🇮🇳

Hyderabad, India

Sahyadri Specialty Hospital

🇮🇳

Pune, India

Sourasky MC Ichilov Hospital Tel Aviv

🇮🇱

Tel Aviv, Israel

Gachon University Gil Hospital

🇰🇷

Incheon, Korea, Republic of

The Catholic University of Korea

🇰🇷

Seoul, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

American University of Beirut Medical Center

🇱🇧

Beirut, Lebanon

Clinique Dr. Rizk

🇱🇧

Beirut, Lebanon

Antiguo Hospital Civil de Guadalajara Fray Antonio Alcalde

🇲🇽

Guadalajara, Mexico

Rafik Hariri University Hospital

🇱🇧

Beirut, Lebanon

Instituto Nacional de Ciencias Medicas y Nutricion Salvador

🇲🇽

Mexico City, Mexico

Hospital Central Dr Ignacio Morones Prieto

🇲🇽

San Luis Potosi, Mexico

Samodzielny Publiczny Centralny Szpital Kliniczny

🇵🇱

Warszawa, Poland

S.I. Russian Oncological Research Center n.a. N.N. Blokhin

🇷🇺

Moscow, Russian Federation

State Institution "Hematology Research Center" RAMS

🇷🇺

Moscow, Russian Federation

Republican Hospital named after V.A. Baranov

🇷🇺

Petrozavodsk, Russian Federation

St-Petersburg MA Postgraduate Education

🇷🇺

St. Petersburg, Russian Federation

Private Practice

🇿🇦

Lyttleton, Gauteng, South Africa

Songklanagarind Hospital

🇹🇭

Hat Yai, Thailand

Maharat Nakhon Ratchasima Hospital

🇹🇭

Muang, Thailand

Srinagarind Hospital

🇹🇭

Muang, Thailand

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