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To Evaluate the Effect of Different Doses of SAR156597 Given to Patients With Idiopathic Pulmonary Fibrosis (IPF)

Phase 1
Completed
Conditions
Idiopathic Pulmonary Fibrosis
Interventions
Drug: Placebo (for SAR156597)
Registration Number
NCT01529853
Lead Sponsor
Sanofi
Brief Summary

Primary Objective:

To assess in adult patients with Idiopathic Pulmonary Fibrosis (IPF) the safety and tolerability of ascending doses of SAR156597 administered subcutaneously (SC) once weekly over a 6-week period.

Secondary Objectives:

To assess in adult patients with IPF:

* The pharmacodynamic effects of SAR156597, as measured on pulmonary function tests (PFTs), pulse oximetry and patient reported outcome and peripheral blood biomarkers.

* The trough plasma concentrations of SAR156597

* The potential immunogenicity of SAR156597.

Detailed Description

The study consists of a screening period of up to 28 days, treatment period of up to 6 weeks and a post-treatment follow-up period of up to 12 weeks. Total study duration is up to 22 weeks.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
24
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
SAR156597 dose 1SAR156597SAR156597 dose 1, subcutaneous injection once every week
SAR156597 dose 2SAR156597SAR156597 dose 2, subcutaneous injection once every week
SAR156597 dose 3SAR156597SAR156597 dose 3, subcutaneous injection once every week
PlaceboPlacebo (for SAR156597)Placebo (for SAR156597), subcutaneous injection once every week
Primary Outcome Measures
NameTimeMethod
Safety/tolerability: Number of participants with Adverse eventsfrom first dose of study drug up to Week 18
Secondary Outcome Measures
NameTimeMethod
Pharmacodynamic: Change in plasma levels of biomarkersfrom baseline to week 18
Pharmacokinetic: SAR156597 plasma concentrationfrom baseline to week 18
Pharmacodynamic: Change in forced (expiratory) vital capacity (FVC)from baseline to week 6
Pharmacodynamic: Change in carbon monoxide diffusing lung capacity (DLco)from baseline to week 6
Pharmacodynamic: Change in Saint George Respiratory Questionnaire (SGRQ)from baseline to week 6

Trial Locations

Locations (21)

Investigational Site Number 840010

🇺🇸

Charleston, South Carolina, United States

Investigational Site Number 152003

🇨🇱

Santiago, Chile

Investigational Site Number 840013

🇺🇸

New York, New York, United States

Investigational Site Number 840009

🇺🇸

Jacksonville, Florida, United States

Investigational Site Number 724002

🇪🇸

Barcelona, Spain

Investigational Site Number 152001

🇨🇱

Santiago, Chile

Investigational Site Number 724001

🇪🇸

Barcelona, Spain

Investigational Site Number 124001

🇨🇦

Hamilton, Canada

Investigational Site Number 840011

🇺🇸

Jacksonville, Florida, United States

Investigational Site Number 152002

🇨🇱

Santiago, Chile

Investigational Site Number 484003

🇲🇽

Mexico City, Mexico

Investigational Site Number 124002

🇨🇦

Vancouver, Canada

Investigational Site Number 840004

🇺🇸

Joliet, Illinois, United States

Investigational Site Number 840002

🇺🇸

Wichita, Kansas, United States

Investigational Site Number 484002

🇲🇽

Monterrey, Mexico

Investigational Site Number 124003

🇨🇦

Edmonton, Canada

Investigational Site Number 840008

🇺🇸

Sacramento, California, United States

Investigational Site Number 840006

🇺🇸

Chicago, Illinois, United States

Investigational Site Number 840005

🇺🇸

Maywood, Illinois, United States

Investigational Site Number 840003

🇺🇸

Minneapolis, Minnesota, United States

Investigational Site Number 840014

🇺🇸

Cincinnati, Ohio, United States

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