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Characteristics of Patients With Sickle Cell Disease

Completed
Conditions
Sickle Cell Disease
Interventions
Other: Crizanlizumab
Registration Number
NCT05494541
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

This was a retrospective descriptive analysis of health care claims data using the IQVIA open source medical and pharmacy claims databases.

Detailed Description

Patients with a diagnosis of SCD between November 1, 2018 and April 30, 2021 were identified. Among these patients, those who initiated crizanlizumab between November 1, 2019 and January 31, 2021 (index period) were selected into the treatment cohort. The indexing timeframe allowed for a 1-year lookback period and a minimum of 3 months (3m cohort) of follow-up. A subset of the 3m cohort with 6-months of available (6m cohort) follow-up was performed. The index date was the date of the first crizanlizumab administration.

Study period: 01 November 2018 - 30 April 2021 Index period: 01 November 2019 - 31 January 2021 Index date: Date of the first claim for administration of crizanlizumab in the index period

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
540
Inclusion Criteria
  • At least 1 claim in IQVIA Patient Centric Medical Claims Database (Dx) with SCD diagnosis (ICD-10 D57.xx, except D57.3) within the study period;
  • At least 1 claim for administration of crizanlizumab within the index period. Index date was the date of first administration;
  • At least 1 claim with HCPCs for crizanlizumab (J0791) OR with at least one claim for an unspecified biologic (J3590) on the same day as a claim for SCD (ICD-10 D57.xx, except D57.3) OR with at least one claim with HCPCs C9053;
  • At least 16 years of age on the index date;
  • Linkage to the IQVIA Longitudinal Prescription Database (LRx) within the study period;
  • Stability and eligibility in Dx during the 12 months prior to the index date;
  • Stability and eligibility in LRx during the 12 months prior to the index date
Exclusion Criteria
  • None

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Overall cohortCrizanlizumabAll the patients who met the base inclusion criteria were included in the cohort.
Three-month cohort (3m cohort)CrizanlizumabPatients with stability and eligibility in IQVIA Patient Centric Medical Claims Database (Dx) and stability and eligibility in IQVIA Longitudinal Prescription Database (LRx) during the 3 months following the index date were included in the cohort.
Six-month cohort (6m cohort)CrizanlizumabA subset of patients from the 3m cohort with stability and eligibility in Dx and stability and eligibility in LRx during the 6 months following the index date were included in this cohort.
Primary Outcome Measures
NameTimeMethod
Number of patients by Charlson Comorbidity Index (CCI) score categoryBaseline

Severity of comorbidity was categorized into three grades: mild, with CCI scores of 1-2; moderate, with CCI scores of 3-4; and severe, with CCI scores ≥5.

Number of patients with history of additional SCD-related comorbidities associated with organ damageBaseline

Number of patients with history of additional SCD-related comorbidities associated with organ damage were reported.

Number of patients : History of hydroxyurea useBaseline

Pre-index treatment history for sickle cell disease was reported.

Number of patients by comorbidityBaseline

Number of patients by IQVIA's standard comorbidity list were reported.

Number of patients : SCD genotypeBaseline

Number of patients with sickle cell disease genotype were reported.

Number of patients: GenderBaseline

Gender information was reported.

Number of patients: Geographic regionBaseline

The following categories were included:

Northeast, Midwest, South, West

Number of patients : History of L-glutamine useBaseline

Pre-index treatment history for sickle cell disease was reported.

Number of patients : History of Voxelotor useBaseline

Pre-index treatment history for sickle cell disease was reported.

Number of patients: Insurance typeBaseline

When multiple payer types were observed, the following hierarchy was used: Medicare, Commercial, Medicaid, Cash, Unspecifed.

When commercially-managed Medicaid was observed, the Medicaid designation was assigned.

AgeBaseline

Age information was reported.

Secondary Outcome Measures
NameTimeMethod
Number of hydroxyurea claimsThroughout the follow-up period, approximately 1.5 years

Concomitant SCD treatments after initiating crizanlizumab

Number of voxelotor claimsThroughout the follow-up period, approximately 1.5 years

Concomitant SCD treatments after initiating crizanlizumab

Proportion of patients with claims for L-glutamine while on crizanlizumab therapyThroughout the follow-up period, approximately 1.5 years

Concomitant SCD treatments after initiating crizanlizumab

Number of L-glutamine claimsThroughout the follow-up period, approximately 1.5 years

Concomitant SCD treatments after initiating crizanlizumab

Proportion of patients with claims for hydroxyurea while on crizanlizumab therapyThroughout the follow-up period, approximately 1.5 years

Concomitant SCD treatments after initiating crizanlizumab

Proportion of patients with claims for voxelotor while on crizanlizumab therapyThroughout the follow-up period, approximately 1.5 years

Concomitant SCD treatments after initiating crizanlizumab

Trial Locations

Locations (1)

Novartis Investigative Site

🇺🇸

East Hanover, New Jersey, United States

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