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Phe for Me? The Effects of L-Phe on PKU Carriers and Non-carriers

Not Applicable
Recruiting
Conditions
Autosomal Recessive Disorder (Genetic Carriers of PKU)
Interventions
Dietary Supplement: L-Phenylalanine
Registration Number
NCT06119048
Lead Sponsor
University of Guelph
Brief Summary

This is a clinical intervention study of PKU carriers (cases) and non-carriers (controls). Upon completing the informed consent process, participants will complete baseline measures of chronic mental health prior to the intervention (PHQ-9, GAD-7, BIS-11). Participants will attend the Human Nutraceutical Research Unit (HNRU) at the University of Guelph, fasted, and first undergo baseline measures of cognition and acute mental health (mood) and provide samples or saliva, urine and dried blood spots to evaluate phenylalanine (Phe), tyrosine (Tyr) and their metabolites (PAH pathway functioning) as well as for genetic testing of the PAH gene. Participants will also complete a brief questionnaire which will include age, sex, ethnicity, income, weight and height (measured using a stadiometer and calibrated weigh scale), and confirmation that participants arrived to the lab fasted (i.e. have only had water to drink and no other foods/ beverages prior to analyses). Blood pressure and heart rate will also be measured at baseline.

Following baseline tests, participants will consume a pure L-Phe supplement dosed at 100 mg/kg mixed with 125 mL of water and 125mL of orange juice. Blood pressure and heart rate will be repeated at 1-hour post-L-Phe consumption. Two-hours postprandial, participants will repeat the cognitive tests and acute mental health (mood) assessment, blood pressure and heart rate measurement and provide follow-up saliva, urine and dried blood spot samples. Participants will also be asked to report any side effects they experienced with the L-Phe consumption.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
50
Inclusion Criteria
  • Carrier or non-carrier of PKU
  • At least 18 Years of age
  • Comfortable fasting the morning of the study (no food or drink other than water)
Exclusion Criteria
  • Diagnosed with: PKU, severe neurodegenerative conditions affecting cognition (e.g. Alzheimer's, Parkinson's, dementia), melanoma, hypertension, liver disease and/or kidney disease
  • Diagnosed with hypertension or hypotension
  • Taking a monoamine oxidase inhibitor anti-depressant
  • Pregnant or breastfeeding
  • Orange/citrus allergy or intolerance
  • Body weight 150 kg or greater
  • History of fainting during blood sampling

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Genetic Carriers and Non-Carriers of PKUL-Phenylalanine-
Primary Outcome Measures
NameTimeMethod
Stop Signal Reaction TimeChange from baseline to 2-hours post L-Phe supplementation

Response Inhibition

Secondary Outcome Measures
NameTimeMethod
Working MemoryChange from baseline to 2-hours post L-Phe supplementation

N-Back Test Outcome

Tyrosine LevelsChange from baseline to 2-hours post L-Phe supplementation

Blood, saliva and urine sample analyses

Tyrosine MetabolitesChange from baseline to 2-hours post L-Phe supplementation

e.g. L-DOPA, dopamine, norepinephrine, epinephrine, p-hydroxyphenylpyruvate, homogentisic acid, fumarate, others

MoodChange from baseline to 2-hours post L-Phe supplementation

Profile of Mood State (POMS) Outcome

Individual Coefficient of Variance (Variability in Reaction Time)Change from baseline to 2-hours post L-Phe supplementation

Stop Signal Task Outcome

Phenylalanine LevelsChange from baseline to 2-hours post L-Phe supplementation

Blood, saliva and urine sample analyses

Phenylalanine MetabolitesChange from baseline to 2-hours post L-Phe supplementation

e.g. phenylethylamine, tyramine, phenylpyruvate, others

Blood PressureChange from baseline to 1-hour and 2-hours post L-Phe supplementation

Systolic and Diastolic

Heart rateChange from baseline to 1-hour and 2-hours post L-Phe supplementation

BPM

Side Effects Following L-Phe Consumption0-3 hours post L-Phe consumption

To be monitored throughout the visit to the research unit

Trial Locations

Locations (1)

University of Guelph

🇨🇦

Guelph, Ontario, Canada

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