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A Pilot Study to Assess Safety and Efficacy of SIR1-365 in Patients With Severe COVID-19

Phase 1
Completed
Conditions
Corona Virus Infection
Interventions
Drug: Matching Placebo
Registration Number
NCT04622332
Lead Sponsor
Sironax USA, Inc.
Brief Summary

Primary Objective:

• To evaluate overall safety and tolerability of SIR1-365 in patients with severe COVID-19

Secondary Objectives:

* To assess the clinical efficacy of SIR1-365 in patients with severe COVID-19

* To assess the effects of SIR1-365 on multiple inflammatory biomarker levels including C-reactive protein (CRP), ferritin, lymphocyte and neutrophil counts, cytokines, and chemokines

* To assess the effects of SIR1-365 on biomarkers indicative of target engagement in patients with severe COVID-19

* To assess the effects of SIR1-365 on biomarkers indicative of kidney injury in patients with severe COVID-19

* To assess the effects of SIR1-365 on biomarkers indicative of cardiovascular endothelial cell damage in patients with severe COVID-19

* To characterize plasma pharmacokinetics (PK) of SIR1-365 in patients with severe COVID-19

Detailed Description

Study duration per participant is approximately 28 days including a 14-day treatment period

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
45
Inclusion Criteria
  • Hospitalized patient with clinical diagnosis of SARS-CoV-2 virus infection per World Health Organization criteria including positive nucleic acid test of any specimen (e.g., respiratory, blood, or other bodily fluid) within 2 weeks prior to screening.
  • Symptoms suggestive of severe systemic illness with COVID-19, which could include any of the following symptoms: fever, cough, sore throat, malaise, headache, muscle pain, gastrointestinal symptoms, or shortness of breath at rest, or respiratory distress.
  • Clinical signs indicative of severe systemic illness with COVID-19, which could include any of the following clinical signs: respiratory rate ≥ 30 per minutes, heart rate ≥ 125 per minute, SpO2 ≤ 93% on room air, or PaO2/FiO2 ratio < 300 mmHg.
  • Men or women ≥18 but ≤80 years of age at the time of signing the informed consent.
  • Patient is able to understand the purpose and risks of the study and provide signed and dated informed consent or have a legal representative provide consent and authorization to use protected health information (in accordance with national and local patient privacy regulations).
Exclusion Criteria
  • Patient requires endotracheal intubation and mechanical ventilation, oxygen delivered by high-flow nasal cannula (heated, humidified, oxygen delivered via reinforced nasal cannula at flow rates >20 L/min with fraction of delivered oxygen ≥ 0.5), noninvasive positive pressure ventilation, extracorporeal membrane oxygenation (ECMO), or clinical diagnosis of respiratory failure.
  • Patient with shock defined by systolic blood pressure < 90 mm Hg, or diastolic blood pressure < 60 mm Hg or requiring vasopressor.
  • Patient with multi-organ dysfunction or failure defined by an increase in the Sequential Organ Failure Assessment score of 2 points or more.
  • Patient is unlikely to survive beyond 2 days at the discretion of Investigator.
  • Patient has used chronic systemic corticosteroids within 2 weeks prior to screening.
  • Patient with positive results for human immunodeficiency virus (HIV) or hepatitis B or C test.
  • Patient has known active tuberculosis (TB), history of uncontrolled TB, suspected or known systemic bacterial or fungal infections within 4 weeks prior to screening.
  • Patient has any other condition, which makes the patient unsuitable for study participation

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Matching placeboMatching PlaceboMatching placebo dose 1 daily for 14 days
SIR1-365SIR1-365SIR1-365 dose 1 daily for 14 days
Primary Outcome Measures
NameTimeMethod
Proportion of patients with any TEAEs during the treatment periodBaseline to Day 14

Primary Safety Endpoint

Secondary Outcome Measures
NameTimeMethod
Proportion of patients with any AEs, SAEs and drug-related AEs during the studyBaseline to Day 14 and Day 28

Secondary Safety Endpoint

Proportion of patients with clinically significant abnormality in clinical laboratory tests and ECG during the studyBaseline to Day 14 and Day 28

Secondary Safety Endpoint

Change from Baseline to Day 7 and Day 14 in PaO2/FiO2 ratioBaseline to Day 7 and Day 14

Clinical Efficacy Endpoint

Time to improvement of oxygenation defined as oxygen saturation (pulse oximetry) >93% and increased ≥1% from Baseline breathing only room air in the 48 hours preceding the measurement during the studyBaseline to Day 28

Clinical Efficacy Endpoint

Number of days without oxygen use during the studyBaseline to Day 28

Clinical Efficacy Endpoint

Proportion of patients with clinical improvement defined as a reduction of 2 points in the WHO ordinal scale during the studyBaseline to Day 28

Clinical Efficacy Endpoint

Number of days hospitalized during the studyBaseline to Day 28

Clinical Efficacy Endpoint

Proportion of patients free of respiratory failure during the studyBaseline to Day 28

Clinical Efficacy Endpoint

All-cause mortality rate during the studyBaseline to Day 28

Clinical Efficacy Endpoint

Change from Baseline to Day 7 and to Day 14 in plasma CRP levelBaseline to Day 7 and to Day 14

Inflammatory Biomarker Measure

Time to reach 50% reduction from Baseline in plasma CRP level during the treatment periodBaseline to Day 14

Inflammatory Biomarker Measure

Plasma drug levelsBaseline to Day 7 and Day 14

Assessment of PK profile

Number of the patients to reach 50% reduction from Baseline in plasma CRP level during the treatment periodBaseline to Day 14

Inflammatory Biomarker Measure

Change from Baseline to Day 7 and Day 14 in serum cytokine levelsBaseline to Day 7 and Day 14

Inflammatory Biomarker Measure

Change from Baseline to Day 7 and Day 14 in plasma pRIP1 and pMLKL levelsBaseline to Day 7 and Day 14

Biomarker Assessment for Target Engagement

Change from Baseline to Day 7 and Day 14 in urine NGAL and KIM-1 levelsBaseline to Day 7 and Day 14

Biomarker Assessment for Kidney Injury

Trial Locations

Locations (9)

Triple O Research Institute

🇺🇸

West Palm Beach, Florida, United States

Baptist Medical Center

🇺🇸

Jackson, Mississippi, United States

Hospital Universitario "Dr. José Eleuterio González"

🇲🇽

Monterrey, Nuevo León, Mexico

Sindh Infectious Disease Hospital

🇵🇰

Karachi, Sindh, Pakistan

Aga Khan University Hospital

🇵🇰

Karachi, Sindh, Pakistan

Hospital Civil Fray Antonio Alcalde

🇲🇽

Guadalajara, Jalisco, Mexico

Dow University Hospital, Ojha Karachi

🇵🇰

Karachi, Sindh, Pakistan

Media Sur - Medica Sur Tlalpan

🇲🇽

Tlalpan, Mexico

OSF St. Francis Medical Center

🇺🇸

Peoria, Illinois, United States

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